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NCT05141357: HBI-8000

A Study of HBI-8000 (Tucidinostat) With Pembrolizumab in Non-Small Cell Lung Cancer

Terminated Phase 2 Results posted Last updated 24 December 2025
What this trial tests

Phase 2 trial testing HBI-8000 in combination with pembrolizumab in Non Small Cell Lung Cancer in 5 participants. Terminated before completion.

Timeline
15 February 2022
Primary endpoint
19 April 2023
19 April 2023

Quick facts

Lead sponsorHUYABIO International, LLC.
PhasePhase 2
StatusTerminated
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment5
Start date15 February 2022
Primary completion19 April 2023
Estimated completion19 April 2023
Sites7 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

HUYABIO International, LLC. — full company profile →

Who can join

18 and older, any sex, with Non Small Cell Lung Cancer. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Safety and Tolerability of HBI-8000 When Administered in Combination With Standard Dose and Regimen of Pembrolizumab Primary · From the start of treatment until 30 days after the last dose of HBI-8000, up to approximately 13 months

Number of participants experiencing treatment-emergent adverse events (TEAEs) graded according to the National Cancer Institute Common Terminology Criteria for Adverse Events (NCI-CTCAE) v5.0

GroupValue95% CI
HBI-8000 in Combination With Pembrolizumab5
HBI-8000 in Combination With Pembrolizumab0

Adverse events — posted to ClinicalTrials.gov

Time frame: Up to approximately 13 months. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

HBI-8000 in Combination With Pembrolizumab
Serious: 3/5 (60%)
Deaths: 0/5

Serious adverse events (10 terms)

ReactionSystemHBI-8000 in Combination Wi…
DiarrhoeaGastrointestinal disorders
Gastrointestinal hemorrhageGastrointestinal disorders
IleusGastrointestinal disorders
COVID-19 pneumoniaInfections and infestations
CellulitisInfections and infestations
PneumoniaInfections and infestations
Chronic obstructive pulmonary diseaseRespiratory, thoracic and mediastinal disorders
HypoxiaRespiratory, thoracic and mediastinal disorders
Pleural effusionRespiratory, thoracic and mediastinal disorders
HypotensionVascular disorders
Other adverse events (81 terms — click to expand)

ReactionSystemHBI-8000 in Combination Wi…
DiarrhoeaGastrointestinal disorders
Decreased appetiteMetabolism and nutrition disorders
AnaemiaBlood and lymphatic system disorders
Iron deficiency anemiaBlood and lymphatic system disorders
ThrombocytopeniaBlood and lymphatic system disorders
NauseaGastrointestinal disorders
Sinus tachycardiaCardiac disorders
VomitingGastrointestinal disorders
FatigueGeneral disorders
Oedema peripheralGeneral disorders
PneumoniaInfections and infestations
Amylase increasedInvestigations
Lipase increasedInvestigations
Platelet count decreasedInvestigations
Weight decreasedInvestigations
White blood cell count decreasedInvestigations
DehydrationMetabolism and nutrition disorders
HypokalaemiaMetabolism and nutrition disorders
Musculoskeletal chest painMusculoskeletal and connective tissue disorders
DizzinessNervous system disorders
CoughRespiratory, thoracic and mediastinal disorders
DyspnoeaRespiratory, thoracic and mediastinal disorders
PruritusSkin and subcutaneous tissue disorders
Atrial fibrillationCardiac disorders
Cardiac failureCardiac disorders
Pericardial effusionCardiac disorders
TachycardiaCardiac disorders
Ear painEar and labyrinth disorders
Middle ear effusionEar and labyrinth disorders
HypothyroidismEndocrine disorders
Periorbital painEye disorders
Vision blurredEye disorders
Abdominal distensionGastrointestinal disorders
Anal incontinenceGastrointestinal disorders
ConstipationGastrointestinal disorders
Feces discoloredGastrointestinal disorders
Gastrooesophageal reflux diseaseGastrointestinal disorders
Gastrointestinal disorderGastrointestinal disorders
Gastrointestinal haemorrhageGastrointestinal disorders
Lip painGastrointestinal disorders

Most-reported serious reactions: Diarrhoea, Gastrointestinal hemorrhage, Ileus, COVID-19 pneumonia, Cellulitis, Pneumonia, Chronic obstructive pulmonary disease, Hypoxia.

Data from ClinicalTrials.gov NCT05141357 adverse events section.

Sponsor's own description

A Phase 2 Study to Assess the Safety and Efficacy of HBI-8000 in Combination with Pembrolizumab for Advanced or Metastatic Non-Small Cell Lung Cancer (NSCLC)

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Epigenetic regulation in the tumor microenvironment: molecular mechanisms and therapeutic targets.
    Yang J, Xu J, Wang W, Zhang B, et al · · 2023 · cited 251× · PMID 37217462 · DOI 10.1038/s41392-023-01480-x
  2. Therapeutic potential of tucidinostat, a subtype-selective HDAC inhibitor, in cancer treatment.
    Sun Y, Hong JH, Ning Z, Pan D, et al · · 2022 · cited 58× · PMID 36120308 · DOI 10.3389/fphar.2022.932914
  3. Super-enhancers complexes zoom in transcription in cancer.
    Wang M, Chen Q, Wang S, Xie H, et al · · 2023 · cited 32× · PMID 37501079 · DOI 10.1186/s13046-023-02763-5
  4. Epi-immunotherapy for cancers: rationales of epi-drugs in combination with immunotherapy and advances in clinical trials.
    Xu Y, Li P, Liu Y, Xin D, et al · · 2022 · cited 29× · PMID 35642676 · DOI 10.1002/cac2.12313
  5. The epigenetic hallmarks of immune cells in cancer.
    Ji Y, Xiao C, Fan T, Deng Z, et al · · 2025 · cited 28× · PMID 40038722 · DOI 10.1186/s12943-025-02255-4
  6. Enhancing HCC Treatment: innovatively combining HDAC2 inhibitor with PD-1/PD-L1 inhibition.
    Han R, Ling C, Wang Y, Lu L. · · 2023 · cited 23× · PMID 37716965 · DOI 10.1186/s12935-023-03051-0
  7. Epigenetic regulation of stem cells in lung cancer oncogenesis and therapy resistance.
    Wu J, Feng J, Zhang Q, He Y, et al · · 2023 · cited 10× · PMID 37144123 · DOI 10.3389/fgene.2023.1120815
  8. Targeting Epigenetic Alterations Linked to Cancer-Associated Fibroblast Phenotypes in Lung Cancer.
    Papavassiliou KA, Sofianidi AA, Gogou VA, Papavassiliou AG. · · 2024 · cited 3× · PMID 39682163 · DOI 10.3390/cancers16233976

Verify or expand the search:

Other recruiting trials for Non Small Cell Lung Cancer

Currently open trials in the same condition.

Other HUYABIO International, LLC. trials

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT05141357.

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