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NCT04501757
Naxitamab and GM-CSF in People With Neuroblastoma
trial testing Naxitamab/GM-CSF in High-Risk Neuroblastoma. No longer available.
Quick facts
| Lead sponsor | Memorial Sloan Kettering Cancer Center |
|---|---|
| Status | NO LONGER AVAILABLE |
| Study type | EXPANDED_ACCESS |
| Sites | 1 location across United States |
Drugs / interventions tested
- Naxitamab/GM-CSF — full drug profile →
Conditions studied
- High-Risk Neuroblastoma — all drugs for High-Risk Neuroblastoma →
Sponsor
Memorial Sloan Kettering Cancer Center — full company profile →
Who can join
18 Months and older, any sex, with High-Risk Neuroblastoma. Patients with the condition only — healthy volunteers not accepted.
Sponsor's own description
This is an Expanded Access Program (EAP) that will give the participants access to the drug naxitamab before it is approved by the FDA. Naxitamab will be combined with granulocyte-macrophage colony stimulating factor (GM-CSF). Participants in this study will have high-risk neuroblastoma that either went away completely after treatment (complete remission) or has come back (relapsed/refractory). Researchers think the combination of naxitamab and GM-CSF will be effective because naxitamab and GM-CSF strengthen the immune system's response to cancer cells in different ways. Naxitamab is an antibody, like the proteins made by the immune system to protect the body from harm. Naxitamab helps the cells of the immune system to find and attack cancer cells. GM-CSF is a protein that strengthens the immune system by increasing the number of immune cells called granulocytes. Granulocytes are white blood cells that fight off cancer cells. The combination of naxitamab and GM-CSF is a type of immunotherapy.
Publications & conference data
4 peer-reviewed publications reference this trial (live from Europe PMC):
-
Anti-glycan monoclonal antibodies: Basic research and clinical applications.
Gillmann KM, Temme JS, Marglous S, Brown CE, et al · · 2023 · cited 25× · PMID 36905763 · DOI 10.1016/j.cbpa.2023.102281 -
Neuroblastoma: an ongoing cold front for cancer immunotherapy.
Kennedy PT, Zannoupa D, Son MH, Dahal LN, et al · · 2023 · cited 19× · PMID 37993280 · DOI 10.1136/jitc-2023-007798 -
The Neuroblastoma Microenvironment, Heterogeneity and Immunotherapeutic Approaches.
Polychronopoulos PA, Bedoya-Reina OC, Johnsen JI. · · 2024 · cited 9× · PMID 38791942 · DOI 10.3390/cancers16101863 -
Immunotherapy with anti-G<sub>D2</sub> monoclonal antibody in infants with high-risk neuroblastoma.
Kushner BH, Modak S, Kramer K, Basu EM, et al · · 2023 · cited 8× · PMID 35913764 · DOI 10.1002/ijc.34233
Verify or expand the search:
- PubMed search for NCT04501757
- Europe PMC full search
- ASCO Meeting Library
- ESMO Meeting Library
- bioRxiv preprints
- medRxiv preprints
- Google Scholar
Related trials
Other recruiting trials for High-Risk Neuroblastoma
Currently open trials in the same condition.
- NCT07502287 — Dual-Target GD2/B7-H3 CAR-NK Cells for Pediatric Relapsed or Refractory Neuroblastoma · Phase 1, PHASE2 · recruiting
- NCT07007117 — PHOX2B PC-CAR T Cells for Relapsed Neuroblastoma · Phase 1 · recruiting
- NCT05272371 — Immunotherapy With Dinutuximab Beta in Combination With Chemotherapy for the Treatment of Patients With Primary Neurobla · Phase 1 · recruiting
Other Memorial Sloan Kettering Cancer Center trials
Trials by the same sponsor.
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- NCT07483307 — A Study of the Impact of Endocrine Therapy on Surgical Outcomes in People With Breast Cancer · Phase 2 · recruiting
- NCT07459673 — HERizon-Breast: A ctDNA-Guided Adaptive Study of Sequential Anti-HER2 Therapies and CNS Prophylaxis to Induce Long-Term · Phase 2 · recruiting
- NCT07449195 — A Study Comparing Two Optical Coherence Tomography Devices in People With Ocular Tumors · NA · recruiting
Verify against primary sources
- ClinicalTrials.gov — authoritative US registry record
- WHO ICTRP — international registry index
- EU Clinical Trials Register
- Sponsor press releases (Google)
- Trial protocol + status: ClinicalTrials.gov NCT04501757 (US National Library of Medicine, public domain)
- Publications: Europe PMC API search by NCT ID, retrieved 10 June 2026
- Drug + disease cross-links: matched in real time against Drug Landscape's normalised drug + company + condition tables
- Sponsor: as reported to ClinicalTrials.gov by Memorial Sloan Kettering Cancer Center
- Last refreshed: 8 December 2022
Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04501757.
Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing