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NCT04556734

Safety and Efficacy of Oral Etrasimod in Adult Participants With Moderate-to-Severe Alopecia Areata

Completed Phase 2 Results posted Last updated 26 June 2024
What this trial tests

Phase 2 trial testing Etrasimod in Alopecia Areata in 80 participants. Completed in 7 June 2023.

Timeline
29 July 2020
Primary endpoint
7 June 2023
7 June 2023

Quick facts

Lead sponsorPfizer
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingtriple
Primary purposetreatment
Enrollment80
Start date29 July 2020
Primary completion7 June 2023
Estimated completion7 June 2023
Sites42 locations across Canada, United States

Drugs / interventions tested

Conditions studied

Sponsor

Pfizer — full company profile →

Who can join

Adults 18 to 70, any sex, with Alopecia Areata. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Percent Change From Baseline in Severity of Alopecia Tool I (SALT I) at Week 24: DB Treatment Period Primary · DB Treatment Period: Baseline (before dose on Day 1), Week 24

SALT I is a well-validated metric used to determine the degree of hair loss based on the percentage (%) of scalp surface area involved on the top (40%), back (24%), left side (18%) and right side (18%) of the scalp for AA. Investigator determines the % scalp hair loss in a given quadrant, multiply this by the total scalp area delineated by that quadrant, and sum the resultant numbers for each quadrant to give the total % scalp hair loss with a maximum score of 100. Score range from 0% (no scalp hair loss) to 100% (complete scalp hair loss), higher scores indicated more scalp hair loss. Percent

GroupValue95% CI
DB Treatment Period: Etrasimod 2 mg-13.79± 8.557
DB Treatment Period: Etrasimod 3 mg-21.43± 6.926
DB Treatment Period: Placebo0.35± 8.933
Change From Baseline in SALT I at Week 24: DB Treatment Period Secondary · DBT Period: Baseline, Week 24

SALT I is a well-validated metric used to determine the degree of hair loss based on the percentage (%) of scalp surface area involved on the top (40%), back (24%), left side (18%) and right side (18%) of the scalp for AA. Investigator determines the % scalp hair loss in a given quadrant, multiply this by the total scalp area delineated by that quadrant, and sum the resultant numbers for each quadrant to give the total % scalp hair loss with a maximum score of 100. Score range from 0% (no scalp hair loss) to 100% (complete scalp hair loss), higher scores indicated more scalp hair loss. Change

GroupValue95% CI
DB Treatment Period: Etrasimod 2 mg-8.87± 4.142
DB Treatment Period: Etrasimod 3 mg-8.62± 3.351
DB Treatment Period: Placebo0.36± 4.314
Percentage of Participants Who Achieved Greater Than or Equal to (>=) 30%, >= 50% and >=75% Improvement From Baseline in SALT I at Week 24: DB Treatment Period Secondary · DB Treatment Period: Baseline, Week 24

SALT I is a well-validated metric used to determine the degree of hair loss based on the percentage of scalp surface area involved on the top, back, and each side of the scalp for alopecia areata (AA). Investigator determine the percent scalp hair loss in a given quadrant, multiply this by the total scalp area delineated by that quadrant, and sum the resultant numbers for each quadrant to give the total percent scalp hair loss with a maximum score of 100. Score range from 0 to 100, where 0 =no scalp hair loss to 100 = complete scalp hair loss, higher scores indicated more scalp hair loss. Perc

>= 30% Improvement
GroupValue95% CI
DB Treatment Period: Etrasimod 2 mg23.56.81 – 49.90
DB Treatment Period: Etrasimod 3 mg36.017.97 – 57.48
DBT Period: Placebo12.51.55 – 38.35
>= 50% Improvement
GroupValue95% CI
DB Treatment Period: Etrasimod 2 mg11.81.46 – 36.44
DB Treatment Period: Etrasimod 3 mg28.012.07 – 49.39
DBT Period: Placebo12.51.55 – 38.35
>= 75% Improvement
GroupValue95% CI
DB Treatment Period: Etrasimod 2 mg5.90.15 – 28.69
DB Treatment Period: Etrasimod 3 mg12.02.55 – 31.22
DBT Period: Placebo0.0000.00 – 20.59
Number of Participants With Adverse Events (AE): DB Treatment Period Secondary · DB Treatment Period: From first dosing date in DB up to (before the first dosing date in OLE) or (last dosing date + 4 weeks + 3 days), whichever is earlier (maximum up to 29 weeks)

An AE is any untoward medical occurrence in a participant temporally associated with the use of a medicinal product, whether or not considered related to the medicinal product. Serious adverse event (SAE) is any untoward medical occurrence that at any dose results in death, is life-threatening, requires hospitalization or prolongation of existing hospitalization, results in disability/incapacity, is a congenital anomaly/birth defect, other situations based on medical significance or any diagnosis of progressive multifocal leukoencephalopathy (PML). AEs included serious AEs and all non-SAEs.

GroupValue95% CI
DB Treatment Period: Etrasimod 2 mg21
DB Treatment Period: Etrasimod 3 mg20
DB Treatment Period: Placebo18
Number of Participants With Adverse Events: OLE Period Secondary · OLE period: From first dosing date in OLE up to last dosing date + 4 weeks + 3 days (maximum up to 33 weeks)

An AE is any untoward medical occurrence in a participant temporally associated with the use of a medicinal product, whether or not considered related to the medicinal product. An SAE is any untoward medical occurrence that at any dose results in death, is life-threatening, requires hospitalization or prolongation of existing hospitalization, results in disability/incapacity, is a congenital anomaly/birth defect, other situations based on medical significance or any diagnosis of PML. AEs included serious AEs and all non-SAEs.

GroupValue95% CI
OLE Period: Etrasimod 2 mg [Etrasimod 2 mg in DB Treatment Period]3
OLE Period: Etrasimod 2 mg [Placebo in DB Treatment Period]2
OLE Period: Etrasimod 3 mg [Etrasimod 3 mg in DBT]18
OLE Period: Etrasimod 3 mg [Etrasimod 2 mg in DB Treatment Period]14
OLE Period: Etrasimod 3 mg [Placebo in DB Treatment Period]11

Adverse events — posted to ClinicalTrials.gov

Time frame: From first dosing date up to last dosing date + 4 weeks + 3 days (maximum up to 57 weeks). Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

DB Treatment Period: Etrasimod 2 mg
Serious: 0/31 (0%)
Deaths: 0/31
DB Treatment Period: Etrasimod 3 mg
Serious: 0/25 (0%)
Deaths: 0/25
DB Treatment Period: Placebo
Serious: 0/23 (0%)
Deaths: 0/23
OLE Period: Etrasimod 2 mg [Etrasimod 2 mg in DB Treatment Period]
Serious: 1/4 (25%)
Deaths: 0/4
OLE Period: Etrasimod 2 mg [Placebo in DB Treatment Period]
Serious: 0/4 (0%)
Deaths: 0/4
OLE Period: Etrasimod 3 mg [Etrasimod 3 mg in DB Treatment Period]
Serious: 1/24 (4%)
Deaths: 0/24
OLE Period: Etrasimod 3 mg [Etrasimod 2 mg in DB Treatment Period]
Serious: 0/20 (0%)
Deaths: 0/20
OLE Period: Etrasimod 3 mg [Placebo in DB Treatment Period]
Serious: 0/13 (0%)
Deaths: 0/13

Serious adverse events (3 terms)

ReactionSystemDB Treatment Period: Etras…DB Treatment Period: Etras…DB Treatment Period: PlaceboOLE Period: Etrasimod 2 mg…OLE Period: Etrasimod 2 mg…OLE Period: Etrasimod 3 mg…OLE Period: Etrasimod 3 mg…OLE Period: Etrasimod 3 mg…
COVID-19 pneumoniaInfections and infestations
MyelopathyNervous system disorders
RadiculopathyNervous system disorders
Other adverse events (46 terms — click to expand)

ReactionSystemDB Treatment Period: Etras…DB Treatment Period: Etras…DB Treatment Period: PlaceboOLE Period: Etrasimod 2 mg…OLE Period: Etrasimod 2 mg…OLE Period: Etrasimod 3 mg…OLE Period: Etrasimod 3 mg…OLE Period: Etrasimod 3 mg…
Lymphocyte count decreasedInvestigations
HeadacheNervous system disorders
COVID-19Infections and infestations
Upper respiratory tract infectionInfections and infestations
Urinary tract infectionInfections and infestations
MyalgiaMusculoskeletal and connective tissue disorders
DiarrhoeaGastrointestinal disorders
NasopharyngitisInfections and infestations
CoughRespiratory, thoracic and mediastinal disorders
NauseaGastrointestinal disorders
FolliculitisInfections and infestations
Joint injuryInjury, poisoning and procedural complications
Gamma-glutamyl transferase increasedInvestigations
Alanine aminotransferase increasedInvestigations
ArthralgiaMusculoskeletal and connective tissue disorders
Pain in extremityMusculoskeletal and connective tissue disorders
DizzinessNervous system disorders
LeukopeniaBlood and lymphatic system disorders
Muscle strainInjury, poisoning and procedural complications
MigraineNervous system disorders
Nasal congestionRespiratory, thoracic and mediastinal disorders
Dermatitis atopicSkin and subcutaneous tissue disorders
LymphopeniaBlood and lymphatic system disorders
Atrioventricular block second degreeCardiac disorders
BradycardiaCardiac disorders
Supraventricular extrasystolesCardiac disorders
Eye painEye disorders
Fuchs' syndromeEye disorders
VomitingGastrointestinal disorders
Abdominal pain upperGastrointestinal disorders
Gastrointestinal disorderGastrointestinal disorders
FatigueGeneral disorders
Influenza like illnessGeneral disorders
MalaiseGeneral disorders
NoduleGeneral disorders
Limb injuryInjury, poisoning and procedural complications
Blood pressure increasedInvestigations
Electrocardiogram abnormalInvestigations
Tri-iodothyronine free increasedInvestigations
Flank painMusculoskeletal and connective tissue disorders

Most-reported serious reactions: COVID-19 pneumonia, Myelopathy, Radiculopathy.

Data from ClinicalTrials.gov NCT04556734 adverse events section.

Sponsor's own description

The purpose of this study is to evaluate the safety and efficacy of etrasimod monotherapy (2 milligrams \[mg\] and 3 mg) in participants with moderate-to-severe alopecia areata (AA).

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Inhibition of T-cell activity in alopecia areata: recent developments and new directions.
    Passeron T, King B, Seneschal J, Steinhoff M, et al · · 2023 · cited 54× · PMID 38022501 · DOI 10.3389/fimmu.2023.1243556
  2. Barrier maintenance by S1P during inflammation and sepsis.
    Ziegler AC, Gräler MH. · · 2021 · cited 10× · PMID 34152926 · DOI 10.1080/21688370.2021.1940069
  3. Unique pharmacological properties of etrasimod among S1P receptor modulators.
    Gaidarov I, Komori HK, Stepniak DT, Bruinsma K, et al · · 2025 · cited 5× · PMID 39564958 · DOI 10.1002/2211-5463.13907
  4. T cell trafficking in human chronic inflammatory diseases.
    Giovenzana A, Codazzi V, Pandolfo M, Petrelli A. · · 2024 · cited 5× · PMID 39171290 · DOI 10.1016/j.isci.2024.110528
  5. Efficacy and safety of etrasimod in alopecia areata: A multicentre, randomized, double-blind, placebo-controlled, Phase 2 study.
    King B, Mesinkovska N, Senna M, Luo X, et al · · 2025 · cited 4× · PMID 40145547 · DOI 10.1111/jdv.20605
  6. Overview of alopecia areata for managed care and payer stakeholders in the United States.
    King B, Pezalla E, Fung S, Tran H, et al · · 2023 · cited 3× · PMID 37219075 · DOI 10.18553/jmcp.2023.22371
  7. From mechanisms to therapies: current advances breakthroughs in alopecia areata immunopathology.
    Zhao HB, Zhang YN, Qiang Y, Wang GM, et al · · 2025 · cited 2× · PMID 40959061 · DOI 10.3389/fimmu.2025.1621492
  8. Low Incidence of Macular Edema and Other Ocular Events in the Etrasimod Development Program.
    Dubinsky MC, Wu J, McDonnell A, Lazin K, et al · · 2025 · cited 2× · PMID 39575597 · DOI 10.1093/ecco-jcc/jjae173

Verify or expand the search:

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Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04556734.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing