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NCT05291962

Procedural Sedation for Pediatric Patients With Spinal Muscular Atrophy

Completed Last updated 23 March 2022
What this trial tests

trial testing Retrospective observational study in Muscular Atrophy, Spinal in 14 participants. Completed in 31 January 2022.

Timeline
1 January 2022
Primary endpoint
31 January 2022
31 January 2022

Quick facts

Lead sponsorAnkara City Hospital Bilkent
StatusCompleted
Study typeOBSERVATIONAL
Enrollment14
Start date1 January 2022
Primary completion31 January 2022
Estimated completion31 January 2022
Sites1 location across Turkey (Türkiye)

Drugs / interventions tested

Conditions studied

Sponsor

Ankara City Hospital Bilkent

Who can join

Under 18, any sex, with Muscular Atrophy, Spinal or Child, Only. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

Background and Aim: Spinal muscular atrophy (SMA) is a neuromuscular disease characterized by progressive symmetrical weakness and atrophy of proximal muscles causing from degeneration of anterior horn cells of spinal cord. Nusinersen must be administered intrathecally and this treatment is specially for spinal muscular atrophy. Procedural sedation is commonly enough for intrathecal treatment in children. In this retrospective study, the investigators aimed to present our experience in procedural sedation for the intrathecal treatment of patients with SMA 1,2 and 3 in our hospital.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Pharmacological Therapies of Spinal Muscular Atrophy: A Narrative Review of Preclinical, Clinical-Experimental, and Real-World Evidence.
    Crisafulli S, Boccanegra B, Vitturi G, Trifirò G, et al · · 2023 · cited 11× · PMID 37891814 · DOI 10.3390/brainsci13101446

Verify or expand the search:

Other trials of Retrospective observational study

Trials testing the same drug.

Other recruiting trials for Muscular Atrophy, Spinal

Currently open trials in the same condition.

Other Ankara City Hospital Bilkent trials

Trials by the same sponsor.

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Data sources for this page

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