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NCT04676373: APOLLO-LOPD

Study to Evaluate Efficacy and Safety in Chinese Patients With Late Onset Pompe Disease With Alglucosidase Alfa Treatmen

Completed Phase 4 Last updated 10 February 2025
What this trial tests

Phase 4 trial testing ALGLUCOSIDASE ALFA in Pompe's Disease in 41 participants. Completed in 25 July 2024.

Timeline
10 March 2021
Primary endpoint
25 July 2024
25 July 2024

Quick facts

Lead sponsorGenzyme, a Sanofi Company
PhasePhase 4
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment41
Start date10 March 2021
Primary completion25 July 2024
Estimated completion25 July 2024
Sites1 location across China

Drugs / interventions tested

Conditions studied

Sponsor

Genzyme, a Sanofi Company — full company profile →

Who can join

3 and older, any sex, with Pompe's Disease. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

Primary Objective: To evaluate the effect of one-year Alglucosidase alfa treatment on motor function \[Six-minute walk test (6MWT) and lung function predicted Forced vital capacity (FVC)\] among Chinese Late Onset Pompe Disease patients above 5 years old. To evaluate the safety of Myozyme 20mg/kg, IV biweekly in Chinese LOPD patients above 3 years old. Secondary Objective: To evaluate the effect of one-year treatment with Alglucosidase alfa on improvement of manual muscle test (MMT), Maximal inspiratory and expiratory pressure (MIP and MEP)\], Quick Motor Function Test scores, and health-related quality of life (SF-12) among LOPD patients over 5 years old.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Role of lysosomes in physiological activities, diseases, and therapy.
    Zhang Z, Yue P, Lu T, Wang Y, et al · · 2021 · cited 238× · PMID 33990205 · DOI 10.1186/s13045-021-01087-1

Verify or expand the search:

Other recruiting trials for Pompe's Disease

Currently open trials in the same condition.

Other Genzyme, a Sanofi Company trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04676373.

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