Last reviewed · How we verify

NCT03898180

Study of First-line Pembrolizumab (MK-3475) With Lenvatinib (MK-7902/E7080) in Urothelial Carcinoma Cisplatin-ineligible Participants Whose Tumors Express Programmed Cell Death-Ligand 1 and in Participants Ineligible for Platinum-containing Chemotherapy (MK-7902-011/E7080-G000-317/ LEAP-011)

Completed Phase 3 Results posted Last updated 5 February 2026
What this trial tests

Phase 3 trial testing Pembrolizumab in Urothelial Carcinoma in 505 participants. Completed in 20 May 2024.

Timeline
6 May 2019
Primary endpoint
26 July 2021
20 May 2024

Quick facts

Lead sponsorMerck Sharp & Dohme LLC
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingtriple
Primary purposetreatment
Enrollment505
Start date6 May 2019
Primary completion26 July 2021
Estimated completion20 May 2024
Sites194 locations across Italy, Japan, Taiwan, Poland, South Korea, Denmark, Netherlands, Russia

Drugs / interventions tested

Conditions studied

Sponsor

Merck Sharp & Dohme LLC — full company profile →

Who can join

18 and older, any sex, with Urothelial Carcinoma. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Progression-free Survival (PFS) Primary · Up to approximately 25 months

PFS was defined as the time from randomization to the first documented PD per Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST 1.1) by blinded independent central review (BICR), or death due to any cause, whichever occurs first. Per RECIST 1.1, PD was defined as ≥20% increase in the sum of diameters of target lesions. In addition to the relative increase of 20%, the sum must also have demonstrated an absolute increase of ≥5 mm. The appearance of one or more new lesions was also considered PD. PFS as assessed by BICR per RECIST 1.1 is presented. Protocol-specified final analysis

GroupValue95% CI
Pembrolizumab + Lenvatinib4.54.0 – 6.0
Pembrolizumab + Placebo4.02.7 – 5.4
Overall Survival (OS) Primary · Up to approximately 25 months

OS was defined as the time from randomization to death due to any cause. Participants without documented death at the time of the final analysis were to be censored at the date of the last follow-up. Protocol-specified final analysis for this primary outcome measure was performed with an analysis data cut-off date of Jul-26-2021.

GroupValue95% CI
Pembrolizumab + Lenvatinib11.89.1 – 15.1
Pembrolizumab + Placebo12.99.8 – 17.8
Objective Response Rate (ORR) Secondary · Up to approximately 25 months

ORR was defined as the percentage of participants who had a confirmed CR (CR: disappearance of all target lesions) or partial response (PR: at least a 30% decrease in the sum of diameters of target lesions) per RECIST 1.1 as assessed by BICR. The percentage of participants who experienced a CR or PR is presented. Protocol-specified final analysis for this secondary outcome measure was performed with an analysis data cut-off date of Jul-26-2021.

GroupValue95% CI
Pembrolizumab + Lenvatinib33.127.2 – 39.3
Pembrolizumab + Placebo28.923.3 – 35.1
Duration of Response (DOR) Secondary · Up to approximately 25 months

For participants who demonstrated a confirmed CR (CR: disappearance of all target lesions) or partial response (PR: at least a 30% decrease in the sum of diameters of target lesions) per RECIST 1.1 as assessed by BICR, DOR was defined as the time from first documented evidence of a CR or PR until PD or death. DOR for participants who had not progressed or died at the time of analysis was to be censored at the date of their last tumor assessment. Per RECIST 1.1, PD was defined as ≥20% increase in the sum of diameters of target lesions as well as an absolute increase of ≥5 mm in the sum of diame

GroupValue95% CI
Pembrolizumab + LenvatinibNANA – NA
Pembrolizumab + PlaceboNANA – NA
Disease Control Rate (DCR) Secondary · Up to approximately 25 months

DCR was defined as the percentage of participants who have a CR (CR: disappearance of all target lesions) or partial response (PR: at least a 30% decrease in the sum of diameters of target lesions) or stable disease (SD: neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for PD \[PD: ≥20% increase in the sum of diameters of target lesions and an absolute increase of ≥5 mm. The appearance of one or more new lesions was also considered PD\]). DCR for participants who had not progressed or died at the time of analysis was to be censored at the date of their last tum

GroupValue95% CI
Pembrolizumab + Lenvatinib66.960.7 – 72.8
Pembrolizumab + Placebo56.249.7 – 62.5
Change From Baseline in European Organisation for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire-Core 30 (QLQ-C30) Global Health Status (GHS) (Item 29) and Quality of Life (QOL) (Item 30) Combined Score Secondary · Baseline and Week 11

The EORTC QLQ-C30 is a questionnaire to assess the overall quality of life of cancer patients. Participant responses to the questions regarding GHS ("How would you rate your overall health during the past week?") and QOL ("How would you rate your overall quality of life during the past week?") were scored on a 7-point scale (1= Very poor to 7=Excellent). Using linear transformation, raw scores were standardized, so that scores range from 0 to 100. The change from baseline in GHS (EORTC QLQ-C30 Item 29) and QOL (EORTC QLQ-C30 Item 30) combined score is presented. A higher score indicates a bett

GroupValue95% CI
Pembrolizumab + Lenvatinib0.73-2.63 – 4.09
Pembrolizumab + Placebo3.790.47 – 7.12
Time to True Deterioration (TTD) Based on Change From Baseline in EORTC QLQ-C30 GHS (Item 29) and QOL (Item 30) Combined Score Secondary · Baseline and up to approximately 25 months

TTD was defined as the time from baseline to the first onset of a ≥10-point negative change (decrease) from baseline in GHS (EORTC QLQ-C30 Item 29) \& QOL (EORTC QLQ-C30 Item 30) combined score. The EORTC QLQ-C30 is a questionnaire to assess the overall quality of life of cancer patients. Participant responses to the questions regarding GHS ("How would you rate your overall health during the past week?") and QOL ("How would you rate your overall quality of life during the past week?") were scored on a 7-point scale (1= Very poor to 7=Excellent). Using linear transformation, raw scores were sta

GroupValue95% CI
Pembrolizumab + Lenvatinib3.42.1 – 4.3
Pembrolizumab + Placebo7.64.2 – NA
Number of Participants Who Experience an AE Secondary · Up to approximately 25 months

An AE was defined as any untoward medical occurrence in a clinical study participant, temporally associated with the use of study intervention, whether or not considered related to the study intervention. An AE could therefore be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of a study intervention. The number of participants who experienced an AE is presented. Final analysis for this secondary outcome measure was performed with an analysis data cut-off date of Jul-26-2021.

GroupValue95% CI
Pembrolizumab + Lenvatinib234
Pembrolizumab + Placebo235
Number of Participants Who Discontinue Study Treatment Due to an AE Secondary · Up to approximately 25 months

An AE was defined as any untoward medical occurrence in a clinical study participant, temporally associated with the use of study intervention, whether or not considered related to the study intervention. An AE could therefore be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of a study intervention. The number of participants who discontinued study treatment due to an AE is presented. Final analysis for this secondary outcome measure was performed with an analysis data cut-off date of

GroupValue95% CI
Pembrolizumab + Lenvatinib83
Pembrolizumab + Placebo44

Adverse events — posted to ClinicalTrials.gov

Time frame: Up to approximately 52 months. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Lenvatinib + Pembrolizumab First Course
Serious: 155/247 (63%)
Deaths: 178/251
Placebo + Pembrolizumab First Course
Serious: 116/254 (46%)
Deaths: 175/254
Lenvatinib + Pembrolizumab → Pembrolizumab Second Course
Serious: 0/2 (0%)
Deaths: 0/2
Placebo + Pembrolizumab → Pembrolizumab Second Course
Serious: 0/5 (0%)
Deaths: 0/5

Serious adverse events (207 terms)

ReactionSystemLenvatinib + Pembrolizumab…Placebo + Pembrolizumab Fi…Lenvatinib + Pembrolizumab…Placebo + Pembrolizumab → …
PneumoniaInfections and infestations
Urinary tract infectionInfections and infestations
Acute kidney injuryRenal and urinary disorders
DeathGeneral disorders
AnaemiaBlood and lymphatic system disorders
HaematuriaRenal and urinary disorders
Cardiac failureCardiac disorders
COVID-19 pneumoniaInfections and infestations
PneumonitisRespiratory, thoracic and mediastinal disorders
Cardiac arrestCardiac disorders
DiarrhoeaGastrointestinal disorders
IleusGastrointestinal disorders
FatigueGeneral disorders
General physical health deteriorationGeneral disorders
PyrexiaGeneral disorders
COVID-19Infections and infestations
Pneumonia aspirationInfections and infestations
SepsisInfections and infestations
UrosepsisInfections and infestations
Platelet count decreasedInvestigations
Chronic obstructive pulmonary diseaseRespiratory, thoracic and mediastinal disorders
HypertensionVascular disorders
ColitisGastrointestinal disorders
PancreatitisGastrointestinal disorders
AstheniaGeneral disorders
Other adverse events (57 terms — click to expand)

ReactionSystemLenvatinib + Pembrolizumab…Placebo + Pembrolizumab Fi…Lenvatinib + Pembrolizumab…Placebo + Pembrolizumab → …
ProteinuriaRenal and urinary disorders
HypertensionVascular disorders
HypothyroidismEndocrine disorders
Decreased appetiteMetabolism and nutrition disorders
DiarrhoeaGastrointestinal disorders
AnaemiaBlood and lymphatic system disorders
Urinary tract infectionInfections and infestations
FatigueGeneral disorders
NauseaGastrointestinal disorders
AstheniaGeneral disorders
Weight decreasedInvestigations
PruritusSkin and subcutaneous tissue disorders
ConstipationGastrointestinal disorders
DysphoniaRespiratory, thoracic and mediastinal disorders
Lipase increasedInvestigations
RashSkin and subcutaneous tissue disorders
VomitingGastrointestinal disorders
PyrexiaGeneral disorders
HaematuriaRenal and urinary disorders
Oedema peripheralGeneral disorders
Blood creatinine increasedInvestigations
Amylase increasedInvestigations
ArthralgiaMusculoskeletal and connective tissue disorders
Abdominal painGastrointestinal disorders
Back painMusculoskeletal and connective tissue disorders
Palmar-plantar erythrodysaesthesia syndromeSkin and subcutaneous tissue disorders
Alanine aminotransferase increasedInvestigations
Aspartate aminotransferase increasedInvestigations
HeadacheNervous system disorders
Mucosal inflammationGeneral disorders
CoughRespiratory, thoracic and mediastinal disorders
DyspnoeaRespiratory, thoracic and mediastinal disorders
Blood alkaline phosphatase increasedInvestigations
HypoalbuminaemiaMetabolism and nutrition disorders
StomatitisGastrointestinal disorders
HyponatraemiaMetabolism and nutrition disorders
InsomniaPsychiatric disorders
HyperthyroidismEndocrine disorders
Platelet count decreasedInvestigations
HyperkalaemiaMetabolism and nutrition disorders

Most-reported serious reactions: Pneumonia, Urinary tract infection, Acute kidney injury, Death, Anaemia, Haematuria, Cardiac failure, COVID-19 pneumonia.

Data from ClinicalTrials.gov NCT03898180 adverse events section.

Sponsor's own description

The purpose of this study is to evaluate the efficacy and safety of lenvatinib (MK-7902/E7080) in combination with pembrolizumab (MK-3475) in the treatment of cisplatin-ineligible participants with a Programmed Cell Death-Ligand 1 (PD-L1) Combined Positive Score (CPS) ≥10, or in participants ineligible for any platinum-containing chemotherapy regardless of CPS, with advanced/unresectable or metastatic urothelial carcinoma (UC). The primary hypotheses for this study are that: 1. Pembrolizumab + lenvatinib is superior to pembrolizumab + placebo with respect to Progression-free Survival (PFS) per Response Evaluation Criteria in Solid Tumors Version 1.1 (RECIST 1.1) by blinded independent central review (BICR), and 2. Pembrolizumab + lenvatinib is superior to pembrolizumab + placebo with respect to Overall Survival (OS). Based on recommendation of the external Data Monitoring Committee (eDMC), Amendment 3 (effective: September \[Sep\]-24-2021) was implemented to unblind the study and discontinue lenvatinib and placebo treatment. The eDMC was then disbanded. With Amendment 4 (effective: December-5-2022) second course pembrolizumab will no longer be offered. Any participant receiving second course pembrolizumab treatment prior to initiation of Amendment 4 will be able to complete treatment as planned. Study participation will end after the final administration of pembrolizumab. Participants who either complete 35 administrations of pembrolizumab or discontinue pembrolizumab will discontinue from the study following the safety follow-up visit. AEs and spontaneously reported pregnancies will be reported and followed per protocol. The overall study ends when the last participant completes the last study-related contact or visit, withdraws from the study, or is lost to follow-up.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Targeting cytokine and chemokine signaling pathways for cancer therapy.
    Yi M, Li T, Niu M, Zhang H, et al · · 2024 · cited 264× · PMID 39034318 · DOI 10.1038/s41392-024-01868-3
  2. Combining Immune Checkpoint Inhibitors with Anti-Angiogenic Agents.
    Ciciola P, Cascetta P, Bianco C, Formisano L, et al · · 2020 · cited 77× · PMID 32138216 · DOI 10.3390/jcm9030675
  3. Current Strategies and Novel Therapeutic Approaches for Metastatic Urothelial Carcinoma.
    Mollica V, Rizzo A, Montironi R, Cheng L, et al · · 2020 · cited 75× · PMID 32498352 · DOI 10.3390/cancers12061449
  4. The LEAP program: lenvatinib plus pembrolizumab for the treatment of advanced solid tumors.
    Taylor MH, Schmidt EV, Dutcus C, Pinheiro EM, et al · · 2021 · cited 50× · PMID 33300372 · DOI 10.2217/fon-2020-0937
  5. Immune Checkpoint Inhibitors in Urothelial Bladder Cancer: State of the Art and Future Perspectives.
    Roviello G, Catalano M, Santi R, Palmieri VE, et al · · 2021 · cited 44× · PMID 34503220 · DOI 10.3390/cancers13174411
  6. Metastatic Urothelial Cancer: a rapidly changing treatment landscape.
    Stecca C, Abdeljalil O, Sridhar SS. · · 2021 · cited 40× · PMID 34616491 · DOI 10.1177/17588359211047352
  7. The Resistance Mechanisms of Checkpoint Inhibitors in Solid Tumors.
    Koustas E, Sarantis P, Papavassiliou AG, Karamouzis MV. · · 2020 · cited 40× · PMID 32344837 · DOI 10.3390/biom10050666
  8. Tumor Vessel Normalization: A Window to Enhancing Cancer Immunotherapy.
    Li S, Zhang Q, Hong Y. · · 2020 · cited 28× · PMID 33287656 · DOI 10.1177/1533033820980116

Verify or expand the search:

Other trials of Pembrolizumab

Trials testing the same drug.

Other recruiting trials for Urothelial Carcinoma

Currently open trials in the same condition.

Other Merck Sharp & Dohme LLC trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03898180.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing