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NCT04921969

A Study to Assess the Efficacy and Safety of Ruxolitinib Cream in Children With Atopic Dermatitis (TRuE-AD3)

Completed Phase 3 Results posted Last updated 28 March 2025
What this trial tests

Phase 3 trial testing Ruxolitinib in Atopic Dermatitis in 330 participants. Completed in 8 April 2024.

Timeline
19 July 2021
Primary endpoint
10 May 2023
8 April 2024

Quick facts

Lead sponsorIncyte Corporation
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingtriple
Primary purposetreatment
Enrollment330
Start date19 July 2021
Primary completion10 May 2023
Estimated completion8 April 2024
Sites67 locations across Canada, United States

Drugs / interventions tested

Conditions studied

Sponsor

Incyte Corporation — full company profile →

Who can join

Adults 2 to 11, any sex, with Atopic Dermatitis. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

VC Period: Percentage of Participants Who Achieved Investigator's Global Assessment - Treatment Success (IGA-TS) at Week 8 Primary · Baseline to Week 8

The IGA is an overall eczema severity rating on a 5-point scale ranging from 0 (clear skin) to 4 (severe disease). The score is based on an overall assessment of the degree of erythema, induration/papulation, and oozing/crusting. The IGA-TS is defined as an IGA score of 0 (clear skin) or 1 (almost clear skin) with ≥2 grade improvement from Baseline.

GroupValue95% CI
VC Period: Vehicle Cream BID10.84.4 – 20.9
VC Period: Ruxolitinib 0.75% Cream BID36.628.4 – 45.3
VC Period: Ruxolitinib 1.5% Cream BID56.547.6 – 65.1
VC Period: Percentage of Participants With a ≥4-Point Improvement in Itch Numerical Rating Scale (NRS) Score From Baseline to Week 8 Secondary · Baseline to Week 8

The Itch NRS is a daily participant-reported measure (24-hour recall) of the worst level of itch intensity using a diary. Participants were asked to rate the itching severity because of their AD by selecting the number from 0 (no itch) to 10 (worst imaginable itch) that best described their worst level of itching in the past 24 hours.

GroupValue95% CI
VC Period: Vehicle Cream BID29.715.873 – 46.980
VC Period: Ruxolitinib 0.75% Cream BID37.526.919 – 49.035
VC Period: Ruxolitinib 1.5% Cream BID43.432.083 – 55.288
VC Period: Percentage of Participants With a ≥4-Point Improvement in Itch NRS Score From Baseline to Day 7 (Week 1) Secondary · Baseline to Day 7 (Week 1)

The Itch NRS is a daily participant-reported measure (24-hour recall) of the worst level of itch intensity using a diary. Participants were asked to rate the itching severity because of their AD by selecting the number from 0 (no itch) to 10 (worst imaginable itch) that best described their worst level of itching in the past 24 hours.

GroupValue95% CI
VC Period: Vehicle Cream BID11.5
VC Period: Ruxolitinib 0.75% Cream BID23.5
VC Period: Ruxolitinib 1.5% Cream BID28.2
VC Period: Percentage of Participants With a ≥4-Point Improvement in Itch NRS Score From Baseline to Day 3 Secondary · Baseline to Day 3

The Itch NRS is a daily participant-reported measure (24-hour recall) of the worst level of itch intensity using a diary. Participants were asked to rate the itching severity because of their AD by selecting the number from 0 (no itch) to 10 (worst imaginable itch) that best described their worst level of itching in the past 24 hours.

GroupValue95% CI
VC Period: Vehicle Cream BID4.1
VC Period: Ruxolitinib 0.75% Cream BID14.6
VC Period: Ruxolitinib 1.5% Cream BID12.1
VC Period: Number of Participants With Any Treatment-emergent Adverse Event (TEAE) Secondary · from Baseline up to Week 8

An adverse event was defined as any untoward medical occurrence associated with the use of a drug in humans, whether or not it was considered drug related. An AE could therefore be any unfavorable or unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of study cream. A TEAE is defined as any AE either reported for the first time or the worsening of a pre-existing event after the first dose of study drug until the end of the safety follow-up.

GroupValue95% CI
VC Period: Vehicle Cream BID18
VC Period: Ruxolitinib 0.75% Cream BID35
VC Period: Ruxolitinib 1.5% Cream BID48
LTS Period: Number of Participants With Any TEAE Secondary · From Week 8 up to Week 56

An adverse event was defined as any untoward medical occurrence associated with the use of a drug in humans, whether or not it was considered drug related. An AE could therefore be any unfavorable or unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of study cream. A TEAE is defined as any AE either reported for the first time or the worsening of a pre-existing event after the first dose of study drug until the end of the safety follow-up.

GroupValue95% CI
LTS Period: Vehicle Cream to Ruxolitinib 0.75% Cream BID9
LTS Period: Vehicle Cream to Ruxolitinib 1.5% Cream BID13
LTS Period: Ruxolitinib 0.75% Cream BID57
LTS Period: Ruxolitinib 1.5% Cream BID63
VC Period: Number of Participants With Any Grade 3 or Higher TEAE Secondary · from Baseline up to Week 8

A TEAE is defined as any AE either reported for the first time or the worsening of a pre-existing event after the first dose of study drug until the end of the safety follow-up. The severity of AEs will be assessed using Common Terminology Criteria for Adverse Events (CTCAE) v5.0 Grades 1 through 5. The investigator made an assessment of intensity for each AE and SAE reported during the study and assigned it to 1 of the following categories: Grade 1: mild; asymptomatic or mild symptoms; clinical or diagnostic observations only; treatment not indicated. Grade 2: moderate; minimal, local, or non

GroupValue95% CI
VC Period: Vehicle Cream BID0
VC Period: Ruxolitinib 0.75% Cream BID0
VC Period: Ruxolitinib 1.5% Cream BID2
LTS Period: Number of Participants With Any Grade 3 or Higher TEAE Secondary · From Week 12 up to Week 56

A TEAE is defined as any AE either reported for the first time or the worsening of a pre-existing event after the first dose of study drug until the end of the safety follow-up. The severity of AEs will be assessed using Common Terminology Criteria for Adverse Events (CTCAE) v5.0 Grades 1 through 5. The investigator made an assessment of intensity for each AE and SAE reported during the study and assigned it to 1 of the following categories: Grade 1: mild; asymptomatic or mild symptoms; clinical or diagnostic observations only; treatment not indicated. Grade 2: moderate; minimal, local, or non

GroupValue95% CI
LTS Period: Vehicle Cream to Ruxolitinib 0.75% Cream BID0
LTS Period: Vehicle Cream to Ruxolitinib 1.5% Cream BID0
LTS Period: Ruxolitinib 0.75% Cream BID3
LTS Period: Ruxolitinib 1.5% Cream BID3
VC Period: Percentage of Participants Who Achieved IGA-TS at Weeks 2 and 4 Secondary · Baseline to Weeks 2 and 4

The IGA is an overall eczema severity rating on a 5-point scale ranging from 0 (clear skin) to 4 (severe disease). The score is based on an overall assessment of the degree of erythema, induration/papulation, and oozing/crusting. The IGA-TS is defined as an IGA score of 0 (clear skin) or 1 (almost clear skin) with ≥2 grade improvement from Baseline.

Week 2
GroupValue95% CI
VC Period: Vehicle Cream BID4.61.0 – 12.9
VC Period: Ruxolitinib 0.75% Cream BID24.617.6 – 32.8
VC Period: Ruxolitinib 1.5% Cream BID35.127.0 – 43.9
Week 4
GroupValue95% CI
VC Period: Vehicle Cream BID12.35.5 – 22.8
VC Period: Ruxolitinib 0.75% Cream BID36.628.4 – 45.3
VC Period: Ruxolitinib 1.5% Cream BID48.139.3 – 57.0
VC Period: Percentage of Participants With a ≥4-Point Improvement in Itch NRS Score From Baseline to Week 2 and 4 Secondary · Baseline to Weeks 2 and 4

The Itch NRS is a daily participant-reported measure (24-hour recall) of the worst level of itch intensity using a diary. Participants were asked to rate the itching severity because of their AD by selecting a number from 0 (no itch) to 10 (worst imaginable itch) that best described their worst level of itching in the past 24 hours.

Week 2
GroupValue95% CI
VC Period: Vehicle Cream BID8.11.704 – 21.910
VC Period: Ruxolitinib 0.75% Cream BID23.814.945 – 34.578
VC Period: Ruxolitinib 1.5% Cream BID23.714.682 – 34.824
Week 4
GroupValue95% CI
VC Period: Vehicle Cream BID10.83.025 – 25.418
VC Period: Ruxolitinib 0.75% Cream BID33.823.553 – 45.191
VC Period: Ruxolitinib 1.5% Cream BID36.826.058 – 48.686
VC Period: Percentage of Participants Who Achieved Eczema Area and Severity Index 75 (EASI75) at Weeks 2, 4, and 8 Secondary · Baseline to Weeks 2, 4, and 8

The EASI scoring system examines 4 areas of the body (head/neck, trunk, upper limbs, and lower limbs) and weights them for participants of ≥8 years of age. Each of the 4 body regions is assessed separately for erythema (E), induration/papulation/edema (I), excoriations (Ex), and lichenification (l), each on a scale of 0 to 3 (0 = none, absent; 1 = mild; 2 = moderate; 3 = severe). Half scores are allowed between severities 1, 2, and 3. The final EASI score was obtained by weight-averaging these 4 scores and will range from 0 to 72; the severity strata are as follows: 0 = clear; 0.1 to 1.0 = alm

Week 2
GroupValue95% CI
VC Period: Vehicle Cream BID6.21.702 – 15.013
VC Period: Ruxolitinib 0.75% Cream BID35.827.728 – 44.556
VC Period: Ruxolitinib 1.5% Cream BID43.534.876 – 52.447
Week 4
GroupValue95% CI
VC Period: Vehicle Cream BID12.35.466 – 22.819
VC Period: Ruxolitinib 0.75% Cream BID53.044.178 – 61.658
VC Period: Ruxolitinib 1.5% Cream BID62.653.718 – 70.890
Week 8
GroupValue95% CI
VC Period: Vehicle Cream BID15.47.632 – 26.478
VC Period: Ruxolitinib 0.75% Cream BID51.542.708 – 60.210
VC Period: Ruxolitinib 1.5% Cream BID67.258.432 – 75.123
VC Period: Time to Achieve Itch NRS Score Improvement of at Least 2 or 4 Points Secondary · up to Week 8

The Itch NRS is a daily participant-reported measure (24-hour recall), of the worst level of itch intensity using a diary. Participants are asked to rate the itching severity because of their AD by selecting a number from 0 (no itch) to 10 (worst imaginable itch) that best describes their worst level of itching in the past 24 hours. Kaplan-Meier estimation method was used for analyses.

Improvement of at least 2 points
GroupValue95% CI
VC Period: Vehicle Cream BID6.04.0 – 21.0
VC Period: Ruxolitinib 0.75% Cream BID4.03.0 – 5.0
VC Period: Ruxolitinib 1.5% Cream BID5.03.0 – 6.0
Improvement of at least 4 points
GroupValue95% CI
VC Period: Vehicle Cream BID23.013.0 – NA
VC Period: Ruxolitinib 0.75% Cream BID11.09.0 – 20.0
VC Period: Ruxolitinib 1.5% Cream BID13.09.0 – 17.0

Adverse events — posted to ClinicalTrials.gov

Time frame: up to 60 weeks. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Vehicle Cream BID
Serious: 0/65 (0%)
Deaths: 0/65
Ruxolitinib 0.75% Cream BID
Serious: 0/159 (0%)
Deaths: 0/159
Ruxolitinib 1.5% Cream BID
Serious: 3/154 (2%)
Deaths: 0/154

Serious adverse events (2 terms)

ReactionSystemVehicle Cream BIDRuxolitinib 0.75% Cream BIDRuxolitinib 1.5% Cream BID
AsthmaRespiratory, thoracic and mediastinal disorders
Eczema herpeticumInfections and infestations
Other adverse events (5 terms — click to expand)

ReactionSystemVehicle Cream BIDRuxolitinib 0.75% Cream BIDRuxolitinib 1.5% Cream BID
Upper respiratory tract infectionInfections and infestations
NasopharyngitisInfections and infestations
COVID-19Infections and infestations
PyrexiaGeneral disorders
Pharyngitis streptococcalInfections and infestations

Most-reported serious reactions: Asthma, Eczema herpeticum.

Data from ClinicalTrials.gov NCT04921969 adverse events section.

Sponsor's own description

The purpose of the study is to assess the efficacy and safety of ruxolitinib cream in children with Atopic Dermatitis. This is a randomized, double-blind, Vehicle Controlled study. Participants will be randomized 2:2:1 to blinded treatment with ruxolitinib cream 0.75% ,1.5% , or vehicle cream, with stratification by baseline IGA score and age. At Week 8, efficacy will be evaluated. Participants who complete Week 8 assessments with no additional safety concerns will continue into the 44-week Long Term Safety (LTS) period with the same treatment regimen, except those initially randomized to vehicle cream will be rerandomized (1:1) in a blinded manner to 1 of the 2 active treatment groups (ruxolitinib cream 0.75% or 1.5%).

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. The translational revolution in atopic dermatitis: the paradigm shift from pathogenesis to treatment.
    Facheris P, Jeffery J, Del Duca E, Guttman-Yassky E. · · 2023 · cited 150× · PMID 36928371 · DOI 10.1038/s41423-023-00992-4
  2. STAT proteins: a kaleidoscope of canonical and non-canonical functions in immunity and cancer.
    Awasthi N, Liongue C, Ward AC. · · 2021 · cited 97× · PMID 34809691 · DOI 10.1186/s13045-021-01214-y
  3. New and Upcoming Topical Treatments for Atopic Dermatitis: A Review of the Literature.
    Sideris N, Paschou E, Bakirtzi K, Kiritsi D, et al · · 2022 · cited 28× · PMID 36078904 · DOI 10.3390/jcm11174974
  4. Topical anti-inflammatory treatments for eczema: network meta-analysis.
    Lax SJ, Van Vogt E, Candy B, Steele L, et al · · 2024 · cited 22× · PMID 39105474 · DOI 10.1002/14651858.cd015064.pub2
  5. Novel Therapeutic Strategies in the Topical Treatment of Atopic Dermatitis.
    Pinto LM, Chiricozzi A, Calabrese L, Mannino M, et al · · 2022 · cited 17× · PMID 36559261 · DOI 10.3390/pharmaceutics14122767
  6. Efficacy, Safety, and Long-Term Disease Control of Ruxolitinib Cream Among Adolescents with Atopic Dermatitis: Pooled Results from Two Randomized Phase 3 Studies.
    Eichenfield LF, Simpson EL, Papp K, Szepietowski JC, et al · · 2024 · cited 12× · PMID 38698175 · DOI 10.1007/s40257-024-00855-2
  7. Efficacy and safety of ruxolitinib cream in children aged 2 to 11 years with atopic dermatitis: Results from TRuE-AD3, a phase 3, randomized double-blind study.
    Eichenfield LF, Stein Gold LF, Simpson EL, Zaenglein AL, et al · · 2025 · cited 8× · PMID 40378883 · DOI 10.1016/j.jaad.2025.05.1385
  8. Ruxolitinib Cream Monotherapy Improved Symptoms and Quality of Life in Adults and Adolescents with Mild-to-Moderate Atopic Dermatitis: Patient-Reported Outcomes from Two Phase III Studies.
    Simpson EL, Augustin M, Thaçi D, Misery L, et al · · 2025 · cited 8× · PMID 39546129 · DOI 10.1007/s40257-024-00901-z

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Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04921969.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing