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NCT04007991: D1AMOND

Ecopipam Tablets to Study Tourette's Syndrome in Children and Adolescents

Completed Phase 2 Results posted Last updated 4 October 2023
What this trial tests

Phase 2 trial testing Ecopipam in Tourette Syndrome in 153 participants. Completed in 23 September 2021.

Timeline
28 June 2019
Primary endpoint
23 September 2021
23 September 2021

Quick facts

Lead sponsorEmalex Biosciences Inc.
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingtriple
Primary purposetreatment
Enrollment153
Start date28 June 2019
Primary completion23 September 2021
Estimated completion23 September 2021
Sites70 locations across France, Germany, Poland, Canada, United States

Drugs / interventions tested

Conditions studied

Sponsor

Emalex Biosciences Inc. — full company profile →

Who can join

Adults 6 to 17, any sex, with Tourette Syndrome. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Change From Baseline in the Yale Global Tic Severity Scale-Total Tic Score (YGTSS-TTS) at Week 12 Primary · Baseline, Week 12

The YGTSS was a semi-structured clinical interview designed to measure the tic severity. This scale consisted of a tic inventory, with 5 separate rating scales to rate the severity of symptoms, and an impairment ranking. Ratings were made along 5 different dimensions on a scale of 0=none to 5=severe for motor and vocal tics, each including number, frequency, intensity, complexity, and interference. The YGTSS TTS was the summation of the severity scores of motor and vocal tics. The total tic score (TTS) ranged from 0 (none) to 50 (severe) with higher score represent more severe symptoms. A nega

GroupValue95% CI
Ecopipam HCI 2 mg/kg/Day-9.87± 1.062
Placebo-6.42± 1.006
Change From Baseline in Clinical Global Impression of Tourette Syndrome Severity (CGI-TS-S) at Week 12 Secondary · Baseline, Week 12

Clinical Global Impression (CGI) scale was used to assess overall severity on a 7-point Likert scale consisted of 2 reliable and valid 7-item Likert scales used to assess severity and change in clinical symptoms. The CGI severity scale ranges from 1 = Normal, not at all ill; 2 = Borderline ill; 3 = Mildly ill; 4 = Moderately ill; 5 = Markedly ill; 6 = Severely ill; 7 = Among the most extremely ill subject. 1 = "normal, not ill at all" to 7 = "extremely ill." A negative change indicates improvement in the condition.

GroupValue95% CI
Ecopipam HCI 2 mg/kg/Day-0.91± 0.141
Placebo-0.53± 0.130

Adverse events — posted to ClinicalTrials.gov

Time frame: Screening up to 30 days after the last dose ( up to Week 16). Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Ecopipam HCI 2 mg/kg/Day
Serious: 2/76 (3%)
Deaths: 0/76
Placebo
Serious: 1/77 (1%)
Deaths: 0/77

Serious adverse events (3 terms)

ReactionSystemEcopipam HCI 2 mg/kg/DayPlacebo
VomitingGastrointestinal disorders
Suicidal ideationPsychiatric disorders
Coronavirus infectionInfections and infestations
Other adverse events (31 terms — click to expand)

ReactionSystemEcopipam HCI 2 mg/kg/DayPlacebo
HeadacheNervous system disorders
InsomniaPsychiatric disorders
SomnolenceNervous system disorders
FatigueGeneral disorders
NasopharyngitisInfections and infestations
NauseaGastrointestinal disorders
AnxietyPsychiatric disorders
RestlessnessPsychiatric disorders
Decreased appetiteMetabolism and nutrition disorders
ContusionInjury, poisoning and procedural complications
DizzinessNervous system disorders
PyrexiaGeneral disorders
DiarrheaGastrointestinal disorders
Depressed moodPsychiatric disorders
IrritabilityPsychiatric disorders
Middle insomniaPsychiatric disorders
Sleep disorderPsychiatric disorders
FallInjury, poisoning and procedural complications
Muscle strainInjury, poisoning and procedural complications
SunburnInjury, poisoning and procedural complications
Abdominal painGastrointestinal disorders
Abdominal pain upperGastrointestinal disorders
Nasal congestionRespiratory, thoracic and mediastinal disorders
Oropharyngeal painRespiratory, thoracic and mediastinal disorders
DepressionPsychiatric disorders
TicPsychiatric disorders
Back painMusculoskeletal and connective tissue disorders
MyalgiaMusculoskeletal and connective tissue disorders
Neck painMusculoskeletal and connective tissue disorders
VomitingGastrointestinal disorders
Coronavirus infectionInfections and infestations

Most-reported serious reactions: Vomiting, Suicidal ideation, Coronavirus infection.

Data from ClinicalTrials.gov NCT04007991 adverse events section.

Sponsor's own description

This study evaluates the effect of ecopipam tablets in children and adolescents in the treatment of Tourette's Syndrome (TS). Half of the participants will receive ecopipam tablets, while the other half will receive matching placebo tablets

Publications & conference data

4 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Current Management of Tics and Tourette Syndrome: Behavioral, Pharmacologic, and Surgical Treatments.
    Billnitzer A, Jankovic J. · · 2020 · cited 71× · PMID 32856174 · DOI 10.1007/s13311-020-00914-6
  2. Tourette Syndrome Treatment Updates: a Review and Discussion of the Current and Upcoming Literature.
    Frey J, Malaty IA. · · 2022 · cited 29× · PMID 35107785 · DOI 10.1007/s11910-022-01177-8
  3. Treatment of dystonia and tics.
    Bellows S, Jankovic J. · · 2020 · cited 6× · PMID 34316614 · DOI 10.1016/j.prdoa.2019.11.005
  4. Plain Language Summary of a Phase 2b Randomized Controlled Trial of Ecopipam and Its 12-Month Open-Label Extension in Children and Adolescents With Tourette Syndrome
    Gilbert D, Kim D, Miller M, Atkinson S, et al · · 2026

Verify or expand the search:

Other trials of Ecopipam

Trials testing the same drug.

Other recruiting trials for Tourette Syndrome

Currently open trials in the same condition.

Other Emalex Biosciences Inc. trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT04007991.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing