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NCT06307990: ADAM-THAD

Understanding, Diagnosis and Monitoring of Thyroid Hormone Action Defects

Recruiting now Last updated 2 September 2025
What this trial tests

trial testing NGS sequencing in Resistance, Thyroid Hormone in 150 participants. Currently enrolling.

Timeline
1 January 2023
Primary endpoint
31 October 2025
31 January 2026

Quick facts

Lead sponsorIstituto Auxologico Italiano
StatusRecruiting now
Study typeOBSERVATIONAL
Enrollment150
Start date1 January 2023
Primary completion31 October 2025
Estimated completion31 January 2026
Sites2 locations across Italy

Drugs / interventions tested

Conditions studied

Sponsor

Istituto Auxologico Italiano — full company profile →

Who can join

Eligibility, any sex, with Resistance, Thyroid Hormone. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

The goal of this observational study is to learn about the neurological and cardiological phenotype of patients with resistance to thyroid hormone (RTH) syndromes beta and alpha (RTHß and RTHa) due to dominant negative variants in the genes encoding the thyroid hormone receptors alpha (THRA) and beta (THRB). The main question\[s\] it aims to answer are: * Define frequency and improve early diagnosis for RTH syndromes * Developing tools to accelerate diagnosis of RTH syndromes * Development and validation of monitoring tools Participants, recruited at neonatal screening or from cohorts of patients with unexplained specific neuro-cognitive or cardiovascular phenotypes will be submitted to biochemical and genetic investigations. In addition pluripotent stem cells will be generated from peripheral blood cells of RTHs patients and studied in vitro to understand the molecular mechanisms underlying neurological and cardiovascular consequences. In vitro and clinical data, will be correlated to identify biomarkers for monitoring treatment.

Publications & conference data

No peer-reviewed publications indexed yet for this trial.

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Other Istituto Auxologico Italiano trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT06307990.

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