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NCT04831281

ATH-1017 Treatment in Subjects With Parkinson's Disease Dementia or Dementia With Lewy Bodies (SHAPE Trial)

Terminated Phase 2 Results posted Last updated 4 March 2025
What this trial tests

Phase 2 trial testing ATH-1017 in Parkinson Disease Dementia in 28 participants. Terminated before completion.

Timeline
20 January 2022
Primary endpoint
19 April 2023
19 April 2023

Quick facts

Lead sponsorLeonaBio
PhasePhase 2
StatusTerminated
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposetreatment
Enrollment28
Start date20 January 2022
Primary completion19 April 2023
Estimated completion19 April 2023
Sites10 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

LeonaBio — full company profile →

Who can join

Adults 40 to 85, any sex, with Parkinson Disease Dementia or Dementia With Lewy Bodies. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Global Statistical Test (GST) Score at Baseline Primary · Baseline

The Global Statistical Test (GST) score is a composite of the change from baseline (CFB) z-scores to Week 26 in the Alzheimer's Disease Assessment Scale - Cognitive Subscale, 13-Item Version (ADAS-Cog13; range 0-85; higher scores indicate greater impairment) and Event Related Potential P300 Latency (ERP P300; longer latency (milliseconds) indicates greater impairment). This composite approach was used to assess overall change in disease status and treatment effects of ATH-1017. The GST score was defined as a single outcome variable based on standardizing and combining individual patient-level

GroupValue95% CI
Placebo-0.222± 0.6365
ATH-1017 40 mg0.332± 0.6337
ATH-1017 70 mg-0.036± 1.0050
Event-related Potential (ERP) P300 Latency at Baseline Secondary · Baseline

ERP P300 was a method of recording brain activity elicited by external stimuli, for example (e.g.), an oddball auditory stimulus, particularly of working memory access. The participant had to perform a task related to auditory stimuli in order to assess the P300 component (latency). The stimulus consisted of an oddball paradigm with 2 sound stimuli. Stimuli were presented through headphones and auditory stimulation for P300 was assessed in a recording lasting up to 10 minutes. It was calculated as the average across the pre-dose values at Baseline visit.

GroupValue95% CI
Placebo381.84± 51.739
ATH-1017 40 Milligrams (mg)373.19± 18.669
ATH-1017 70 mg367.84± 45.635
Alzheimer's Disease Assessment Scale-Cognitive Subscale (ADAS-Cog13) at Baseline Secondary · Baseline

The Alzheimer's Disease Assessment Scale - Cognitive Subscale, 13-Item Version (ADAS-Cog13) is designed to measure cognitive symptom change. The test comprises 9 performance items and 4 clinician-rated items (total score ranging from 0 to 85). Higher scores indicate more severe cognitive impairment.

GroupValue95% CI
Placebo16.9± 6.94
ATH-1017 40 Milligrams (mg)29.7± 10.03
ATH-1017 70 mg23.8± 11.49

Adverse events — posted to ClinicalTrials.gov

Time frame: Up to Week 30. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Placebo
Serious: 1/9 (11%)
Deaths: 0/9
ATH-1017 40 Milligrams (mg)
Serious: 1/9 (11%)
Deaths: 0/9
ATH-1017 70 mg
Serious: 1/10 (10%)
Deaths: 1/10

Serious adverse events (3 terms)

ReactionSystemPlaceboATH-1017 40 Milligrams (mg)ATH-1017 70 mg
Femoral neck fractureInjury, poisoning and procedural complications
Subarachnoid haemorrhageNervous system disorders
Psychotic symptomPsychiatric disorders
Other adverse events (58 terms — click to expand)

ReactionSystemPlaceboATH-1017 40 Milligrams (mg)ATH-1017 70 mg
Injection site reactionGeneral disorders
FallInjury, poisoning and procedural complications
Injection site noduleGeneral disorders
Injection site painGeneral disorders
Urinary tract infectionInfections and infestations
AnaemiaBlood and lymphatic system disorders
PalpitationsCardiac disorders
TinnitusEar and labyrinth disorders
DiarrhoeaGastrointestinal disorders
DysphagiaGastrointestinal disorders
Intestinal obstructionGastrointestinal disorders
NauseaGastrointestinal disorders
VomitingGastrointestinal disorders
Injection site pruritusGeneral disorders
Injection site warmthGeneral disorders
FatigueGeneral disorders
Gait disturbanceGeneral disorders
Injection site hypersensitivityGeneral disorders
Injection site rashGeneral disorders
Injection site swellingGeneral disorders
OedemaGeneral disorders
PainGeneral disorders
COVID-19Infections and infestations
NasopharyngitisInfections and infestations
Herpes pharyngitisInfections and infestations
InfluenzaInfections and infestations
Lip infectionInfections and infestations
Bone contusionInjury, poisoning and procedural complications
Femoral neck fractureInjury, poisoning and procedural complications
Joint injuryInjury, poisoning and procedural complications
Lip injuryInjury, poisoning and procedural complications
Procedural nauseaInjury, poisoning and procedural complications
Skin lacerationInjury, poisoning and procedural complications
Alanine aminotransferase increasedInvestigations
HypokalaemiaMetabolism and nutrition disorders
Iron deficiencyMetabolism and nutrition disorders
Foot deformityMusculoskeletal and connective tissue disorders
Back painMusculoskeletal and connective tissue disorders
Muscle spasmsMusculoskeletal and connective tissue disorders
Rotator cuff syndromeMusculoskeletal and connective tissue disorders

Most-reported serious reactions: Femoral neck fracture, Subarachnoid haemorrhage, Psychotic symptom.

Data from ClinicalTrials.gov NCT04831281 adverse events section.

Sponsor's own description

This study is designed to evaluate the safety and treatment effects of fosgonimeton (ATH-1017) in subjects with Parkinson's Disease Dementia or Dementia with Lewy Bodies, with a randomized treatment duration of 26 weeks.

Publications & conference data

5 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Proteomic changes in Alzheimer's disease associated with progressive Aβ plaque and tau tangle pathologies.
    Pichet Binette A, Gaiteri C, Wennström M, Kumar A, et al · · 2024 · cited 103× · PMID 39187705 · DOI 10.1038/s41593-024-01737-w
  2. Cognitive Impairment in Parkinson's Disease: An Updated Overview Focusing on Emerging Pharmaceutical Treatment Approaches.
    Degirmenci Y, Angelopoulou E, Georgakopoulou VE, Bougea A. · · 2023 · cited 32× · PMID 37893474 · DOI 10.3390/medicina59101756
  3. Predictive Power of Cognitive Biomarkers in Neurodegenerative Disease Drug Development: Utility of the P300 Event-Related Potential.
    Olichney J, Xia J, Church KJ, Moebius HJ. · · 2022 · cited 28× · PMID 36398135 · DOI 10.1155/2022/2104880
  4. Dementia with Lewy Bodies Drug Therapies in Clinical Trials: Systematic Review up to 2022.
    Abdelnour C, Gonzalez MC, Gibson LL, Poston KL, et al · · 2023 · cited 22× · PMID 37017910 · DOI 10.1007/s40120-023-00467-8
  5. Approaches for treating neuropsychiatric symptoms in Parkinson's disease: a narrative review.
    Rodríguez-Antigüedad J, Olmedo-Saura G, Pagonabarraga J, Martínez-Horta S, et al · · 2025 · cited 4× · PMID 40433403 · DOI 10.1177/17562864251336903

Verify or expand the search:

Other trials of ATH-1017

Trials testing the same drug.

Other recruiting trials for Parkinson Disease Dementia

Currently open trials in the same condition.

Other LeonaBio trials

Trials by the same sponsor.

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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing