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NCT07150013

Rett REVOLUTION Trial: An Exploratory Evaluation of the Safety and Efficacy of Vorinostat in Rett Syndrome

Not yet recruiting Phase 1 Last updated 2 September 2025
What this trial tests

Phase 1 trial testing Vorinostat (SAHA) in Rett Syndrome in 15 participants. Not yet recruiting.

Timeline
15 October 2025
Primary endpoint
15 July 2026
15 October 2026

Quick facts

Lead sponsorUnravel Biosciences, Inc.
PhasePhase 1
StatusNot yet recruiting
Study typeINTERVENTIONAL
Allocationnon randomized
Designcrossover
Maskingdouble
Primary purposetreatment
Enrollment15
Start date15 October 2025
Primary completion15 July 2026
Estimated completion15 October 2026
Sites1 location across Colombia

Drugs / interventions tested

Conditions studied

Sponsor

Unravel Biosciences, Inc. — full company profile →

Who can join

Adults 6 to 21, female only, with Rett Syndrome. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

The RETT REVOLUTION trial is a placebo-controlled, single-blinded, exploratory study with patients serving as their own control ("N of 1" trial design) where the safety and efficacy of vorinostat in the treatment of Rett syndrome will be evaluated. Each patient will be self-controlled in an adapted N-of-1 study design methodology by using a 4-week placebo baseline. Vorinostat dose escalation will occur every 8 weeks of daily dosing: placebo, 80mg/m2/day, 160mg/m2/day. Key study objectives will include: * To confirm the safety and tolerability of oral vorinostat 80mg/m2/day and 160mg/ m2/day dose levels when administered to typical Rett patients * To identify the nature and magnitude of treatment response to vorinostat, as measured by changes in clinical and laboratory parameters indicative of trend towards benefit, as well as changes in mRNA expression (transcriptome response) * Provide a data-driven justification for future study design and statistical analysis plan for subsequent clinical studies assessing safety and efficacy of vorinostat in Rett syndrome

Publications & conference data

No peer-reviewed publications indexed yet for this trial.

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Other trials of Vorinostat (SAHA)

Trials testing the same drug.

Other recruiting trials for Rett Syndrome

Currently open trials in the same condition.

Other Unravel Biosciences, Inc. trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT07150013.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing