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NCT04102020: VIALE-M

A Study of Oral Venetoclax Tablets and Oral Azacitidine as Maintenance Therapy in Adult Participants With Acute Myeloid Leukemia in First Remission After Conventional Chemotherapy

Completed Phase 3 Results posted Last updated 8 April 2026
What this trial tests

Phase 3 trial testing Venetoclax in Acute Myeloid Leukemia (AML) in 112 participants. Completed in 20 February 2026.

Timeline
26 March 2020
Primary endpoint
29 September 2022
20 February 2026

Quick facts

Lead sponsorAbbVie
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationnon randomized
Designsequential
Maskingnone
Primary purposetreatment
Enrollment112
Start date26 March 2020
Primary completion29 September 2022
Estimated completion20 February 2026
Sites156 locations across Italy, Japan, Taiwan, South Korea, Russia, United States, France, Greece

Drugs / interventions tested

Conditions studied

Sponsor

AbbVie — full company profile →

Who can join

18 and older, any sex, with Acute Myeloid Leukemia (AML). Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Number of Participants With Dose-Limiting Toxicities (DLTs) of Venetoclax in Combination With Azacitidine (AZA) (Part 1) Primary · Up to 28 days (Cycle 1)

DLTs are any of the hematologic, nonhematologic toxicities, adverse events (AEs) occurring following administration of venetoclax as described in the protocol and evaluated by the Investigator and the sponsor.

Neutropenia
GroupValue95% CI
Part 1: Venetoclax 400 mg + Azacitidine 20 mg/m^23
Part 1: Venetoclax 400 mg + Azacitidine 36 mg/m^24
Part 1: Venetoclax 400 mg + Azacitidine 50 mg/m^24
Leukopenia
GroupValue95% CI
Part 1: Venetoclax 400 mg + Azacitidine 20 mg/m^21
Part 1: Venetoclax 400 mg + Azacitidine 36 mg/m^20
Part 1: Venetoclax 400 mg + Azacitidine 50 mg/m^20
Thrombocytopenia
GroupValue95% CI
Part 1: Venetoclax 400 mg + Azacitidine 20 mg/m^21
Part 1: Venetoclax 400 mg + Azacitidine 36 mg/m^20
Part 1: Venetoclax 400 mg + Azacitidine 50 mg/m^20
Platelet count decreased
GroupValue95% CI
Part 1: Venetoclax 400 mg + Azacitidine 20 mg/m^21
Part 1: Venetoclax 400 mg + Azacitidine 36 mg/m^20
Part 1: Venetoclax 400 mg + Azacitidine 50 mg/m^20
Number of Participants With DLTs of Venetoclax in Combination With Oral AZA (Part 3 Dose Finding Portion) Primary · Up to 28 days (Cycle 1)

DLTs are hematologic toxicities consisting of any Grade ≥ 3 neutropenia or thrombocytopenia lasting more than 7 days and nonhematologic toxicities as described in the protocol and evaluated by the Investigator and the Sponsor. In addition, AEs that lead to omitting \> 20% of the scheduled dose within the cycle is considered as a DLT unless clearly related to underlying disease. Treatment delay due to toxicity lasting greater than 14 days since the last dose of Venetoclax is also considered a DLT.

Neutropenia
GroupValue95% CI
Part 3: Dose Level 1 - Venetoclax 400mg + CC-486 200mg1
Part 3: Dose Level 2 - Venetoclax 400mg + CC-486 300mg2
Thrombocytopenia
GroupValue95% CI
Part 3: Dose Level 1 - Venetoclax 400mg + CC-486 200mg1
Part 3: Dose Level 2 - Venetoclax 400mg + CC-486 300mg1
Febrile neutropenia
GroupValue95% CI
Part 3: Dose Level 1 - Venetoclax 400mg + CC-486 200mg0
Part 3: Dose Level 2 - Venetoclax 400mg + CC-486 300mg1
Fatigue
GroupValue95% CI
Part 3: Dose Level 1 - Venetoclax 400mg + CC-486 200mg0
Part 3: Dose Level 2 - Venetoclax 400mg + CC-486 300mg1
Neutrophil count decreased
GroupValue95% CI
Part 3: Dose Level 1 - Venetoclax 400mg + CC-486 200mg1
Part 3: Dose Level 2 - Venetoclax 400mg + CC-486 300mg1
Platelet count decreased
GroupValue95% CI
Part 3: Dose Level 1 - Venetoclax 400mg + CC-486 200mg0
Part 3: Dose Level 2 - Venetoclax 400mg + CC-486 300mg1
Dizziness
GroupValue95% CI
Part 3: Dose Level 1 - Venetoclax 400mg + CC-486 200mg1
Part 3: Dose Level 2 - Venetoclax 400mg + CC-486 300mg0

Adverse events — posted to ClinicalTrials.gov

Time frame: All-cause mortality and adverse event tables include events reported from the time of informed consent to the interim cutoff date of 05OCT2022. The median time on follow-up was 446, 687, 389 days for Part 1 VEN400_AZA20, VEN400_AZA36, VEN400_AZA50 and 67.5, 275 days for Part 3 Dose Level 1 (VEN400_CC200), Dose Level 2 (VEN400_CC300), respectively.. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Part 1: Venetoclax 400 mg + Azacitidine 20 mg/m^2
Serious: 5/23 (22%)
Deaths: 3/23
Part 1: Venetoclax 400 mg + Azacitidine 36 mg/m^2
Serious: 7/23 (30%)
Deaths: 5/23
Part 1: Venetoclax 400 mg + Azacitidine 50 mg/m^2
Serious: 5/20 (25%)
Deaths: 1/20
Part 3: Dose Level 1 - Venetoclax 400mg + CC-486 200mg
Serious: 5/30 (17%)
Deaths: 1/30
Part 3: Dose Level 2 - Venetoclax 400mg + CC-486 300mg
Serious: 3/16 (19%)
Deaths: 1/16

Serious adverse events (23 terms)

ReactionSystemPart 1: Venetoclax 400 mg …Part 1: Venetoclax 400 mg …Part 1: Venetoclax 400 mg …Part 3: Dose Level 1 - Ven…Part 3: Dose Level 2 - Ven…
FEBRILE NEUTROPENIABlood and lymphatic system disorders
NEUTROPENIABlood and lymphatic system disorders
THROMBOCYTOPENIABlood and lymphatic system disorders
LEUKOPENIABlood and lymphatic system disorders
ATRIAL FIBRILLATIONCardiac disorders
CARDIAC TAMPONADECardiac disorders
VERTIGOEar and labyrinth disorders
COLITISGastrointestinal disorders
ANORECTAL INFECTIONInfections and infestations
BACILLUS INFECTIONInfections and infestations
CELLULITISInfections and infestations
COVID-19Infections and infestations
COVID-19 PNEUMONIAInfections and infestations
PNEUMONIAInfections and infestations
PSEUDOMONAL SEPSISInfections and infestations
SEPSISInfections and infestations
NEUTROPHIL COUNT DECREASEDInvestigations
EUGLYCAEMIC DIABETIC KETOACIDOSISMetabolism and nutrition disorders
HYPONATRAEMIAMetabolism and nutrition disorders
HAEMORRHAGIC STROKENervous system disorders
HEADACHENervous system disorders
SYNCOPENervous system disorders
ACUTE KIDNEY INJURYRenal and urinary disorders
Other adverse events (121 terms — click to expand)

ReactionSystemPart 1: Venetoclax 400 mg …Part 1: Venetoclax 400 mg …Part 1: Venetoclax 400 mg …Part 3: Dose Level 1 - Ven…Part 3: Dose Level 2 - Ven…
NEUTROPENIABlood and lymphatic system disorders
NAUSEAGastrointestinal disorders
THROMBOCYTOPENIABlood and lymphatic system disorders
DIARRHOEAGastrointestinal disorders
VOMITINGGastrointestinal disorders
ANAEMIABlood and lymphatic system disorders
CONSTIPATIONGastrointestinal disorders
LEUKOPENIABlood and lymphatic system disorders
COVID-19Infections and infestations
ABDOMINAL PAIN UPPERGastrointestinal disorders
PLATELET COUNT DECREASEDInvestigations
WHITE BLOOD CELL COUNT DECREASEDInvestigations
DIZZINESSNervous system disorders
PRURITUSSkin and subcutaneous tissue disorders
LYMPHOPENIABlood and lymphatic system disorders
FATIGUEGeneral disorders
ALANINE AMINOTRANSFERASE INCREASEDInvestigations
NEUTROPHIL COUNT DECREASEDInvestigations
HEADACHENervous system disorders
RASHSkin and subcutaneous tissue disorders
ABDOMINAL PAINGastrointestinal disorders
DYSPEPSIAGastrointestinal disorders
ASTHENIAGeneral disorders
INFLUENZA LIKE ILLNESSGeneral disorders
PAINGeneral disorders
PYREXIAGeneral disorders
RHINITISInfections and infestations
URINARY TRACT INFECTIONInfections and infestations
ASPARTATE AMINOTRANSFERASE INCREASEDInvestigations
HYPERURICAEMIAMetabolism and nutrition disorders
HYPOKALAEMIAMetabolism and nutrition disorders
ARTHRALGIAMusculoskeletal and connective tissue disorders
PAIN IN EXTREMITYMusculoskeletal and connective tissue disorders
COUGHRespiratory, thoracic and mediastinal disorders
FEBRILE NEUTROPENIABlood and lymphatic system disorders
TINNITUSEar and labyrinth disorders
VISION BLURREDEye disorders
ABDOMINAL DISTENSIONGastrointestinal disorders
ANAL FISTULAGastrointestinal disorders
DENTAL CARIESGastrointestinal disorders

Most-reported serious reactions: FEBRILE NEUTROPENIA, NEUTROPENIA, THROMBOCYTOPENIA, LEUKOPENIA, ATRIAL FIBRILLATION, CARDIAC TAMPONADE, VERTIGO, COLITIS.

Data from ClinicalTrials.gov NCT04102020 adverse events section.

Sponsor's own description

This study will be conducted in two parts. Part 1 will be the Dose Confirmation portion to determine recommended Phase 3 dose (RPTD) of venetoclax in combination with azacitidine (AZA). Part 3 will be the Dose Finding portion to determine RPTD of venetoclax in combination with AZA. Part 2 and Part 3 Randomization of the study were removed.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Recent advances in targeted therapies in acute myeloid leukemia.
    Bhansali RS, Pratz KW, Lai C. · · 2023 · cited 151× · PMID 36966300 · DOI 10.1186/s13045-023-01424-6
  2. Epigenetics-targeted drugs: current paradigms and future challenges.
    Dai W, Qiao X, Fang Y, Guo R, et al · · 2024 · cited 131× · PMID 39592582 · DOI 10.1038/s41392-024-02039-0
  3. Crosstalk between metabolic reprogramming and epigenetics in cancer: updates on mechanisms and therapeutic opportunities.
    Ge T, Gu X, Jia R, Ge S, et al · · 2022 · cited 129× · PMID 36266736 · DOI 10.1002/cac2.12374
  4. Acute Myeloid Leukemia: 2025 Update on Diagnosis, Risk-Stratification, and Management.
    Shimony S, Stahl M, Stone RM. · · 2025 · cited 102× · PMID 39936576 · DOI 10.1002/ajh.27625
  5. The clinical impact of the molecular landscape of acute myeloid leukemia.
    Kayser S, Levis MJ. · · 2023 · cited 91× · PMID 36722402 · DOI 10.3324/haematol.2022.280801
  6. Maintenance therapy in acute myeloid leukemia: advances and controversies.
    Senapati J, Kadia TM, Ravandi F. · · 2023 · cited 26× · PMID 37139599 · DOI 10.3324/haematol.2022.281810
  7. Venetoclax in Acute Myeloid Leukemia: Molecular Basis, Evidences for Preclinical and Clinical Efficacy and Strategies to Target Resistance.
    Garciaz S, Saillard C, Hicheri Y, Hospital MA, et al · · 2021 · cited 20× · PMID 34830763 · DOI 10.3390/cancers13225608
  8. How We Incorporate Venetoclax in Treatment Regimens for Acute Myeloid Leukemia.
    Maiti A, Konopleva MY. · · 2022 · cited 19× · PMID 35072368 · DOI 10.1097/ppo.0000000000000567

Verify or expand the search:

Other trials of Venetoclax

Trials testing the same drug.

Other recruiting trials for Acute Myeloid Leukemia (AML)

Currently open trials in the same condition.

Other AbbVie trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04102020.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing