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NCT07413211

Genetic Developmental and Epileptic Encephalopathy Natural History Study for Clinical Trial Readiness

Recruiting now Last updated 17 February 2026
What this trial tests

trial testing Observation in MEF2C in 22,068 participants. Currently enrolling.

Timeline
26 February 2025
Primary endpoint
30 April 2037
30 April 2037

Quick facts

Lead sponsorWeill Medical College of Cornell University
StatusRecruiting now
Study typeOBSERVATIONAL
Enrollment22,068
Start date26 February 2025
Primary completion30 April 2037
Estimated completion30 April 2037
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Weill Medical College of Cornell University

Who can join

Eligibility, any sex, with MEF2C or DEE. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

Phase 0 non-interventional longitudinal study of children and adults with Developmental and Epileptic Encephalopathy (DEE) due to a genetic cause. There are six arms of the study. Arms 1, 2, and 3 are devoted to one example DEE, MEF2C Haploinsufficiency Syndrome (MCHS). Arms 4, 5, and 6 are open to all DEE. Arm 1 (in-person) will enroll children 0 to 15, who will make in-person visits to Weill Cornell Medicine four times over two years. Arm 2 (virtual) will enroll people of all ages and older who will make virtual visits over Weill Cornell Zoom to Weill Cornell Medicine over two years (2 if 16 and older; 4 if 0 to 15). Arm 3 (registry) will enroll people of all ages in an online-only survey. Arms 4 - 6 mirror this structure but they are open to all children with DEE. Arm 4 (in-person) will enroll children of any age, who will make in-person visits every 6 months for 10 years. Arm 5 (virtual) will enroll children of any age for virtual visits, twice a year of 0 to 15, once a year if 16 or older. Arm 6 (registry) will enroll people of all ages in an online only survey.

Publications & conference data

No peer-reviewed publications indexed yet for this trial.

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Other trials of Observation

Trials testing the same drug.

Other Weill Medical College of Cornell University trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT07413211.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing