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NCT04608487
Axi-cel in CNS Lymphoma
Phase 1 trial testing Fludarabine in Lymphoma in 18 participants. Participants enrolled and being followed up; not accepting new ones.
14 June 2025
Quick facts
| Lead sponsor | Dana-Farber Cancer Institute |
|---|---|
| Phase | Phase 1 |
| Status | Active, enrolled |
| Study type | INTERVENTIONAL |
| Allocation | na |
| Design | single group |
| Masking | none |
| Primary purpose | treatment |
| Enrollment | 18 |
| Start date | 4 December 2020 |
| Primary completion | 14 June 2025 |
| Estimated completion | 14 June 2038 |
| Sites | 2 locations across United States |
Drugs / interventions tested
- Fludarabine (FLUDARABINE) — full drug profile →
- Cyclophosphamide (cyclophosphamide) — full drug profile →
- Axicabtagene Ciloleucel — full drug profile →
Conditions studied
- Lymphoma — all drugs for Lymphoma →
- Lymphoma Cns — all drugs for Lymphoma Cns →
Sponsor
Dana-Farber Cancer Institute
Who can join
18 and older, any sex, with Lymphoma or Lymphoma Cns. Patients with the condition only — healthy volunteers not accepted.
Sponsor's own description
This research is being done to test the safety and effectiveness of axicabtagene ciloleucel (axi-cel), an anti-CD19 directed chimeric antigen receptor (CAR) T-cell therapy in treating relapsed/refractory central nervous system (CNS) lymphoma, systemic lymphoma with concurrent CNS lymphoma, or systemic lymphoma with a history of treated CNS lymphoma, and to better understand what causes neurological toxicity following treatment with axi-cel. The names of the study drug(s) involved in this study are: * axicabtagene ciloleucel (axi-cel) * ludarabine will be given with axicel to help axicel work more effectively * cyclophosphamide will be given with axicel to help axicel work more effectively
Publications & conference data
8 peer-reviewed publications reference this trial (live from Europe PMC):
-
CAR-T cell therapy for cancer: current challenges and future directions.
Zugasti I, Espinosa-Aroca L, Fidyt K, Mulens-Arias V, et al · · 2025 · cited 81× · PMID 40610404 · DOI 10.1038/s41392-025-02269-w -
Prevention and management of secondary central nervous system lymphoma.
Bobillo S, Khwaja J, Ferreri AJM, Cwynarski K. · · 2023 · cited 47× · PMID 36384246 · DOI 10.3324/haematol.2022.281457 -
CAR T-cell-associated neurotoxicity in central nervous system hematologic disease: Is it still a concern?
Velasco R, Mussetti A, Villagrán-García M, Sureda A. · · 2023 · cited 39× · PMID 37090983 · DOI 10.3389/fneur.2023.1144414 -
How I treat secondary CNS involvement by aggressive lymphomas.
Alderuccio JP, Nayak L, Cwynarski K. · · 2023 · cited 22× · PMID 37702537 · DOI 10.1182/blood.2023020168 -
CAR T-Cells for CNS Lymphoma: Driving into New Terrain?
Karschnia P, Blobner J, Teske N, Schöberl F, et al · · 2021 · cited 19× · PMID 34065471 · DOI 10.3390/cancers13102503 -
Emerging Approaches for Solid Tumor Treatment Using CAR-T Cell Therapy.
Chung H, Jung H, Noh JY. · · 2021 · cited 18× · PMID 34830003 · DOI 10.3390/ijms222212126 -
Update on Novel Therapeutics for Primary CNS Lymphoma.
Schaff LR, Grommes C. · · 2021 · cited 15× · PMID 34771535 · DOI 10.3390/cancers13215372 -
Recent Progress on Primary Central Nervous System Lymphoma-From Bench to Bedside.
Shao L, Xu C, Wu H, Jamal M, et al · · 2021 · cited 13× · PMID 34485125 · DOI 10.3389/fonc.2021.689843
Verify or expand the search:
- PubMed search for NCT04608487
- Europe PMC full search
- ASCO Meeting Library
- ESMO Meeting Library
- bioRxiv preprints
- medRxiv preprints
- Google Scholar
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Other recruiting trials for Lymphoma
Currently open trials in the same condition.
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Trials by the same sponsor.
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Verify against primary sources
- ClinicalTrials.gov — authoritative US registry record
- WHO ICTRP — international registry index
- EU Clinical Trials Register
- Sponsor press releases (Google)
- Trial protocol + status: ClinicalTrials.gov NCT04608487 (US National Library of Medicine, public domain)
- Publications: Europe PMC API search by NCT ID, retrieved 10 June 2026
- Drug + disease cross-links: matched in real time against Drug Landscape's normalised drug + company + condition tables
- Sponsor: as reported to ClinicalTrials.gov by Dana-Farber Cancer Institute
- Last refreshed: 30 July 2025
Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04608487.
Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing