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NCT05154851

HBCMD01- Expanded Access for the Treatment of Congenital Muscular Dystrophy.

NO LONGER AVAILABLE Last updated 29 September 2025
What this trial tests

trial testing HB-adMSCs in Congenital Muscular Dystrophy Due to Lamin A/C Mutation. No longer available.

Quick facts

Lead sponsorHope Biosciences Research Foundation
StatusNO LONGER AVAILABLE
Study typeEXPANDED_ACCESS
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Hope Biosciences Research Foundation

Who can join

Eligibility, any sex, with Congenital Muscular Dystrophy Due to Lamin A/C Mutation. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

This individual patient expanded access IND is requested for a patient diagnosed with LMNA-related congenital muscular dystrophy (L-CMD). In this expanded access, the patient will receive the investigational product through 14 intravenous infusions, followed by Follow-Up visit and an End of Study.

Publications & conference data

No peer-reviewed publications indexed yet for this trial.

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Other trials of HB-adMSCs

Trials testing the same drug.

Other Hope Biosciences Research Foundation trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT05154851.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing