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NCT03963999

Validating Ultrasound Biomarkers for Hepatic Sinusoidal Obstruction Syndrome in Pediatric Hematopoietic Cell Transplant Patients

Withdrawn Phase 4 Last updated 13 January 2020
What this trial tests

Phase 4 trial testing Ultrasound Elastography in Sinusoidal Obstruction Syndrome. Withdrawn.

Timeline
1 April 2020
Primary endpoint
30 April 2024
1 April 2025

Quick facts

Lead sponsorChildren's Mercy Hospital Kansas City
PhasePhase 4
StatusWithdrawn
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposediagnostic
Start date1 April 2020
Primary completion30 April 2024
Estimated completion1 April 2025
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Children's Mercy Hospital Kansas City

Who can join

Adults 1 Month to 25, any sex, with Sinusoidal Obstruction Syndrome or Veno Occlusive Disease, Hepatic. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

Hepatic veno-occlusive disease/sinusoidal obstructive syndrome (VOD/SOS) is a potentially fatal complication of hematopoietic cell transplant (HCT). Historically VOD/SOS has been clinically diagnosed using the modified Seattle criteria or the Baltimore criteria. The modified Seattle Criteria define VOD/SOS diagnosis is made when two of the following three criteria are present in a patient within 21 days of transplantation: hyperbilirubinemia (total serum bilirubin \> 2 mg/dL), hepatomegaly or right upper quadrant liver pain, and weight gain (\> 2% of baseline) or ascites. Other conditions like graft versus host disease, sepsis syndrome (fever and hypotension), cardiac failure, or tumor infiltration) have to be excluded. This definition was from a well-designed retrospective cohort study on 255 adult and pediatric HCT patients in which the VOD/SOS incidence was 21%. McDonald et al followed up this work with a prospective cohort study of 355 patients noting an incidence of VOD/SOS of 54%. These seminal studies have had a major impact on the field by defining clinical diagnostic criteria. An alternative diagnostic criteria (Baltimore criteria) was proposed by Jones et al as a part of a well-designed retrospective review of 235 HCT patients finding a VOD/SOS incidence of 22%. Jones defined VOD/SOS as the presence of hyperbilirubinemia (total serum bilirubin \> 2 mg/dL) along with at least 2 of 3 other findings: hepatomegaly, ascites, and weight gain (\> 5% of baseline).

Publications & conference data

No peer-reviewed publications indexed yet for this trial.

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Other trials of Ultrasound Elastography

Trials testing the same drug.

Other recruiting trials for Sinusoidal Obstruction Syndrome

Currently open trials in the same condition.

Other Children's Mercy Hospital Kansas City trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

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