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Alexion Pharmaceuticals, Inc. — Portfolio Competitive Intelligence Brief
1 marketed
0 filed
5 Phase 3
8 Phase 2
35 Phase 1
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Portfolio leaders (marketed + Phase 3 / filed)
| Drug | Generic | Phase | Class | Target | Area | First approval |
|---|---|---|---|---|---|---|
| Ultomiris | Ultomiris | marketed | Complement C5 | Other | ||
| ALXN1850 | ALXN1850 | phase 3 | Complement C3 inhibitor | Complement C3 | Nephrology / Immunology | |
| ALXN2060 | ALXN2060 | phase 3 | Complement C3 inhibitor | Complement C3 | Immunology / Hematology | |
| C5 Inhibitor | C5 Inhibitor | phase 3 | Complement C5 inhibitor | C5 | Immunology | |
| CAEL-101 | CAEL-101 | phase 3 | Transthyretin (TTR) stabilizer | Transthyretin (TTR) | Rare Disease / Amyloidosis | |
| pexelizumab in conjunction with CABG | pexelizumab in conjunction with CABG | phase 3 | Monoclonal antibody | Complement component 5 (C5) | Cardiovascular |
Therapeutic area mix
- Rare Disease · 2
- Cardiovascular · 1
- Genetics and Rare Diseases · 1
- Immunology · 1
- Immunology / Hematology · 1
- Nephrology / Immunology · 1
- Neurology · 1
- Other · 1
- Autoimmune diseases · 1
- Rare Disease / Amyloidosis · 1
Recent regulatory actions (last 90 days)
Upcoming PDUFA dates (next 180 days)
Patent timeline (forward window)
Competitive overlap (companies sharing drug classes)
- Sanofi · 2 shared drug classes
- CSL Behring · 2 shared drug classes
- Hoffmann-La Roche · 2 shared drug classes
- Pfizer Inc. · 2 shared drug classes
- Arbeitsgemeinschaft medikamentoese Tumortherapie · 1 shared drug class
- Assistance Publique - Hôpitaux de Paris · 1 shared drug class
- Aldeyra Therapeutics, Inc. · 1 shared drug class
- Apellis Pharmaceuticals, Inc. · 1 shared drug class
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Cite this brief
Drug Landscape (2026). Alexion Pharmaceuticals, Inc. — Portfolio Competitive Intelligence Brief. https://druglandscape.com/ci/company/alexion-pharmaceuticals-inc. Accessed 2026-05-16.