Last reviewed · How we verify

NCT06678165

A Pilot Study on the Safety and Efficacy of YOLT-204 for Transfusion-Dependent Beta-Thalassemia

Not yet recruiting EARLY_PHASE1 Last updated 7 November 2024
What this trial tests

EARLY_PHASE1 trial testing YOLT-204 in Transfusion Dependent Beta Thalassemia in 3 participants. Not yet recruiting.

Timeline
31 December 2024
Primary endpoint
1 June 2026
1 June 2026

Quick facts

Lead sponsorFirst Affiliated Hospital of Guangxi Medical University
PhaseEARLY_PHASE1
StatusNot yet recruiting
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment3
Start date31 December 2024
Primary completion1 June 2026
Estimated completion1 June 2026
Sites1 location across China

Drugs / interventions tested

Conditions studied

Sponsor

First Affiliated Hospital of Guangxi Medical University

Who can join

Adults 18 to 35, any sex, with Transfusion Dependent Beta Thalassemia. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

This study is a single-arm, open-label, dose-escalation trial, planning to enroll 3-9 patients with transfusion-dependent β-thalassemia, aimed at assessing the safety and tolerability of a single-dose of YOLT-204 in patients with transfusion-dependent β-thalassemia; to preliminarily evaluate the impact of a single -dose of YOLT-204 on the levels of fetal hemoglobin in the plasma

Publications & conference data

No peer-reviewed publications indexed yet for this trial.

Verify or expand the search:

Other trials of YOLT-204

Trials testing the same drug.

Other recruiting trials for Transfusion Dependent Beta Thalassemia

Currently open trials in the same condition.

Other First Affiliated Hospital of Guangxi Medical University trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT06678165.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing