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NCT05643274: HiFi-NDD

Use of Long Read Genome Sequencing in Patients Suffering From Neurodevelopmental Troubles

Completed Last updated 24 April 2024
What this trial tests

trial in Genetic Disease in 10 participants. Completed in 8 March 2024.

Timeline
19 December 2022
Primary endpoint
8 March 2023
8 March 2024

Quick facts

Lead sponsorNantes University Hospital
StatusCompleted
Study typeOBSERVATIONAL
Enrollment10
Start date19 December 2022
Primary completion8 March 2023
Estimated completion8 March 2024
Sites5 locations across France

Conditions studied

Sponsor

Nantes University Hospital

Who can join

Eligibility, any sex, with Genetic Disease or Neurologic Disorder. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

Patients with neurodevelopmental diseases and their families need to identify the genetic cause of the disease to allow for recognition of the disability, genetic counseling, and possible hope for participation in therapeutic research studies. Access to high-throughput genomic exome or genome analysis allows the identification of a genetic cause for approximately half of the patients. However, families with no result or with a variant of unknown significance after these tests may find themselves in a new diagnostic impasse. The high-throughput sequencing used today generates sequences of the order of 100 base pairs (so-called "short read" sequencing). This allows an analysis of about 90% of the genome. However, many regions are not accessible in regions of interest for the genetic diagnosis of rare diseases. Long fragment sequencing generates sequences that are about 20 times larger and its use has recently made it possible to sequence the human genome almost completely (https://www.science.org/doi/10.1126/science.abj6987). The main contribution lies in the analysis of complex regions of the genome such as segmental duplications or centromeric regions. It is likely that this technology increases the sensitivity of detection of genetic variants in patients with genetic diseases. Its contribution should be studied in patients for whom no genetic cause has been identified by classical techniques. This study aim to investigate the contribution of long fragment genome sequencing.

Publications & conference data

No peer-reviewed publications indexed yet for this trial. Completed trials usually publish results within 12-18 months.

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Other recruiting trials for Genetic Disease

Currently open trials in the same condition.

Other Nantes University Hospital trials

Trials by the same sponsor.

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Data sources for this page

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