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NCT03861481: MyCIDPchoice

A Study to Assess the Efficacy, Safety and Tolerability of Rozanolixizumab in Subjects With Chronic Inflammatory Demyelinating Polyradiculoneuropathy

Completed Phase 2 Results posted Last updated 1 August 2023
What this trial tests

Phase 2 trial testing Rozanolixizumab in Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP) in 34 participants. Completed in 31 March 2021.

Timeline
26 March 2019
Primary endpoint
31 March 2021
31 March 2021

Quick facts

Lead sponsorUCB Biopharma S.P.R.L.
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposetreatment
Enrollment34
Start date26 March 2019
Primary completion31 March 2021
Estimated completion31 March 2021
Sites22 locations across Denmark, France, Netherlands, Belgium, United Kingdom, Germany, United States, Spain

Drugs / interventions tested

Conditions studied

Sponsor

UCB Biopharma S.P.R.L. — full company profile →

Who can join

18 and older, any sex, with Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP). Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Change From Baseline to Week 13 (Day 85) in Inflammatory Rasch-built Overall Disability Scale (iRODS) Score Primary · From Baseline up to Week 13 (Day 85)

iRODS is a linearly weighted patient-reported outcome measure (questionnaire) that captures activity and social participation limitations in participants with chronic inflammatory demyelinating polyradiculoneuropathy. Questionnaire consisted of 24 items (including eating, taking a shower, walking a flight of stairs, standing for hours, etc.) and assesses a participant's ability to perform daily and social activities. Participants had 3 response options: 0=impossible to perform; 1=performed with difficulty; 2=easily performed, performed without difficulty. Raw sum scores of iRODS (range 0 to 48

GroupValue95% CI
Placebo0.234± 0.379
Rozanolixizumab0.181± 0.468

Adverse events — posted to ClinicalTrials.gov

Time frame: From Baseline until the Safety Follow-up Visit (up to Week 24). Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Placebo
Serious: 0/17 (0%)
Deaths: 0/17
Rozanolixizumab
Serious: 2/17 (12%)
Deaths: 0/17

Serious adverse events (1 terms)

ReactionSystemPlaceboRozanolixizumab
Chronic inflammatory demyelinating polyradiculoneuropathyNervous system disorders
Other adverse events (14 terms — click to expand)

ReactionSystemPlaceboRozanolixizumab
HeadacheNervous system disorders
Chronic inflammatory demyelinating polyradiculoneuropathyNervous system disorders
DiarrhoeaGastrointestinal disorders
Infusion site erythemaGeneral disorders
Peripheral swellingGeneral disorders
FatigueGeneral disorders
Urinary tract infectionInfections and infestations
ArthralgiaMusculoskeletal and connective tissue disorders
NauseaGastrointestinal disorders
PainGeneral disorders
FallInjury, poisoning and procedural complications
Bacterial test positiveInvestigations
HypoaesthesiaNervous system disorders
RashSkin and subcutaneous tissue disorders

Most-reported serious reactions: Chronic inflammatory demyelinating polyradiculoneuropathy.

Data from ClinicalTrials.gov NCT03861481 adverse events section.

Sponsor's own description

The purpose of the study is to evaluate clinical efficacy of rozanolixizumab as a treatment for subjects with chronic inflammatory demyelinating polyradiculoneuropathy (CIDP).

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. The therapeutic age of the neonatal Fc receptor.
    Pyzik M, Kozicky LK, Gandhi AK, Blumberg RS. · · 2023 · cited 166× · PMID 36726033 · DOI 10.1038/s41577-022-00821-1
  2. FcRn inhibitors: a novel option for the treatment of myasthenia gravis.
    Zhu LN, Hou HM, Wang S, Zhang S, et al · · 2023 · cited 53× · PMID 36751773 · DOI 10.4103/1673-5374.363824
  3. Therapeutic Monoclonal Antibody Therapies in Chronic Autoimmune Demyelinating Neuropathies.
    Briani C, Visentin A. · · 2022 · cited 39× · PMID 35349079 · DOI 10.1007/s13311-022-01222-x
  4. Neonatal Fc Receptor-Targeted Therapies in Neurology.
    Nelke C, Spatola M, Schroeter CB, Wiendl H, et al · · 2022 · cited 32× · PMID 34997443 · DOI 10.1007/s13311-021-01175-7
  5. Rozanolixizumab: First Approval.
    Hoy SM. · · 2023 · cited 24× · PMID 37656420 · DOI 10.1007/s40265-023-01933-1
  6. Next-generation antibody-based therapies in neurology.
    Ruck T, Nimmerjahn F, Wiendl H, Lünemann JD. · · 2022 · cited 20× · PMID 34928330 · DOI 10.1093/brain/awab465
  7. Efficacy, safety and tolerability of rozanolixizumab in patients with chronic inflammatory demyelinating polyradiculoneuropathy: a randomised, subject-blind, investigator-blind, placebo-controlled, phase 2a trial and open-label extension study.
    Querol L, De Sèze J, Dysgaard T, Levine T, et al · · 2024 · cited 18× · PMID 38729747 · DOI 10.1136/jnnp-2023-333112
  8. Non-human primates in the PKPD evaluation of biologics: Needs and options to reduce, refine, and replace. A BioSafe White Paper.
    Ménochet K, Yu H, Wang B, Tibbitts J, et al · · 2022 · cited 15× · PMID 36418217 · DOI 10.1080/19420862.2022.2145997

Verify or expand the search:

Other trials of Rozanolixizumab

Trials testing the same drug.

Other recruiting trials for Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP)

Currently open trials in the same condition.

Other UCB Biopharma S.P.R.L. trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03861481.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing