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NCT04807517

Buspirone Treatment of Anxiety in Williams Syndrome

Completed Phase 4 Results posted Last updated 3 December 2024
What this trial tests

Phase 4 trial testing Buspirone in Williams Syndrome in 20 participants. Completed in 11 September 2023.

Timeline
1 August 2021
Primary endpoint
11 September 2023
11 September 2023

Quick facts

Lead sponsorMassachusetts General Hospital
PhasePhase 4
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment20
Start date1 August 2021
Primary completion11 September 2023
Estimated completion11 September 2023
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Massachusetts General Hospital

Who can join

Adults 5 to 65, any sex, with Williams Syndrome or Anxiety. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Mean 16-Week Change in Pediatric Anxiety Rating Scale 5-Item Total Score Primary · Baseline, Week 4, Week 8, Week 12, Week 16; Change from Baseline to Week 16 reported

The Pediatric Anxiety Rating Scale (PARS) is a clinician-rated instrument that assesses anxiety symptoms that are commonly associated with social anxiety, separation anxiety, and generalized anxiety disorders. Scaled score ranges from 0-25 with higher scores indicating more severe anxiety symptoms. Mean change was estimated using a repeated measures linear regression model with time in categories as the covariate and all non-missing scores for all measurement times as outcomes. A linear contrast estimated mean change between Baseline and Week 16.

GroupValue95% CI
Buspirone-7.9-10.0 – -5.9
Proportion of Participants Who Responded to Treatment at 16 Weeks According to the Improvement Item of the Clinical Global Impression-Scale (Response Defined as CGI-I=1 or CGI-I=2) Secondary · 16 weeks

The Clinical Global Impressions Global Improvement (CGI-I) is designed to take into account all factors to arrive at an assessment of response to treatment. The CGI-I scale ranges from 1 to 7 (1=very much improved; 2=much improved; 3=minimally improved; 4=no change; 5=minimally worse; 6=much worse; 7=very much worse), with lower scales indicating improvement (1=very much improved; 2=much improved). In this study, the CGI-I will be focused on the target symptom of anxiety. Participants with a CGI-I score of 1 or 2 will be classified as responders.

GroupValue95% CI
Buspirone1.000.82 – 1.00
Mean 16-Week Change in Child and Adolescent Symptom Inventory Anxiety-Modified Score Secondary · Baseline, Week 4, Week 8, Week 12, Week 16; Change from Baseline to Week 16 reported

The Child and Adolescent Symptom Inventory (CASI) is a caregiver completed questionnaire with items that map directly onto Diagnostic and Statistical Manual of Mental Disorders diagnostic criteria for anxiety disorders in children and adolescents. The CASI-Modified which includes 20 specific items that have been used to assess anxiety in subjects with developmental disabilities will be administered. Total score ranges from 0-20 with higher scores indicating more severe anxiety symptoms. Mean change was estimated using a repeated measures linear regression model with time in categories as the c

GroupValue95% CI
Buspirone-8.9-12.8 – -4.9
Mean 16-Week Change in Screen for Childhood Anxiety Related Emotional Disorders Total Score Secondary · Baseline, Week 4, Week 8, Week 12, Week 16; Change from Baseline to Week 16 reported

The Screen for Childhood Anxiety Related Emotional Disorders (SCARED) includes both a child/self-report and parent-report form, each containing 41-items. It is used to screen for symptoms of panic disorder, separation anxiety disorder, social phobia, generalized anxiety disorder, and school phobia. Total score ranges from 0-82 and a total score of 25 or greater may indicate the presence of an anxiety disorder. Mean change was estimated using a repeated measures linear regression model with time in categories as the covariate and all non-missing scores for all measurement times as outcomes. A l

Child/self-report form
GroupValue95% CI
Buspirone-16.0-28.1 – -3.9
Parent-report form
GroupValue95% CI
Buspirone-9.3-13.4 – -5.1
Mean 16-Week Change in Each Subscale of the Aberrant Behavior Checklist Secondary · Baseline, Week 4, Week 8, Week 12, Week 16; Change from Baseline to Week 16 reported

The Aberrant Behavior Checklist (ABC-2) is a caregiver rated instrument that measures psychiatric symptoms and behavioral disturbance in subjects with developmental disability with 5 subscales. Each of its 58 items is scored on a 4-point scale (0=never a problem to 3=severe problem). The 5 subscales and their range of scores are: Irritability 0-45, with higher scores indicating more severe irritability; Social Withdrawal/Lethargy 0-48, with higher scores indicating more severe social withdrawal; Stereotypy 0-21, with higher scores indicating more severe stereotypy; Hyperactivity 0-48, with hig

Irritability
GroupValue95% CI
Buspirone-6.3-10.3 – -2.4
Social withdrawal/lethargy
GroupValue95% CI
Buspirone-3.6-6.1 – -1.0
Stereotypy
GroupValue95% CI
Buspirone-1.8-3.0 – -0.6
Hyperactivity
GroupValue95% CI
Buspirone-6.2-9.4 – -2.9
Inappropriate speech
GroupValue95% CI
Buspirone-0.8-1.7 – 0.1
Mean 16-Week Change in Pittsburgh Sleep Quality Index Global Score Secondary · Baseline, Week 4, Week 8, Week 12, Week 16; Change from Baseline to Week 16 reported

The Pittsburgh Sleep Quality Index (PSQI) questionnaire that will be completed by the subject's caregiver to assess sleep quality. The global score ranges from 0-21, where a higher score indicates greater sleep difficulty. Mean change was estimated using a repeated measures linear regression model with time in categories as the covariate and all non-missing scores for all measurement times as outcomes. A linear contrast estimated mean change between Baseline and Week 16.

GroupValue95% CI
Buspirone-1.4-2.3 – -0.5

Adverse events — posted to ClinicalTrials.gov

Time frame: The earlier of 16 weeks or study discontinuation. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Buspirone
Serious: 0/20 (0%)
Deaths: 0/20
Other adverse events (38 terms — click to expand)

ReactionSystemBuspirone
DiarrheaGastrointestinal disorders
Appetite decreaseGeneral disorders
Stomach or abdominal discomfortGastrointestinal disorders
Nasal congestion or coldInfections and infestations
NauseaGastrointestinal disorders
VomitingGastrointestinal disorders
SadnessPsychiatric disorders
HeadacheNervous system disorders
Flu or other respiratory problemsInfections and infestations
Dry mouthGeneral disorders
Interrupted sleep/ other sleep problemsPsychiatric disorders
Tiredness/fatigueGeneral disorders
ConstipationGastrointestinal disorders
IrritabilityPsychiatric disorders
Sedation/drowsinessGeneral disorders
WeaknessGeneral disorders
Dizziness/faintnessNervous system disorders
Asthmatic symptomsRespiratory, thoracic and mediastinal disorders
Appetite increaseGeneral disorders
IndigestionGastrointestinal disorders
Localized rashSkin and subcutaneous tissue disorders
SweatingGeneral disorders
Change in speechPsychiatric disorders
ConfusionNervous system disorders
DisinhibitionPsychiatric disorders
Suicidal ideasPsychiatric disorders
FeverGeneral disorders
Acid refluxGastrointestinal disorders
AtaxiaNervous system disorders
BelchingGastrointestinal disorders
Hand painMusculoskeletal and connective tissue disorders
Lip pickingPsychiatric disorders
ParesthesiaNervous system disorders
PneumoniaInfections and infestations
Shoulder injuryMusculoskeletal and connective tissue disorders
Social withdrawalPsychiatric disorders
StutteringNervous system disorders
Urinary tract infectionRenal and urinary disorders

Data from ClinicalTrials.gov NCT04807517 adverse events section.

Sponsor's own description

The purpose of this study is to do a preliminary assessment of whether buspirone is effective, safe, and tolerable in the treatment of anxiety in children, adolescents, and adults with Williams syndrome.

Publications & conference data

No peer-reviewed publications indexed yet for this trial. Completed trials usually publish results within 12-18 months.

Verify or expand the search:

Other trials of Buspirone

Trials testing the same drug.

Other recruiting trials for Williams Syndrome

Currently open trials in the same condition.

Other Massachusetts General Hospital trials

Trials by the same sponsor.

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Data sources for this page

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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing