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NCT05312736: GYROS

Gyrate Atrophy Ocular and Systemic Study

Active, enrolled Last updated 26 January 2026
What this trial tests

trial in Gyrate Atrophy in 46 participants. Participants enrolled and being followed up; not accepting new ones.

Timeline
21 November 2023
Primary endpoint
31 December 2028
31 December 2028

Quick facts

Lead sponsorJaeb Center for Health Research
StatusActive, enrolled
Study typeOBSERVATIONAL
Enrollment46
Start date21 November 2023
Primary completion31 December 2028
Estimated completion31 December 2028
Sites11 locations across France, Italy, Finland, United Kingdom, Germany, Canada, United States, Brazil

Conditions studied

Sponsor

Jaeb Center for Health Research — full company profile →

Who can join

12 and older, any sex, with Gyrate Atrophy or Gyrata of Choroid and Retina; Atrophy. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

The Gyrate Atrophy Ocular and Systemic Study characterizes the natural history of ornithine levels and retinal degeneration (RD) associated with disease-causing OAT variants in the presence of standard care dietary treatment regimens over 4 years. The research goal is to understand the impact of OAT mutations on plasma ornithine levels and retinal degeneration. Funding Source- FDA OOPD

Publications & conference data

3 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Inherited Retinal Degenerations and Non-Neovascular Age-Related Macular Degeneration: Progress and Unmet Needs.
    Duncan JL, Bowman A, Laster A, Gelfman C, et al · · 2024 · cited 5× · PMID 39688851 · DOI 10.1167/tvst.13.12.28
  2. Molecular and cellular mechanisms underlying gyrate atrophy: Why is the retina primarily affected?
    Buijs MJN, Balfoort BM, Brands MM, Ten Asbroek ALMA, et al · · 2025 · cited 2× · PMID 40192087 · DOI 10.1111/aos.17498
  3. A novel phenotype-guided genome analysis pipeline for variant discovery.
    Ahmed L, Tavares E, Li JM, Ahmed K, et al · · 2026 · PMID 41904215 · DOI 10.1038/s41525-026-00557-0

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Other Jaeb Center for Health Research trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT05312736.

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