Last reviewed · How we verify

NCT06030648

MT2022-01: MSCs for ALD

Suspended Phase 1 Last updated 30 May 2025
What this trial tests

Phase 1 trial testing Mesenchymal stem cells (IV-MSC) in Cerebral Adrenoleukodystrophy in 10 participants. Suspended.

Timeline
28 August 2023
Primary endpoint
1 May 2026
1 May 2028

Quick facts

Lead sponsorMasonic Cancer Center, University of Minnesota
PhasePhase 1
StatusSuspended
Study typeINTERVENTIONAL
Allocationnon randomized
Designparallel
Maskingnone
Primary purposetreatment
Enrollment10
Start date28 August 2023
Primary completion1 May 2026
Estimated completion1 May 2028
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Masonic Cancer Center, University of Minnesota

Who can join

3 and older, any sex, with Cerebral Adrenoleukodystrophy. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

This is a single-institution study to evaluate the use of intravenously administered allogeneic, 3rd party mesenchymal stem cells (IV-MSC) in patients with active, cerebral adrenoleukodystrophy (CALD), as a bridge to hematopoietic stem cell transplant or gene therapy, or in patients who are too advanced for gene therapy or HSCT. The intervention will occur in the time between diagnosis of active CALD and transplant which is currently 8-12 weeks.

Publications & conference data

2 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Emerging Landscape of Mesenchymal Stem Cell Senescence Mechanisms and Implications on Therapeutic Strategies.
    Wang J, Zhang M, Wang H. · · 2024 · cited 13× · PMID 39144566 · DOI 10.1021/acsptsci.4c00284
  2. Stem cell and gene therapies for leukodystrophies.
    Lin W, Zhang M, Zheng S, Lian Q. · · 2025 · cited 1× · PMID 40836959 · DOI 10.1016/j.omtm.2025.101527

Verify or expand the search:

Other Masonic Cancer Center, University of Minnesota trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT06030648.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing