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NCT05373901

Evaluation of the Safety and Pharmacokinetics of Dinutuximab Beta As Maintenance Therapy in Chinese Participants With High-Risk Neuroblastoma

Completed Phase 1 Results posted Last updated 4 October 2024
What this trial tests

Phase 1 trial testing Dinutuximab Beta in High-risk Neuroblastoma in 8 participants. Completed in 29 June 2023.

Timeline
7 June 2022
Primary endpoint
29 June 2023
29 June 2023

Quick facts

Lead sponsorBeiGene
PhasePhase 1
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment8
Start date7 June 2022
Primary completion29 June 2023
Estimated completion29 June 2023
Sites3 locations across China

Drugs / interventions tested

Conditions studied

Sponsor

BeiGene — full company profile →

Who can join

12 Months and older, any sex, with High-risk Neuroblastoma. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Number of Participants With Adverse Events (AEs) Primary · From the first dose of study drug(s) to 40 days after the last dose; up to approximately 1 year and 1 month

Number of participants with treatment-emergent adverse events (TEAEs) and serious treatment-emergent adverse event, characterized by type, frequency, severity (as graded by the National Cancer Institute- Common Terminology Criteria for Adverse Events Version 5.0 \[NCI-CTCAE v 5.0\]), timing, seriousness, relationship to study treatment, and other safety assessments.

Participants With At Least 1 TEAE
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid8
Participants with Serious TEAEs
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid1
Area Under the Serum Concentration-time Curve From Zero to the Last Measurable Concentration (AUC0-t) of Dinutuximab Beta Primary · From Cycle 1 Day 1 pre-dose to Cycle 2 Day 1 pre-dose (Each cycle is 35 Days)
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid3956.3± 33.11
Area Under the Serum Concentration-time Curve From Zero to Infinity (AUC0-∞) of Dinutuximab Beta Primary · From Cycle 1 Day 1 pre-dose to Cycle 2 Day 1 pre-dose (Each cycle is 35 Days)
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid4228.6± 31.94
Maximum Observed Serum Concentration (Cmax) of Dinutuximab Beta Primary · From Cycle 1 Day 1 pre-dose to Cycle 2 Day 1 pre-dose (Each cycle is 35 Days)
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid13.49± 32.682
Time to Maximum Serum Concentration (Tmax) of Dinutuximab Beta Primary · From Cycle 1 Day 1 pre-dose to Cycle 2 Day 1 pre-dose (Each cycle is 35 Days)
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid240.4168 – 252
Half-Life (t1/2) of Dinutuximab Beta Primary · From Cycle 1 Day 1 pre-dose to Cycle 2 Day 1 pre-dose (Each cycle is 35 Days)
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid253.9200 – 332
Clearance (CL) of Dinutuximab Beta Primary · From Cycle 1 Day 1 pre-dose to Cycle 2 Day 1 pre-dose (Each cycle is 35 Days)
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid17.19± 34.627
Volume of Distribution During Terminal Phase (Vz) of Dinutuximab Beta Primary · From Cycle 1 Day 1 pre-dose to Cycle 2 Day 1 pre-dose (Each cycle is 35 Days)
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid6295.9± 48.87
Volume of Distribution at Steady State (Vss) of Dinutuximab Beta Primary · From Cycle 1 Day 1 pre-dose to Cycle 2 Day 1 pre-dose (Each cycle is 35 Days)
GroupValue95% CI
Dinutuximab Beta + 13-cis-Retinoic Acid3594.0± 37.12

Adverse events — posted to ClinicalTrials.gov

Time frame: All-cause mortality and adverse events (AEs): From the first dose of study drug(s) to 40 days after the last dose; up to approximately 1 year and 1 month. Reporting threshold: 3%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Dinutuximab Beta + 13-cis-Retinoic Acid
Serious: 1/8 (13%)
Deaths: 0/8

Serious adverse events (2 terms)

ReactionSystemDinutuximab Beta + 13-cis-…
PneumoniaInfections and infestations
Decreased appetiteMetabolism and nutrition disorders
Other adverse events (97 terms — click to expand)

ReactionSystemDinutuximab Beta + 13-cis-…
Abdominal painGastrointestinal disorders
PyrexiaGeneral disorders
DiarrhoeaGastrointestinal disorders
Alanine aminotransferase increasedInvestigations
Decreased appetiteMetabolism and nutrition disorders
RashSkin and subcutaneous tissue disorders
AnaemiaBlood and lymphatic system disorders
Aspartate aminotransferase increasedInvestigations
Gamma-glutamyltransferase increasedInvestigations
Dry skinSkin and subcutaneous tissue disorders
HypotensionVascular disorders
Angular cheilitisGastrointestinal disorders
VomitingGastrointestinal disorders
ChillsGeneral disorders
COVID-19Infections and infestations
Upper respiratory tract infectionInfections and infestations
Blood lactate dehydrogenase increasedInvestigations
C-reactive protein increasedInvestigations
Heart rate increasedInvestigations
Neutrophil count decreasedInvestigations
Platelet count decreasedInvestigations
HypertriglyceridaemiaMetabolism and nutrition disorders
HypoalbuminaemiaMetabolism and nutrition disorders
Sinus tachycardiaCardiac disorders
ConstipationGastrointestinal disorders
Fibrin D dimer increasedInvestigations
HypokalaemiaMetabolism and nutrition disorders
HypophagiaMetabolism and nutrition disorders
Pain in extremityMusculoskeletal and connective tissue disorders
CoughRespiratory, thoracic and mediastinal disorders
PapuleSkin and subcutaneous tissue disorders
PruritusSkin and subcutaneous tissue disorders
Skin exfoliationSkin and subcutaneous tissue disorders
EosinophiliaBlood and lymphatic system disorders
LeukocytosisBlood and lymphatic system disorders
ThrombocytopeniaBlood and lymphatic system disorders
Supraventricular tachycardiaCardiac disorders
Ear painEar and labyrinth disorders
Dry eyeEye disorders
PhotophobiaEye disorders

Most-reported serious reactions: Pneumonia, Decreased appetite.

Data from ClinicalTrials.gov NCT05373901 adverse events section.

Sponsor's own description

This was an open-label, multi-center, single-arm, Phase 1 study. The purpose of this study was for evaluating the safety and pharmacokinetics of dinutuximab beta as maintenance therapy in Chinese participants with high-risk neuroblastoma

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. The Neuroblastoma Microenvironment, Heterogeneity and Immunotherapeutic Approaches.
    Polychronopoulos PA, Bedoya-Reina OC, Johnsen JI. · · 2024 · cited 9× · PMID 38791942 · DOI 10.3390/cancers16101863

Verify or expand the search:

Other recruiting trials for High-risk Neuroblastoma

Currently open trials in the same condition.

Other BeiGene trials

Trials by the same sponsor.

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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing