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NCT05358821

28-Day Study of SAGE-718 on Functioning Capacity in Participants With Huntington's Disease

Completed Phase 2 Results posted Last updated 15 September 2025
What this trial tests

Phase 2 trial testing SAGE-718 in Huntington Disease in 69 participants. Completed in 10 April 2024.

Timeline
26 May 2022
Primary endpoint
29 February 2024
10 April 2024

Quick facts

Lead sponsorSupernus Pharmaceuticals, Inc.
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposetreatment
Enrollment69
Start date26 May 2022
Primary completion29 February 2024
Estimated completion10 April 2024
Sites14 locations across Canada, United States

Drugs / interventions tested

Conditions studied

Sponsor

Supernus Pharmaceuticals, Inc. — full company profile →

Who can join

Adults 25 to 65, any sex, with Huntington Disease. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Difference in Huntington's Disease Cognitive Assessment Battery (HD-CAB) Composite Score Between Participants With HD vs HP at Baseline Primary · Baseline

HD-CAB assesses cognitive function using 6 subtests:Symbol Digit Modalities Test-correctly coded items(0-110); One Touch Stockings of Cambridge(OTS)-mean time to reach correct response(range not defined); Trail Making Test Trail B (TMT-B)-time to complete task(0-240 sec); Hopkins Verbal Learning Test Revised-total correct recall trials(0-48); Paced Tapping Test-reciprocal of standard deviation(SD) of intertap intervals (range not defined); Emotion Recognition Test-negative emotions correctly identified(0-24). Values of OTS \& TMT B are multiplied by -1 to represent higher is better direction a

GroupValue95% CI
Participants With HD-3.3657± 1.4613
Healthy Participants0.0000± 0.5673
Number of Participants With HD With Treatment-Emergent Adverse Events (TEAEs) and Serious TEAEs Secondary · Up to Day 42

An adverse event (AE) is any untoward medical occurrence in a participant administered a pharmaceutical product and that does not necessarily have a causal relationship with this treatment. Treatment-emergent adverse events are defined as any adverse events with onset on or after the first dose of IP. A serious TEAE is any untoward medical occurrence that at any dose results in death, places the participant at immediate risk of death (a life-threatening event), requires in-patient hospitalization or prolongation of existing hospitalization, results in persistent or significant disability or in

TEAEs
GroupValue95% CI
Placebo6
SAGE-71811
Serious TEAEs
GroupValue95% CI
Placebo0
SAGE-7180
Number of Participants With HD With Clinically Significant Change From Baseline in Vital Sign Measurements Secondary · Up to Day 42

Vital signs including oral temperature, respiratory rate, heart rate (supine and standing), and blood pressures (supine and standing). Number of participants with clinically significant change in vital signs measurements which were deemed clinically significant by the investigator were reported.

GroupValue95% CI
Placebo0
SAGE-7180
Number of Participants With HD With Clinically Significant Change From Baseline in Clinical Laboratory Assessments Secondary · Up to Day 42

Clinical laboratory assessments including hematology, serum chemistry, coagulation, and urinalysis were performed. Number of participants with clinically significant change in laboratory assessments which were deemed clinically significant by the investigator were reported.

GroupValue95% CI
Placebo0
SAGE-7180

Adverse events — posted to ClinicalTrials.gov

Time frame: Up to Day 42. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Placebo
Serious: 0/19 (0%)
Deaths: 0/19
SAGE-718
Serious: 0/21 (0%)
Deaths: 0/21
Healthy Participants
Serious: 0/29 (0%)
Deaths: 0/29
Other adverse events (12 terms — click to expand)

ReactionSystemPlaceboSAGE-718Healthy Participants
NauseaGastrointestinal disorders
FatigueGeneral disorders
NasopharyngitisInfections and infestations
SomnolenceNervous system disorders
ArthralgiaMusculoskeletal and connective tissue disorders
DyspepsiaGastrointestinal disorders
DepressionPsychiatric disorders
EpistaxisRespiratory, thoracic and mediastinal disorders
Micturition urgencyRenal and urinary disorders
MigraineNervous system disorders
Reflexes abnormalNervous system disorders
SinusitisInfections and infestations

Data from ClinicalTrials.gov NCT05358821 adverse events section.

Sponsor's own description

The primary purpose of this study is to assess the magnitude of the baseline difference between participants with early Huntington's Disease (HD) and healthy participants (HP) with respect to measures of cognitive performance.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Therapeutic potential of N-methyl-D-aspartate receptor modulators in psychiatry.
    Hanson JE, Yuan H, Perszyk RE, Banke TG, et al · · 2024 · cited 79× · PMID 37369776 · DOI 10.1038/s41386-023-01614-3
  2. Huntington's Disease: Complex Pathogenesis and Therapeutic Strategies.
    Tong H, Yang T, Xu S, Li X, et al · · 2024 · cited 50× · PMID 38612657 · DOI 10.3390/ijms25073845
  3. Polyglutamine (PolyQ) Diseases: Navigating the Landscape of Neurodegeneration.
    Tenchov R, Sasso JM, Zhou QA. · · 2024 · cited 31× · PMID 38996083 · DOI 10.1021/acschemneuro.4c00184
  4. Huntington's Disease Clinical Trials Corner: March 2024.
    Estevez-Fraga C, Tabrizi SJ, Wild EJ. · · 2024 · cited 31× · PMID 38489195 · DOI 10.3233/jhd-240017
  5. Huntington's Disease Clinical Trials Corner: August 2023.
    Estevez-Fraga C, Tabrizi SJ, Wild EJ. · · 2023 · cited 22× · PMID 37483021 · DOI 10.3233/jhd-239001
  6. Latest advances on new promising molecular-based therapeutic approaches for Huntington's disease.
    Cheng Y, Zhang S, Shang H. · · 2024 · cited 13× · PMID 38779119 · DOI 10.2478/jtim-2023-0142
  7. Dysfunction of the NMDA Receptor in the Pathophysiology of Schizophrenia and/or the Pathomechanisms of Treatment-Resistant Schizophrenia.
    Okubo R, Okada M, Motomura E. · · 2024 · cited 12× · PMID 39334894 · DOI 10.3390/biom14091128
  8. Huntington's disease clinical trials update: March 2025.
    Farag M, Tabrizi SJ, Wild EJ. · · 2025 · cited 7× · PMID 40302443 · DOI 10.1177/18796397251337000

Verify or expand the search:

Other trials of SAGE-718

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Other Supernus Pharmaceuticals, Inc. trials

Trials by the same sponsor.

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