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NCT04209725

A Study of CPX-351 (Vyxeos™) With Quizartinib for the Treatment of FLT3-ITD Mutation-Positive Acute Myeloid Leukemia

Terminated Phase 2 Results posted Last updated 5 December 2023
What this trial tests

Phase 2 trial testing CPX-351 in Leukemia, Myeloid, Acute in 1 participant. Terminated before completion.

Timeline
3 June 2020
Primary endpoint
20 April 2021
20 April 2021

Quick facts

Lead sponsorSCRI Development Innovations, LLC
PhasePhase 2
StatusTerminated
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment1
Start date3 June 2020
Primary completion20 April 2021
Estimated completion20 April 2021
Sites5 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

SCRI Development Innovations, LLC — full company profile →

Who can join

Adults 18 to 80, any sex, with Leukemia, Myeloid, Acute. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Number of Patients With Treatment Related Adverse Events After Taking CPX-351 and Quizartinib Primary · Collected during treatment and for 30 days after last dose, approximately 35 total days for the 1 patient treated.

Counting the number of patients with treatment related adverse events as a measure of safety and tolerability.

GroupValue95% CI
CPX-351 and Quizartinib Treatment1
Overall Survival (OS) Secondary · Up to 8 months

Overall survival is defined as the time from the first date of treatment until death as a result of any cause. For OS time, patients that have not died or are lost to follow-up will be censored at the date the patient was last known to be alive or the date of last contact.

GroupValue95% CI
CPX-351 and Quizartinib Treatment7.7
Number of Patients Who Can Receive Consolidation and Maintenance Therapy Secondary · approximately 3 months

Patients who proceed through induction to next stages of consolidation and maintenance

GroupValue95% CI
CPX-351 and Quizartinib Treatment0
Treatment-related Mortality Rate Secondary · Observed during treatment and for 30 days after last dose, so approximately 35 days for the 1 patient treated.

As determined by the number of treatment related deaths during study treatment

GroupValue95% CI
CPX-351 and Quizartinib Treatment0

Adverse events — posted to ClinicalTrials.gov

Time frame: Collected for 30 days after last dose, so approximately 35 days for the 1 patient treated.. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

CPX-351 and Quizartinib Treatment
Serious: 0/1 (0%)
Deaths: 1/1
Other adverse events (13 terms — click to expand)

ReactionSystemCPX-351 and Quizartinib Tr…
AnaemiaBlood and lymphatic system disorders
Febrile neutropeniaBlood and lymphatic system disorders
NeutropeniaBlood and lymphatic system disorders
ThrombocytopeniaBlood and lymphatic system disorders
DiarrhoeaGastrointestinal disorders
HypocalcaemiaMetabolism and nutrition disorders
ChillsGeneral disorders
Electrocardiogram QT prolongedInvestigations
Orthostatic hypotensionVascular disorders
InsomniaPsychiatric disorders
ConstipationGastrointestinal disorders
Mucosal inflammationGeneral disorders
HeadacheNervous system disorders

Data from ClinicalTrials.gov NCT04209725 adverse events section.

Sponsor's own description

This is a research study to be done at multiple sites in participants with advanced acute myeloid leukemia (AML) that have a mutation in Fms-like tyrosine kinase-3 internal tandem duplications (FLT3-ITD). This study is to learn more about an investigational drug, quizartinib, being tested with the anti-cancer medicine CPX-351 (also called Vyxeos™), which is approved and widely used to treat AML. The purpose of this study is to assess the safety, tolerability and survival of patients receiving the combination of CPX-351 and quizartinib.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Recent advances in targeted therapies in acute myeloid leukemia.
    Bhansali RS, Pratz KW, Lai C. · · 2023 · cited 151× · PMID 36966300 · DOI 10.1186/s13045-023-01424-6
  2. A review of FLT3 inhibitors in acute myeloid leukemia.
    Zhao JC, Agarwal S, Ahmad H, Amin K, et al · · 2022 · cited 137× · PMID 34774343 · DOI 10.1016/j.blre.2021.100905
  3. <i>FLT3</i> Mutations in Acute Myeloid Leukemia: Key Concepts and Emerging Controversies.
    Kennedy VE, Smith CC. · · 2020 · cited 132× · PMID 33425766 · DOI 10.3389/fonc.2020.612880
  4. FLT3 mutated acute myeloid leukemia: 2021 treatment algorithm.
    Daver N, Venugopal S, Ravandi F. · · 2021 · cited 115× · PMID 34045454 · DOI 10.1038/s41408-021-00495-3
  5. Advances in Acute Myeloid Leukemia: Recently Approved Therapies and Drugs in Development.
    Stanchina M, Soong D, Zheng-Lin B, Watts JM, et al · · 2020 · cited 62× · PMID 33139625 · DOI 10.3390/cancers12113225
  6. Advances in targeted therapy for acute myeloid leukemia.
    Yu J, Jiang PYZ, Sun H, Zhang X, et al · · 2020 · cited 48× · PMID 32477567 · DOI 10.1186/s40364-020-00196-2
  7. New drugs before, during, and after hematopoietic stem cell transplantation for patients with acute myeloid leukemia.
    Mohty R, El Hamed R, Brissot E, Bazarbachi A, et al · · 2023 · cited 28× · PMID 36722403 · DOI 10.3324/haematol.2022.280798
  8. What Does the Economic Burden of Acute Myeloid Leukemia Treatment Look Like for the Next Decade? An Analysis of Key Findings, Challenges and Recommendations.
    Forsythe A, Sandman K. · · 2021 · cited 16× · PMID 33981169 · DOI 10.2147/jbm.s279736

Verify or expand the search:

Other trials of CPX-351

Trials testing the same drug.

Other recruiting trials for Leukemia, Myeloid, Acute

Currently open trials in the same condition.

Other SCRI Development Innovations, LLC trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04209725.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing