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NCT04051944

A Study to Assess Long-term Safety, Tolerability and Efficacy of Rozanolixizumab in Subjects With Chronic Inflammatory Demyelinating Polyradiculoneuropathy

Completed Phase 2 Results posted Last updated 3 November 2022
What this trial tests

Phase 2 trial testing Rozanolixizumab in Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP) in 21 participants. Completed in 10 November 2021.

Timeline
21 August 2019
Primary endpoint
10 November 2021
10 November 2021

Quick facts

Lead sponsorUCB Biopharma SRL
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment21
Start date21 August 2019
Primary completion10 November 2021
Estimated completion10 November 2021
Sites14 locations across Denmark, France, Netherlands, Belgium, United Kingdom, Germany, United States, Spain

Drugs / interventions tested

Conditions studied

Sponsor

UCB Biopharma SRL — full company profile →

Who can join

18 and older, any sex, with Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP). Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Number of Participants With Treatment-emergent Adverse Event (TEAEs) Primary · From Baseline until Follow-Up Visit (up to Week 84)

An Adverse Event (AE) is any untoward medical occurrence in a participant or clinical investigation subject administered a pharmaceutical product, which does not necessarily had a causal relationship with this treatment. An AE could therefore be any unfavorable and unintended sign, symptom, or disease temporally associated with the use of a medicinal (investigational) product, whether or not related to the medicinal (investigational) product. A TEAE was defined as any event that was not present prior the first administration of investigational medicinal product (IMP) in CIDP04 study or any unr

GroupValue95% CI
Rozanolixizumab (Newly Treated)10
Rozanolixizumab (Previously Treated)10

Adverse events — posted to ClinicalTrials.gov

Time frame: From Baseline until Follow-Up Visit (up to Week 84). Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Rozanolixizumab (Newly Treated)
Serious: 2/11 (18%)
Deaths: 0/11
Rozanolixizumab (Previously Treated)
Serious: 2/10 (20%)
Deaths: 0/10

Serious adverse events (4 terms)

ReactionSystemRozanolixizumab (Newly Tre…Rozanolixizumab (Previousl…
Urinary tract infectionInfections and infestations
Malignant melanomaNeoplasms benign, malignant and unspecified (incl cysts and polyps)
Chronic inflammatory demyelinating polyradiculoneuropathyNervous system disorders
Sensory lossNervous system disorders
Other adverse events (21 terms — click to expand)

ReactionSystemRozanolixizumab (Newly Tre…Rozanolixizumab (Previousl…
Blood immunoglobulin G decreasedInvestigations
HeadacheNervous system disorders
FatigueGeneral disorders
ConstipationGastrointestinal disorders
PyrexiaGeneral disorders
InfluenzaInfections and infestations
NasopharyngitisInfections and infestations
Upper respiratory tract infectionInfections and infestations
Urinary tract infectionInfections and infestations
Muscle strainInjury, poisoning and procedural complications
FallInjury, poisoning and procedural complications
Joint swellingMusculoskeletal and connective tissue disorders
Muscle spasmsMusculoskeletal and connective tissue disorders
Muscular weaknessMusculoskeletal and connective tissue disorders
NeuralgiaNervous system disorders
Sensory lossNervous system disorders
DiarrhoeaGastrointestinal disorders
Peripheral swellingGeneral disorders
Back painMusculoskeletal and connective tissue disorders
RhinorrhoeaRespiratory, thoracic and mediastinal disorders
RashSkin and subcutaneous tissue disorders

Most-reported serious reactions: Urinary tract infection, Malignant melanoma, Chronic inflammatory demyelinating polyradiculoneuropathy, Sensory loss.

Data from ClinicalTrials.gov NCT04051944 adverse events section.

Sponsor's own description

The purpose of the study is to assess long-term safety and tolerability of weekly doses of rozanolixizumab in subjects with chronic inflammatory demyelinating polyradiculoneuropathy (CIDP).

Publications & conference data

5 peer-reviewed publications reference this trial (live from Europe PMC):

  1. The therapeutic age of the neonatal Fc receptor.
    Pyzik M, Kozicky LK, Gandhi AK, Blumberg RS. · · 2023 · cited 166× · PMID 36726033 · DOI 10.1038/s41577-022-00821-1
  2. Rozanolixizumab: First Approval.
    Hoy SM. · · 2023 · cited 24× · PMID 37656420 · DOI 10.1007/s40265-023-01933-1
  3. Efficacy, safety and tolerability of rozanolixizumab in patients with chronic inflammatory demyelinating polyradiculoneuropathy: a randomised, subject-blind, investigator-blind, placebo-controlled, phase 2a trial and open-label extension study.
    Querol L, De Sèze J, Dysgaard T, Levine T, et al · · 2024 · cited 18× · PMID 38729747 · DOI 10.1136/jnnp-2023-333112
  4. Targeting the Neonatal Fc Receptor in Autoimmune Diseases: Pipeline and Progress.
    Gjølberg TT, Mester S, Calamera G, Telstad JS, et al · · 2025 · cited 10× · PMID 40156757 · DOI 10.1007/s40259-025-00708-2
  5. Targeting the neonatal Fc receptor (FcRn) to treat autoimmune diseases and maternal-fetal immune cytopenias.
    Wyckoff SL, Hudson KE. · · 2021 · cited 7× · PMID 33650699 · DOI 10.1111/trf.16341

Verify or expand the search:

Other trials of Rozanolixizumab

Trials testing the same drug.

Other recruiting trials for Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP)

Currently open trials in the same condition.

Other UCB Biopharma SRL trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04051944.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing