Last reviewed · How we verify

NCT04692077

Safety, Tolerability and Acceptability of Long-Acting Cabotegravir (CAB LA) for the Prevention of HIV Among Adolescent Males

Completed Phase 2 Results posted Last updated 20 May 2025
What this trial tests

Phase 2 trial testing Cabotegravir (CAB) tablet in HIV Infections in 9 participants. Completed in 7 July 2023.

Timeline
19 February 2020
Primary endpoint
7 July 2023
7 July 2023

Quick facts

Lead sponsorNational Institute of Allergy and Infectious Diseases (NIAID)
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposeprevention
Enrollment9
Start date19 February 2020
Primary completion7 July 2023
Estimated completion7 July 2023
Sites4 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

National Institute of Allergy and Infectious Diseases (NIAID)

Who can join

Under 17, male only, with HIV Infections. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Safety Endpoint: Proportion of Participants Experiencing Any Grade 2 or Higher Clinical Adverse Events (AEs) and Laboratory Abnormalities Among Participants Who Receive at Least One Injection of CAB LA. Primary · Measured through participant's first injection visit up to 8 weeks after the last Step 2 injection visit or Week 41, whichever comes first.

Number and percent of participants experiencing any Grade 2 or higher clinical adverse events (AEs) or laboratory abnormalities (reported as adverse events) from the first injection visit to 8 weeks after the last Step 2 injection visit, or Week 41, whichever comes first.

GroupValue95% CI
Cabotegravir Long Acting8
Tolerability Endpoint: Proportion of Participants Who Receive at Least 1 Injection and Who Discontinue Receiving Injections Prior to the Full Course of Injections Due to Intolerability of Injection, Frequency of Injections or Burden of Study Procedures. Primary · Measured through participant's first injection visit up to 8 weeks after the last Step 2 injection visit or Week 41, whichever comes first.

Number and percent of participants who receive at least 1 injection and who discontinue receiving injections prior to the full course of injections due to intolerability of injection or burden of study procedures. Reasons for intolerability may include: 1. Injection site reaction 2. Burden of study procedure 1. Participant refused further participation 2. Participant is unwilling or unable to comply with required study procedures 3. Participant refused further study product use 4. Participant unable to adhere to visit schedule

Number of participants who received at least 1 injection of CAB LA
GroupValue95% CI
Cabotegravir Long Acting9
Number of participants who reported any injection site reaction (ISR)
GroupValue95% CI
Cabotegravir Long Acting5
Number of participants who have reported any Grade 2 (moderate) or above ISR
GroupValue95% CI
Cabotegravir Long Acting3
Participants who Discontinued Early due to Intolerability of Injection or Burden of Study Procedure
GroupValue95% CI
Cabotegravir Long Acting1
Number of participants who completed all scheduled injections
GroupValue95% CI
Cabotegravir Long Acting8
Acceptability Endpoint: Proportion of Participants Who Complete All Scheduled Injections and Proportion of Participants Who Receive at Least One Injection Whom Would Consider Using CAB LA for HIV Prevention in the Future. Primary · Measured through participant's first injection visit up to 8 weeks after the last Step 2 injection visit or Week 41, whichever comes first.

Definition of completing all scheduled injections for participants who are confirmed HIV positive or discontinue product due to the following reasons: * Death * Early study closure * HBV infection During Step 2: Both enrolled and injection populations: completed all injections whose target window closed prior to death/seroconversion/product discontinuation date

Participant who received at least one injection among all enrolled participants
GroupValue95% CI
Cabotegravir Long Acting9
Participants with acceptability endpoint at the end of Step 2
GroupValue95% CI
Cabotegravir Long Acting6
Participants who received at least one injection and preferred injectable PrEP at the end of Step 2
GroupValue95% CI
Cabotegravir Long Acting4
If you wanted to protect yourself from HIV: Prefer not using a product
GroupValue95% CI
Cabotegravir Long Acting0
If you wanted to protect yourself from HIV: Condoms only
GroupValue95% CI
Cabotegravir Long Acting1
If you wanted to protect yourself from HIV: Oral PrEP pills only
GroupValue95% CI
Cabotegravir Long Acting0
If you wanted to protect yourself from HIV: Injectable PrEP only
GroupValue95% CI
Cabotegravir Long Acting0
If you wanted to protect yourself from HIV: Condoms and oral PrEP pills together
GroupValue95% CI
Cabotegravir Long Acting1
Count of Participant-study Visits Above the Protein-adjusted Inhibitor Concentration (90%; PA-IC90) Secondary · Measured from the participant's first injection visit up to 8 weeks after the last Step 2 injection visit or Week 41

CAB drug concentrations will be measured in plasma to generate CAB-LA concentration-time profiles among study participants. Measurements will occur at study visits during the injection phase of the study as well as during the pharmacologic "tail" phase. Count of participants for injection visits in which a participant remains above the 1x (0.166 mcg/mL), 4x (0.664 mcg/mL) and 8x (1.33 mcg/mL) PA-IC90.Concentrations above the 3 PA-IC90 are associated with rectal protection in a non-human primate study, and concentrations above the 8x PA-IC90 are expected to be associated with protection in huma

Injection 1
GroupValue95% CI
Cabotegravir Long Acting1
Cabotegravir Long Acting0
Cabotegravir Long Acting0
Cabotegravir Long Acting8
Injection 2
GroupValue95% CI
Cabotegravir Long Acting0
Cabotegravir Long Acting1
Cabotegravir Long Acting2
Cabotegravir Long Acting6
Injection 3
GroupValue95% CI
Cabotegravir Long Acting0
Cabotegravir Long Acting1
Cabotegravir Long Acting0
Cabotegravir Long Acting7
Injection 4
GroupValue95% CI
Cabotegravir Long Acting0
Cabotegravir Long Acting0
Cabotegravir Long Acting2
Cabotegravir Long Acting6
Injection 5
GroupValue95% CI
Cabotegravir Long Acting0
Cabotegravir Long Acting0
Cabotegravir Long Acting1
Cabotegravir Long Acting6
Step 3 +8 weeks
GroupValue95% CI
Cabotegravir Long Acting0
Cabotegravir Long Acting0
Cabotegravir Long Acting0
Cabotegravir Long Acting7
Count and Percentage of Participants Experiencing Grade 2 or Higher Clinical AEs and LaboratoryAbnormalities in the Oral Phase and the Aggregate Oral and Injection Phases Secondary · Measured through participant's first oral visit up to 8 weeks after the last Step 2 injection visit or Week 41, whichever comes first.

Number and percent of participants experiencing any Grade 2 or higher clinical adverse events (AEs) or laboratory abnormalities from: 1. enrollment to week 5 (oral phase (step 1), including interim visits). 2. enrollment to 8 weeks following the last injection received (aggregate over oral + injection phases (step 1-step 2) including interim visits)

Number of participants with Grade 2 or Higher AEs in Oral Phase
GroupValue95% CI
Cabotegravir Long Acting3
Number of participants with Grade 2 or Higher AEs in Oral and Injection Phase
GroupValue95% CI
Cabotegravir Long Acting8
Proportion of Participants Receiving One or More Injections Who Experience Grade 2 or Higher Clinical AEs and Laboratory Abnormalities From Initial Injection to 36 Weeks Later. Secondary · Measured through participant's first injection visit up to 8 weeks after the last Step 2 injection visit or Week 41, whichever comes first.

Number and percent of participants experiencing any Grade 2 or higher clinical adverse events (AEs) or laboratory abnormalities from the first injection visit to approximately 36 weeks later regardless of whether participants received all 5 injections.

GroupValue95% CI
Cabotegravir Long Acting8
Proportion of Injection Visits That Occurred "On-time". Secondary · Measured through participant's last step 2 injection.

Number and percentage of injections given, using the number of injections expected as the denominator. while the number and percent of injection visits (up to 5 per participant) that occur "on-time", using the number of injections given as the denominator. This will be presented along with the total number and percent of injections given, among all intended injections (i.e. 5 injections per participant). Those who have been terminated, are HIV infected, or have permanently discontinued study products at the time of visit will be excluded from the number of expected injections.

Number of injections given
GroupValue95% CI
Cabotegravir Long Acting40
Number of injections given on-time
GroupValue95% CI
Cabotegravir Long Acting32
Change From Enrollment of Self-reported Sexual Behavior (Number of Sexual Partners) During the Study Period Secondary · Measured through participant's first oral visit up to last Step 2 injection visit.

Counts of sexual partners will be summarized (mean and sd) at enrollment and each regular Step 1 and Step 2 follow-up visit (W4, W5, W9, W17, W25, W33).

Enrollment
GroupValue95% CI
Cabotegravir Long Acting0± 0.4
Week 4
GroupValue95% CI
Cabotegravir Long Acting0± 0.5
Week 4: Change from previous visit
GroupValue95% CI
Cabotegravir Long Acting0± 0.0
Week 4: Change from baseline
GroupValue95% CI
Cabotegravir Long Acting0± 0.0
Week 5
GroupValue95% CI
Cabotegravir Long Acting0± 0.7
Week 5: Change from previous visit
GroupValue95% CI
Cabotegravir Long Acting0± 0.4
Week 5: Change from baseline
GroupValue95% CI
Cabotegravir Long Acting0± 0.4
Week 9
GroupValue95% CI
Cabotegravir Long Acting0± 0.4
Change From Enrollment of Self-reported Sexual Behavior (Number of Episodes of Anal Intercourse Without a Condom) During the Study Period Secondary · Measured through participant's first oral visit up to the last Step 2 injection visit.

Counts of episodes of anal intercourse without a condom will be summarized (mean and sd) at enrollment and each regular Step 1 and Step 2 follow-up visit (W4, W5, W9, W17, W25, W33).

Enrollment
GroupValue95% CI
CAB LA1± 1.3
Week 4
GroupValue95% CI
CAB LA1± 2.3
Week 4: Change from previous visit
GroupValue95% CI
CAB LA0± 1.1
Week 4: Change from baseline
GroupValue95% CI
CAB LA0± 1.1
Week 5
GroupValue95% CI
CAB LA0± 0.7
Week 5: Change from previous visit
GroupValue95% CI
CAB LA-1± 1.8
Week 5: Change from baseline
GroupValue95% CI
CAB LA0± 0.7
Week 9
GroupValue95% CI
CAB LA0± 0.4
Evaluate Rates of HIV Drug Resistance Among Participants Who Acquire HIV Infection During the Study Secondary · Measured through participant's last study visit, up to approximately 1.5 years after study entry.

Data from steps 1, 2, and 3 will be included. The number of cases of drug resistance will be summarized. All cases of drug resistance among incident HIV infections will be described.

Number of participants HIV-positive at enrollment
GroupValue95% CI
Cabotegravir Long Acting0
Number of participants infected
GroupValue95% CI
Cabotegravir Long Acting0
Number of drug resistant cases
GroupValue95% CI
Cabotegravir Long Acting0

Adverse events — posted to ClinicalTrials.gov

Time frame: Measured from participant's first Oral visit up to follow-up 48 weeks Step 3.. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Step 1 - CAB LA Oral Phase
Serious: 0/9 (0%)
Deaths: 0/9
Step 2 - CAB LA Injection Phase
Serious: 0/9 (0%)
Deaths: 0/9
Step 3 - CAB LA Injection Follow-up
Serious: 1/6 (17%)
Deaths: 0/6
Step 3 - Tenofovir/Emtricitabine Follow-up
Serious: 0/3 (0%)
Deaths: 0/3

Serious adverse events (1 terms)

ReactionSystemStep 1 - CAB LA Oral PhaseStep 2 - CAB LA Injection …Step 3 - CAB LA Injection …Step 3 - Tenofovir/Emtrici…
Suicidal ideationPsychiatric disorders
Other adverse events (47 terms — click to expand)

ReactionSystemStep 1 - CAB LA Oral PhaseStep 2 - CAB LA Injection …Step 3 - CAB LA Injection …Step 3 - Tenofovir/Emtrici…
Creatinine renal clearance decreasedInvestigations
Blood phosphorus decreasedInvestigations
ProteinuriaRenal and urinary disorders
Alanine aminotransferase increasedInvestigations
Amylase increasedInvestigations
Aspartate aminotransferase increasedInvestigations
Blood calcium increasedInvestigations
Blood creatinine increasedInvestigations
HyperglycaemiaMetabolism and nutrition disorders
AnxietyPsychiatric disorders
Tricuspid valve incompetenceCardiac disorders
DiarrhoeaGastrointestinal disorders
NauseaGastrointestinal disorders
ProctalgiaGastrointestinal disorders
Rectal haemorrhageGastrointestinal disorders
VomitingGastrointestinal disorders
FatigueGeneral disorders
MalaiseGeneral disorders
COVID-19Infections and infestations
Ear infectionInfections and infestations
Upper respiratory tract infectionInfections and infestations
Limb injuryInjury, poisoning and procedural complications
Muscle strainInjury, poisoning and procedural complications
Blood alkaline phosphatase increasedInvestigations
Blood cholesterol increasedInvestigations
Blood creatine increasedInvestigations
Blood creatine phosphokinase increasedInvestigations
Blood glucose decreasedInvestigations
Blood potassium increasedInvestigations
Blood pressure increasedInvestigations
Blood triglycerides increasedInvestigations
Lipase increasedInvestigations
Low density lipoprotein increasedInvestigations
Platelet count decreasedInvestigations
ArthralgiaMusculoskeletal and connective tissue disorders
DizzinessNervous system disorders
HeadacheNervous system disorders
Behaviour disorderPsychiatric disorders
DepressionPsychiatric disorders
Disruptive mood dysregulation disorderPsychiatric disorders

Most-reported serious reactions: Suicidal ideation.

Data from ClinicalTrials.gov NCT04692077 adverse events section.

Sponsor's own description

This study will establish the minimum safety, tolerability and acceptability data needed to support the use of cabotegravir long-acting injection (CAB LA) in an adolescent population, potentially transforming the field of HIV prevention for young people.

Publications & conference data

3 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Cabotegravir for HIV Prevention in Cisgender Men and Transgender Women.
    Landovitz RJ, Donnell D, Clement ME, Hanscom B, et al · · 2021 · cited 671× · PMID 34379922 · DOI 10.1056/nejmoa2101016
  2. Cabotegravir for the prevention of HIV-1 in women: results from HPTN 084, a phase 3, randomised clinical trial.
    Delany-Moretlwe S, Hughes JP, Bock P, Ouma SG, et al · · 2022 · cited 421× · PMID 35378077 · DOI 10.1016/s0140-6736(22)00538-4
  3. Long-Acting Cabotegravir for HIV/AIDS Prophylaxis.
    Engelman KD, Engelman AN. · · 2021 · cited 19× · PMID 34029457 · DOI 10.1021/acs.biochem.1c00157

Verify or expand the search:

Other trials of Cabotegravir (CAB) tablet

Trials testing the same drug.

Other recruiting trials for HIV Infections

Currently open trials in the same condition.

Other National Institute of Allergy and Infectious Diseases (NIAID) trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04692077.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing