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NCT04873232: REGAiN-1B

A 6-Month Extension Study of VMDN-003-2 to Assess Engensis in Participants With Painful Diabetic Peripheral Neuropathy

Completed Phase 3 Results posted Last updated 9 October 2025
What this trial tests

Phase 3 trial testing Engensis in Diabetic Peripheral Neuropathy in 106 participants. Completed in 23 July 2024.

Timeline
17 May 2021
Primary endpoint
14 September 2023
23 July 2024

Quick facts

Lead sponsorHelixmith Co., Ltd.
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationnon randomized
Designparallel
Maskingquadruple
Primary purposetreatment
Enrollment106
Start date17 May 2021
Primary completion14 September 2023
Estimated completion23 July 2024
Sites16 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

Helixmith Co., Ltd. — full company profile →

Who can join

18 and older, any sex, with Diabetic Peripheral Neuropathy. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

To Evaluate the Efficacy of Intramuscular Administration of Engensis on Reducing Pain in Participants With Painful Diabetic Peripheral Neuropathy in the Feet and Lower Legs as Compared to Placebo Primary · From the 7 days prior to the Day 0 Visit (Study VMDN-003-2, NCT04469270), Day 270, to the 7 days prior to the Day 365 Visit in the intent-to-treat population

Change in the means of the Average Daily Pain Scores from the full Brief Pain Inventory for Diabetic Peripheral Neuropathy from the 7 days prior to the Day 0 Visit (Study VMDN-003-2) to the 7 days prior to the Day 365 Visit in the intent-to-treat population. The mean of the Average Daily Pain Scores are used for the primary endpoint recorded in the 7 days prior to the Days 270 and 365/ET Visits. The Brief Pain Inventory for Diabetic Peripheral Neuropathy scale is a 0 to 10 point scale with 10 being Pain as bad as you can imagine. The mean of at least 5 daily pain scores recorded for Question

Change from Baseline to Day 270
GroupValue95% CI
Engensis-2.27± 2.083
Placebo-2.62± 2.087
Change from Baseline to 7 Days prior to the Day 365 visit
GroupValue95% CI
Engensis-2.53± 2.173
Placebo-2.78± 2.126
To Evaluate the Efficacy of IM Administration of Engensis on the Worst Pain in Participants With Painful Diabetic Peripheral Neuropathy in the Feet and Lower Legs as Compared to Placebo Secondary · From the 7 days prior to the Day 0 Visit (Study VMDN-003-2) to the 7 days prior to the Day 365 Visit for Engensis compared to Placebo

Change in the means of the Worst Pain Scores from the full Brief Pain Inventory for Diabetic Peripheral Neuropathy from the 7 days prior to Day 0 Visit (Study VMDN-003-2), to Day 270, and 7 days prior to the Day 365 Visit for Engensis compared to Placebo. The Brief Pain Inventory for Diabetic Peripheral Neuropathy scale is a 0 to 10 point scale with 10 being Pain as bad as you can imagine. The mean of at least 5 worst daily pain scores recorded for Question 3 of the Brief Pain Inventory for Diabetic Peripheral Neuropathy in the electronic diary during the 7 days prior to the Visits on Days 27

Change from Baseline to Day 270
GroupValue95% CI
Engensis-2.50± 2.376
Placebo-2.94± 2.664
Change from Baseline to Day 365
GroupValue95% CI
Engensis-2.65± 2.485
Placebo-3.19± 2.454
To Evaluate the Safety of IM Administration of Engensis in the Number of Participants With Painful DPN in the Feet and Lower Legs as Compared to Placebo Secondary · From Day 0 Visit (Study VMDN-003-2) to the Day 365 Visit

Number of participants with adverse events and serious adverse events for Engensis compared to Placebo, including the number of participants with clinically significant laboratory values for Engensis compared to Placebo

GroupValue95% CI
Engensis16
Placebo22
To Evaluate the Efficacy of Administration of Engensis on Reducing Pain in Participants With Painful Diabetic Peripheral Neuropathy in the Feet and Lower Legs Secondary · From the 7 days prior to the Day 0 Visit (Study VMDN-003-2), to the 7 days prior to the Day 270 Visit, and 7 days prior to the Day 365 Visit

Proportion of Responders (≥ 50% reduction in the Average Daily Pain Scores from the full Brief Pain Inventory for Diabetic Peripheral Neuropathy) from the 7 days prior to the Day 0 Visit (Study VMDN-003-2) to the 7 days prior to the Day 270 Visit and the 7 days prior to the Day 365 Visit for Engensis compared to Placebo.

Responders with ≥50% reduction by Day 270
GroupValue95% CI
Engensis17
Placebo27
Responders with ≥50% reduction by Day 365
GroupValue95% CI
Engensis16
Placebo27

Adverse events — posted to ClinicalTrials.gov

Time frame: Adverse events that started after the Day 180 Visit (Day 180 Visit date +1 day), and recorded up to the end of the study visit, Day 365.. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Engensis
Serious: 3/49 (6%)
Deaths: 0/49
Placebo
Serious: 6/57 (11%)
Deaths: 0/57

Serious adverse events (11 terms)

ReactionSystemEngensisPlacebo
Acute coronary syndromeCardiac disorders
Angina unstableCardiac disorders
Atrial fibrillationCardiac disorders
Atrioventricular block completeCardiac disorders
Coronary artery stenosisCardiac disorders
CellulitisInfections and infestations
Gastroenteritis viralInfections and infestations
Post procedural cellulitisInfections and infestations
DehydrationMetabolism and nutrition disorders
SyncopeNervous system disorders
AsthmaRespiratory, thoracic and mediastinal disorders
Other adverse events (54 terms — click to expand)

ReactionSystemEngensisPlacebo
COVID-19Infections and infestations
InfluenzaInfections and infestations
HypertriglyceridaemiaMetabolism and nutrition disorders
CystitisInfections and infestations
Eye infectionInfections and infestations
Gastoenteritis viralInfections and infestations
NasopharyngitisInfections and infestations
Post procedural cellulitisInfections and infestations
Postoperative wound infectionInfections and infestations
Tinea pedisInfections and infestations
Tooth abscessInfections and infestations
Urinary tract infectionInfections and infestations
Acute coronary syndromeCardiac disorders
Angina unstableCardiac disorders
Atrial fibrillationCardiac disorders
Atrial flutterCardiac disorders
Atrioventricular block completeCardiac disorders
Bundle branch block leftCardiac disorders
Coronary artery stenosisCardiac disorders
Diabetic retinopathyEye disorders
Conjunctival oedemaEye disorders
Dry age-related macular degenerationEye disorders
Ocular hypertensionEye disorders
Lipase increasedInvestigations
Amylase increasedInvestigations
Blood creatinine abnormalInvestigations
Blood urea abnormalInvestigations
Electrocardiogram QT prolongedInvestigations
Diabetes mellitus inadequate controlMetabolism and nutrition disorders
DehydrationMetabolism and nutrition disorders
HypoglycaemiaMetabolism and nutrition disorders
AnaemiaBlood and lymphatic system disorders
EosinophiliaBlood and lymphatic system disorders
Diabetic neuropathyNervous system disorders
HypoaesthesiaNervous system disorders
Sinus headacheNervous system disorders
SyncopeNervous system disorders
Chronic kidney diseaseRenal and urinary disorders
Renal impairmentRenal and urinary disorders
Urethral stenosisRenal and urinary disorders

Most-reported serious reactions: Acute coronary syndrome, Angina unstable, Atrial fibrillation, Atrioventricular block complete, Coronary artery stenosis, Cellulitis, Gastroenteritis viral, Post procedural cellulitis.

Data from ClinicalTrials.gov NCT04873232 adverse events section.

Sponsor's own description

To evaluate the durability of efficacy and long-term safety of intramuscular administration of Engensis or Placebo that was administered in the double-blind, randomized, VMDN-003-2 Placebo-controlled Phase 3 Study.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. New pharmacological agents and emerging therapeutic targets for painful diabetic neuropathy.
    Panou T, Papanas N, Kempler P. · · 2026 · PMID 41987888 · DOI 10.3389/fendo.2026.1788702

Verify or expand the search:

Other trials of Engensis

Trials testing the same drug.

Other recruiting trials for Diabetic Peripheral Neuropathy

Currently open trials in the same condition.

Other Helixmith Co., Ltd. trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04873232.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing