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NCT05413135

Study of ARO-APOC3 in Adults With Dyslipidemia

Completed Phase 2 Last updated 17 December 2025
What this trial tests

Phase 2 trial testing ARO-APOC3 in Dyslipidemias in 418 participants. Completed in 18 September 2025.

Timeline
7 July 2022
Primary endpoint
18 September 2025
18 September 2025

Quick facts

Lead sponsorArrowhead Pharmaceuticals
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment418
Start date7 July 2022
Primary completion18 September 2025
Estimated completion18 September 2025
Sites60 locations across New Zealand, Netherlands, Hungary, Poland, Canada, Australia, United States

Drugs / interventions tested

Conditions studied

Sponsor

Arrowhead Pharmaceuticals — full company profile →

Who can join

18 and older, any sex, with Dyslipidemias. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

This is an open-label extension of the parent studies AROAPOC3-2001 and AROAPOC3-2002. Adult participants with dyslipidemia who completed the blinded 12-month period from either parent study and continued to meet eligibility criteria had the option to be enrolled into this study. Eligible enrolled participants initially received open-label ARO-APOC3 every three or six months at the assigned dose level of the parent study until a final dose of 25 mg was selected, at which point all participants transitioned to the selected dosing regimen of 25 mg every 3 months.

Publications & conference data

7 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Exploring apolipoprotein C-III: pathophysiological and pharmacological relevance.
    Packard CJ, Pirillo A, Tsimikas S, Ference BA, et al · · 2024 · cited 33× · PMID 38039351 · DOI 10.1093/cvr/cvad177
  2. Hepatocyte targeting <i>via</i> the asialoglycoprotein receptor.
    Ramírez-Cortés F, Ménová P. · · 2025 · cited 22× · PMID 39628900 · DOI 10.1039/d4md00652f
  3. New pharmacological agents and novel cardiovascular pharmacotherapy strategies in 2023.
    Tamargo J, Agewall S, Borghi C, Ceconi C, et al · · 2024 · cited 13× · PMID 38379024 · DOI 10.1093/ehjcvp/pvae013
  4. Current RNA strategies in treating cardiovascular diseases.
    Chia SPS, Pang JKS, Soh BS. · · 2024 · cited 13× · PMID 38291757 · DOI 10.1016/j.ymthe.2024.01.028
  5. New pharmacological agents and novel cardiovascular pharmacotherapy strategies in 2024.
    Tamargo J, Agewall S, Ambrosio G, Borghi C, et al · · 2025 · cited 6× · PMID 40058879 · DOI 10.1093/ehjcvp/pvaf012
  6. RNA interference therapy in cardiology: will new targets improve therapeutic goals?
    Fazoli RT, Drager LF, Kalil-Filho R, Generoso G. · · 2024 · cited 4× · PMID 39188988 · DOI 10.7573/dic.2024-3-1
  7. Realizing the therapeutic potential of rapid knockdown of transthyretin via RNA interference in transthyretin amyloidosis.
    Grogan M, Sheikh FH, Sperry BW, Sweetser MT, et al · · 2025 · PMID 40686854 · DOI 10.1016/j.omtn.2025.102590

Verify or expand the search:

Other trials of ARO-APOC3

Trials testing the same drug.

Other recruiting trials for Dyslipidemias

Currently open trials in the same condition.

Other Arrowhead Pharmaceuticals trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT05413135.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing