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Deficiency of aromatic-L-amino-acid decarboxylase — Treatment Landscape & Competitive Intelligence

Deficiency of aromatic-L-amino-acid decarboxylase (disease) competitive landscape: 1 marketed treatments tracked, 0 Phase 3 candidates, 0 Phase 2 candidates. Recent regulatory actions and upcoming PDUFA dates across the entire treatment set.

1 marketed 0 Phase 3 0 Phase 2 Live · 30-min refresh

Marketed treatment landscape

Approved drugs treating Deficiency of aromatic-L-amino-acid decarboxylase, deduplicated by molecule. See the full disease page for line-of-therapy detail.

DrugGenericSponsorClassTargetLine of therapyFirst approval
Upstaza ELADOCAGENE EXUPARVOVEC PTC Therapeutics International Limited 2022-01-01

Phase 3 pipeline

No Phase 3 pipeline candidates tracked.

Phase 2 pipeline

No Phase 2 pipeline candidates tracked.

Recent regulatory actions (last 90 days)

No regulatory actions in the last 90 days for this treatment set.

Upcoming PDUFA dates (next 180 days)

No PDUFA dates in the next 180 days for this treatment set.

Sponsor landscape

  1. PTC Therapeutics International Limited · 1 drug in Deficiency of aromatic-L-amino-acid decarboxylase

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Every new regulatory action, PDUFA date, or trial completion in Deficiency of aromatic-L-amino-acid decarboxylase:

Cite this brief

Drug Landscape (2026). Deficiency of aromatic-L-amino-acid decarboxylase — Treatment Landscape & Competitive Intelligence Brief. https://druglandscape.com/ci/disease/deficiency-of-aromatic-l-amino-acid-decarboxylase. Accessed 2026-06-10.

Related

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing