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Erdheim-Chester Disease — Treatment Landscape & Competitive Intelligence

Erdheim-Chester Disease (disease) competitive landscape: 2 marketed treatments tracked, 0 Phase 3 candidates, 0 Phase 2 candidates. Recent regulatory actions and upcoming PDUFA dates across the entire treatment set.

2 marketed 0 Phase 3 0 Phase 2 Live · 30-min refresh

Marketed treatment landscape

Approved drugs treating Erdheim-Chester Disease, deduplicated by molecule. See the full disease page for line-of-therapy detail.

DrugGenericSponsorClassTargetLine of therapyFirst approval
Zelboraf vemurafenib Hoffmann La Roche Kinase Inhibitor [EPC] Serine/threonine-protein kinase B-raf 2011-01-01
Zelboraf Zelboraf Hoffmann-La Roche Aspartyl/asparaginyl beta-hydroxylase, Ferrochelatase, mitochondrial, Dual specificity mitogen-activated protein kinase kinase 5

Phase 3 pipeline

No Phase 3 pipeline candidates tracked.

Phase 2 pipeline

No Phase 2 pipeline candidates tracked.

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this treatment set.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this treatment set.

Sponsor landscape

  1. Hoffmann La Roche · 1 drug in Erdheim-Chester Disease
  2. Hoffmann-La Roche · 1 drug in Erdheim-Chester Disease

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Every new regulatory action, PDUFA date, or trial completion in Erdheim-Chester Disease:

Cite this brief

Drug Landscape (2026). Erdheim-Chester Disease — Treatment Landscape & Competitive Intelligence Brief. https://druglandscape.com/ci/disease/erdheim-chester-disease. Accessed 2026-06-10.

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing