Last reviewed · How we verify
NCT06627543
Effect of Enzyme Replacement Therapy on Cardiac Function in Children With Gaucher Disease Type 3
trial testing echo in Gaucher Disease Type 3 in 44 participants. Enrolling by invitation.
1 January 2025
Quick facts
| Lead sponsor | Noha Osman |
|---|---|
| Status | ENROLLING BY INVITATION |
| Study type | OBSERVATIONAL |
| Enrollment | 44 |
| Start date | 1 April 2024 |
| Primary completion | 1 January 2025 |
| Estimated completion | 1 March 2025 |
| Sites | 1 location across Egypt |
Drugs / interventions tested
- echo
Conditions studied
- Gaucher Disease Type 3 — all drugs for Gaucher Disease Type 3 →
Sponsor
Noha Osman
Who can join
Eligibility, any sex, with Gaucher Disease Type 3. Patients with the condition only — healthy volunteers not accepted.
Sponsor's own description
all cases confirmed diagnosis of Gaucher disease type 3 recieving enzyme replacement therapy at Assiut university hospital
Publications & conference data
No peer-reviewed publications indexed yet for this trial.
Verify or expand the search:
- PubMed search for NCT06627543
- Europe PMC full search
- ASCO Meeting Library
- ESMO Meeting Library
- bioRxiv preprints
- medRxiv preprints
- Google Scholar
Related trials
Other recruiting trials for Gaucher Disease Type 3
Currently open trials in the same condition.
- NCT02843035 — Venglustat in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 With Venglustat Monotherapy Extens · Phase 2 · active not recruiting
Other Noha Osman trials
Trials by the same sponsor.
- NCT06579560 — Audio Vestibular Assessment in Patients with Fibromyalgia · recruiting
Verify against primary sources
- ClinicalTrials.gov — authoritative US registry record
- WHO ICTRP — international registry index
- EU Clinical Trials Register
- Sponsor press releases (Google)
- Trial protocol + status: ClinicalTrials.gov NCT06627543 (US National Library of Medicine, public domain)
- Drug + disease cross-links: matched in real time against Drug Landscape's normalised drug + company + condition tables
- Sponsor: as reported to ClinicalTrials.gov by Noha Osman
- Last refreshed: 4 October 2024
Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT06627543.
Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing