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NCT03895528

Lonafarnib for Patients With Hutchinson-Gilford Progeria Syndrome or Progeroid Laminopathy

APPROVED FOR MARKETING Last updated 15 April 2021
What this trial tests

trial testing Lonafarnib in Progeria. Approved for marketing.

Quick facts

Lead sponsorEiger BioPharmaceuticals
StatusAPPROVED FOR MARKETING
Study typeEXPANDED_ACCESS

Drugs / interventions tested

Conditions studied

Sponsor

Eiger BioPharmaceuticals — full company profile →

Who can join

12 Months and older, any sex, with Progeria or HGPS. Patients with the condition only — healthy volunteers not accepted.

Sponsor's own description

This treatment IND protocol will allow patients with HGPS and progeroid laminopathies access to lonafarnib, the only compound shown to have an effect on the HGPS disease process resulting in improved outcomes (Gordon et al, 2018). There are no approved treatments for HGPS and progeroid laminopathies.

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Lonafarnib: First Approval.
    Dhillon S. · · 2021 · cited 88× · PMID 33590450 · DOI 10.1007/s40265-020-01464-z

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Other trials of Lonafarnib

Trials testing the same drug.

Other Eiger BioPharmaceuticals trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03895528.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing