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NCT04823052: IMPACT-FXS

Investigation of Sulindac (HLX-0201) and Gaboxadol (HLX-0206) in Male Fragile X Syndrome Patients Aged 13-40

Withdrawn Phase 2 Last updated 8 December 2022
What this trial tests

Phase 2 trial testing Sulindac (HLX-0201), dose strength 1 in Fragile X Syndrome. Withdrawn.

Timeline
25 May 2022
Primary endpoint
19 October 2022
19 October 2022

Quick facts

Lead sponsorHealx Limited
PhasePhase 2
StatusWithdrawn
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposetreatment
Start date25 May 2022
Primary completion19 October 2022
Estimated completion19 October 2022
Sites10 locations across United States, Australia

Drugs / interventions tested

Conditions studied

Sponsor

Healx Limited — full company profile →

Who can join

Adults 13 to 40, male only, with Fragile X Syndrome. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

This study is to investigate the safety, tolerability and efficacy of Sulindac (HLX-0201) and Gaboxadol (HLX-0206) in males with Fragile X Syndrome (FXS) with confirmed full FMR1 mutation treated over a 10 week period in an outpatient setting.

Publications & conference data

3 peer-reviewed publications reference this trial (live from Europe PMC):

  1. The future of pharmaceuticals: Artificial intelligence in drug discovery and development.
    Fu C, Chen Q. · · 2025 · cited 18× · PMID 40893437 · DOI 10.1016/j.jpha.2025.101248
  2. Neurodevelopment and early pharmacological interventions in Fragile X Syndrome.
    Milla LA, Corral L, Rivera J, Zuñiga N, et al · · 2023 · cited 9× · PMID 37599992 · DOI 10.3389/fnins.2023.1213410
  3. A New Era of Artificial Intelligence (AI): Transforming Drug Discovery and Development.
    Ali S, Tian X, Chen H, Zhou J. · · 2025 · cited 7× · PMID 41306069 · DOI 10.1021/acs.jmedchem.5c03159

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Other recruiting trials for Fragile X Syndrome

Currently open trials in the same condition.

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Data sources for this page

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