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NCT03904862
Testing the Safety and Tolerability of CX-4945 in Patients With Recurrent Medulloblastoma Who May or May Not Have Surgery
Phase 1, PHASE2 trial testing CX 4945 in Medulloblastoma, Childhood in 21 participants. Terminated before completion.
11 August 2025
Quick facts
| Lead sponsor | Pediatric Brain Tumor Consortium |
|---|---|
| Phase | Phase 1, PHASE2 |
| Status | Terminated |
| Study type | INTERVENTIONAL |
| Allocation | non randomized |
| Design | parallel |
| Masking | none |
| Primary purpose | treatment |
| Enrollment | 21 |
| Start date | 25 July 2019 |
| Primary completion | 11 August 2025 |
| Estimated completion | 11 August 2025 |
| Sites | 12 locations across United States |
Drugs / interventions tested
- CX 4945 — full drug profile →
Conditions studied
- Medulloblastoma, Childhood — all drugs for Medulloblastoma, Childhood →
- Medulloblastoma Recurrent — all drugs for Medulloblastoma Recurrent →
- Medulloblastoma — all drugs for Medulloblastoma →
Sponsor
Pediatric Brain Tumor Consortium
Who can join
3 and older, any sex, with Medulloblastoma, Childhood or Medulloblastoma Recurrent. Patients with the condition only — healthy volunteers not accepted.
Sponsor's own description
This is a multi center, Phase I, Phase II and surgical study of the CX-4945 drug (silmitasertib sodium) for patients with recurrent SHH (Sonic Hedgehog) medulloblastoma
Publications & conference data
8 peer-reviewed publications reference this trial (live from Europe PMC):
-
Protein kinase CK2: a potential therapeutic target for diverse human diseases.
Borgo C, D'Amore C, Sarno S, Salvi M, et al · · 2021 · cited 273× · PMID 33994545 · DOI 10.1038/s41392-021-00567-7 -
Role of CK2 inhibitor CX-4945 in anti-cancer combination therapy - potential clinical relevance.
D'Amore C, Borgo C, Sarno S, Salvi M. · · 2020 · cited 74× · PMID 33052585 · DOI 10.1007/s13402-020-00566-w -
The DYRK Family of Kinases in Cancer: Molecular Functions and Therapeutic Opportunities.
Boni J, Rubio-Perez C, López-Bigas N, Fillat C, et al · · 2020 · cited 68× · PMID 32751160 · DOI 10.3390/cancers12082106 -
CK2 Regulation: Perspectives in 2021.
Roffey SE, Litchfield DW. · · 2021 · cited 63× · PMID 34680478 · DOI 10.3390/biomedicines9101361 -
New Insights Into the Role of Phenotypic Plasticity and EMT in Driving Cancer Progression.
Bhatia S, Wang P, Toh A, Thompson EW. · · 2020 · cited 63× · PMID 32391381 · DOI 10.3389/fmolb.2020.00071 -
Molecular stratifications, biomarker candidates and new therapeutic options in current medulloblastoma treatment approaches.
Menyhárt O, Győrffy B. · · 2020 · cited 60× · PMID 31970590 · DOI 10.1007/s10555-020-09854-1 -
The chromosome 21 kinase DYRK1A: emerging roles in cancer biology and potential as a therapeutic target.
Rammohan M, Harris E, Bhansali RS, Zhao E, et al · · 2022 · cited 49× · PMID 35220406 · DOI 10.1038/s41388-022-02245-6 -
Multiomic analysis identifies CPT1A as a potential therapeutic target in platinum-refractory, high-grade serous ovarian cancer.
Huang D, Chowdhury S, Wang H, Savage SR, et al · · 2021 · cited 48× · PMID 35028612 · DOI 10.1016/j.xcrm.2021.100471
Verify or expand the search:
- PubMed search for NCT03904862
- Europe PMC full search
- ASCO Meeting Library
- ESMO Meeting Library
- bioRxiv preprints
- medRxiv preprints
- Google Scholar
Related trials
Other recruiting trials for Medulloblastoma, Childhood
Currently open trials in the same condition.
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- NCT06193759 — Immunotherapy for Malignant Pediatric Brain Tumors Employing Adoptive Cellular Therapy (IMPACT) · Phase 1 · recruiting
- NCT05230758 — Effect of Metformin on Behaviour and the Brain in Children Treated for a Brain Tumour · Phase 3 · recruiting
- NCT05057702 — Individualized Treatment Plan in Children and Young Adults With Relapsed Medulloblastoma and Ependymoma · NA · recruiting
Other Pediatric Brain Tumor Consortium trials
Trials by the same sponsor.
- NCT04482933 — HSV G207 With a Single Radiation Dose in Children With Recurrent High-Grade Glioma · Phase 2 · withdrawn
- NCT05934630 — Testing Cerebrospinal Fluid for Cell-free Tumor DNA in Children, Adolescents, and Young Adults With Brain Tumors · suspended
- NCT04743661 — 131I-Omburtamab, in Recurrent Medulloblastoma and Ependymoma · Phase 2 · active not recruiting
- NCT04295759 — INCB7839 in Treating Children With Recurrent/Progressive High-Grade Gliomas · Phase 1 · completed
- NCT04201457 — A Trial of Dabrafenib, Trametinib and Hydroxychloroquine for Patients With Recurrent LGG or HGG With a BRAF Aberration · Phase 1, PHASE2 · active not recruiting
Verify against primary sources
- ClinicalTrials.gov — authoritative US registry record
- WHO ICTRP — international registry index
- EU Clinical Trials Register
- Sponsor press releases (Google)
- Trial protocol + status: ClinicalTrials.gov NCT03904862 (US National Library of Medicine, public domain)
- Publications: Europe PMC API search by NCT ID, retrieved 10 June 2026
- Drug + disease cross-links: matched in real time against Drug Landscape's normalised drug + company + condition tables
- Sponsor: as reported to ClinicalTrials.gov by Pediatric Brain Tumor Consortium
- Last refreshed: 30 October 2025
Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03904862.
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