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NCT07049588: CMT-MODS

Identification of Novel Biomarkers in Early Charcot-Marie-Tooth 1A Disease

Recruiting now NA Last updated 3 July 2025
What this trial tests

NA trial testing Quantitative neuromuscular MRI in Charcot-Marie-Tooth Disease Type 1A in 55 participants. Currently enrolling.

Timeline
24 June 2025
Primary endpoint
24 June 2027
24 June 2028

Quick facts

Lead sponsorAssistance Publique Hopitaux De Marseille
PhaseNA
StatusRecruiting now
Study typeINTERVENTIONAL
Allocationnon randomized
Designparallel
Maskingnone
Primary purposeother
Enrollment55
Start date24 June 2025
Primary completion24 June 2027
Estimated completion24 June 2028
Sites1 location across France

Drugs / interventions tested

Conditions studied

Sponsor

Assistance Publique Hopitaux De Marseille — full company profile →

Who can join

Adults 10 to 30, any sex, with Charcot-Marie-Tooth Disease Type 1A. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

This is a 2-year follow-up study of a cohort of 35 CMT1A patients and 20 healthy volunteers. The main objective is identifying prognostic markers for CMT1A using multi-omics analysis. The study is recruiting subjects between the ages of 10 and 30. The most common inherited neuropathy is Charcot-Marie-Tooth disease type 1A (CMT1A), caused by a duplication of the gene expressing PMP22. CMT1A patients develop symptoms in early childhood with variable progression and there is no established therapy until now. Therapy must start in childhood, before peripheral nerves degenerate. However, we lack easily obtainable biomarkers in early disease stages. In CMT-MODs, we will identify disease and prognostic biomarkers in young CMT1A patients.

Publications & conference data

No peer-reviewed publications indexed yet for this trial.

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Other recruiting trials for Charcot-Marie-Tooth Disease Type 1A

Currently open trials in the same condition.

Other Assistance Publique Hopitaux De Marseille trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT07049588.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing