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Novartis Gene Therapies — Portfolio Competitive Intelligence Brief
1 marketed
0 filed
0 Phase 3
0 Phase 2
1 Phase 1
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Portfolio leaders (marketed + Phase 3 / filed)
| Drug | Generic | Phase | Class | Target | Area | First approval |
|---|---|---|---|---|---|---|
| Onasemnogene Abeparvovec-xioi | Onasemnogene Abeparvovec-xioi | marketed | Gene therapy | SMN1 gene | Neurology |
Therapeutic area mix
- Neurology · 1
- Rare Disease · 1
Recent regulatory actions (last 90 days)
Upcoming PDUFA dates (next 180 days)
Patent timeline (forward window)
Competitive overlap (companies sharing drug classes)
- Abeona Therapeutics, Inc · 1 shared drug class
- AskBio Inc · 1 shared drug class
- BioLab 612 LLC · 1 shared drug class
- Brain Neurotherapy Bio, Inc. · 1 shared drug class
- Emily de los Reyes · 1 shared drug class
- Eva Morava-Kozicz · 1 shared drug class
- Kolon TissueGene, Inc. · 1 shared drug class
- 4D Molecular Therapeutics · 1 shared drug class
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Cite this brief
Drug Landscape (2026). Novartis Gene Therapies — Portfolio Competitive Intelligence Brief. https://druglandscape.com/ci/company/novartis-gene-therapies. Accessed 2026-05-17.