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NCT04321980

A Clinical Study to Measure the Effect of OP-101 After Being Administered Subcutaneous in Healthy Volunteers

Completed Phase 1 Results posted Last updated 14 June 2021
What this trial tests

Phase 1 trial testing OP-101 in Healthy in 8 participants. Completed in 22 May 2020.

Timeline
19 March 2020
Primary endpoint
22 May 2020
22 May 2020

Quick facts

Lead sponsorOrpheris, Inc.
PhasePhase 1
StatusCompleted
Study typeINTERVENTIONAL
Allocationnon randomized
Designsequential
Maskingnone
Primary purposetreatment
Enrollment8
Start date19 March 2020
Primary completion22 May 2020
Estimated completion22 May 2020
Sites1 location across Australia

Drugs / interventions tested

Conditions studied

Sponsor

Orpheris, Inc.

Who can join

Adults 18 to 65, any sex, with Healthy. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Number of Participants With Treatment Emergent Adverse Events (TEAEs) and Serious Adverse Events Primary · Up to Day 15

An adverse event (AE) was defined as any untoward medical occurrence in a clinical investigation participant administered a pharmaceutical product, which does not necessarily have a causal relationship with this treatment. A TEAE (treatment-emergent adverse event) was defined as an AE that emerges, having been absent prior to the study, or an AE that worsens in severity after the first dose of the study drug. Serious AE (SAE) was an AE resulting in any of the following outcomes: death; life-threatening adverse event, required hospitalization or prolongation of existing hospitalization; persist

Any TEAE
GroupValue95% CI
Cohort 1: 4 mg/kg2
Cohort 2: 8 mg/kg3
Any SAE
GroupValue95% CI
Cohort 1: 4 mg/kg0
Cohort 2: 8 mg/kg0
Pharmacokinetics: Maximum Observed Plasma Concentration (Cmax) of OP-101 Secondary · Pre-dose, 0.5 hours and 1, 2, 4, 6, 8, 10, 12, 16, 24, 30-36, 48 hours post-dose

Cmax: maximum observed plasma concentration.

GroupValue95% CI
Cohort 1: 4 mg/kg3.473± 0.8183
Cohort 2: 8 mg/kg6.640± 0.6073
Pharmacokinetics: Time to Reach Maximum Plasma Concentration (Tmax) of OP-101 Secondary · Pre-dose, 0.5 hours and at 1, 2, 4, 6, 8, 10, 12, 16, 24, 30-36, 48 hours post-dose

Tmax: time to reach maximum observed plasma concentration.

GroupValue95% CI
Cohort 1: 4 mg/kg14.01510.00 – 16.05
Cohort 2: 8 mg/kg16.00012.00 – 24.05
Pharmacokinetics: Area Under the Concentration Versus Time Curve From Time Zero to the Last Quantifiable Concentration (AUC0-last) of OP-101 Secondary · Pre-dose, 0.5 hours and 1, 2, 4, 6, 8, 10, 12, 16, 24, 30-36, 48 hours post-dose

AUC0-last: Area under the concentration versus time curve from time zero to the last quantifiable concentration (Clast).

GroupValue95% CI
Cohort 1: 4 mg/kg80.940± 51.8190
Cohort 2: 8 mg/kg212.325± 30.6459
Pharmacokinetics: Area Under the Concentration Versus Time Curve From Time Zero to 48 Hour Post Dose Time Point (AUC0-48) of OP-101 Secondary · Pre-dose, 0.5 hours and 1, 2, 4, 6, 8, 10, 12, 16, 24, 30-36, 48 hours post-dose

Area under the concentration versus time curve from time zero to 48 hour post dose time point.

GroupValue95% CI
Cohort 1: 4 mg/kg121.705± 16.9069
Cohort 2: 8 mg/kg222.173± 12.4690
Pharmacokinetics: Renal Clearance (CLR) for OP-101 Secondary · Pre-dose, 0 to 4, 4 to 8, 8 to 12, 12 to 18, 18 to 24, and 24 to 48 hours post dose

CLR was defined as renal clearance of the drug from plasma utilizing the AUC and cumulative amount of unchanged study drug excreted into the urine (Ae) to the same duration (as Amount recovered/AUC at 0-48 hours).

GroupValue95% CI
Cohort 1: 4 mg/kg0.175± 0.0354
Cohort 2: 8 mg/kg0.150± 0.0606

Adverse events — posted to ClinicalTrials.gov

Time frame: Up to Day 15. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Cohort 1: 4 mg/kg
Serious: 0/4 (0%)
Deaths: 0/4
Cohort 2: 8 mg/kg
Serious: 0/4 (0%)
Deaths: 0/4
Other adverse events (5 terms — click to expand)

ReactionSystemCohort 1: 4 mg/kgCohort 2: 8 mg/kg
Injection site erythemaGeneral disorders
Injection site massGeneral disorders
Injection site painGeneral disorders
Injection site pallorGeneral disorders
DysmenorrhoeaReproductive system and breast disorders

Data from ClinicalTrials.gov NCT04321980 adverse events section.

Sponsor's own description

A clinical study to measure the Safety, Tolerability, and Pharmacokinetics of OP-101 After Subcutaneous Administration in Healthy Volunteers

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Dendrimers, an Emerging Opportunity in Personalized Medicine?
    Caminade AM. · · 2022 · cited 39× · PMID 36013283 · DOI 10.3390/jpm12081334
  2. Dendrimer-Mediated Delivery of DNA and RNA Vaccines.
    Kisakova LA, Apartsin EK, Nizolenko LF, Karpenko LI. · · 2023 · cited 29× · PMID 37111593 · DOI 10.3390/pharmaceutics15041106
  3. Dendrimers in Corneal Drug Delivery: Recent Developments and Translational Opportunities.
    Dhull A, Yu C, Wilmoth AH, Chen M, et al · · 2023 · cited 28× · PMID 37376040 · DOI 10.3390/pharmaceutics15061591
  4. Targeted drug delivery for maternal and perinatal health: Challenges and opportunities.
    Sharma A, Sah N, Kannan S, Kannan RM. · · 2021 · cited 22× · PMID 34454979 · DOI 10.1016/j.addr.2021.113950
  5. Dendrimers and Derivatives as Multifunctional Nanotherapeutics for Alzheimer's Disease.
    Moreira DA, Santos SD, Leiro V, Pêgo AP. · · 2023 · cited 18× · PMID 37111540 · DOI 10.3390/pharmaceutics15041054
  6. PSMA-targeted dendrimer as an efficient anticancer drug delivery vehicle for prostate cancer.
    Dhull A, Wei J, Pulukuri AJ, Rani A, et al · · 2024 · cited 17× · PMID 38440933 · DOI 10.1039/d3nr06520k
  7. Galactosylated hydroxyl-polyamidoamine dendrimer targets hepatocytes and improves therapeutic outcomes in a severe model of acetaminophen poisoning-induced liver failure.
    Porterfield JE, Sharma R, Jimenez AS, Sah N, et al · · 2023 · cited 9× · PMID 37206223 · DOI 10.1002/btm2.10486
  8. Engineering pH-Responsive Dendrimer-STAT3 Inhibitor Conjugates for Intracellular Delivery.
    Siva Sankara C, Shanbhag AR, Rincón Díaz D, Hodges CA, et al · · 2026 · PMID 41307497 · DOI 10.1021/acs.biomac.5c01648

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Other trials of OP-101

Trials testing the same drug.

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Trials by the same sponsor.

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