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NCT03827798

Study of Efficacy and Safety of Investigational Treatments in Patients With Moderate to Severe Hidradenitis Suppurativa

Active, enrolled Phase 2 Results posted Last updated 6 February 2026
What this trial tests

Phase 2 trial testing CFZ533 in Hidradenitis Suppurativa in 248 participants. Participants enrolled and being followed up; not accepting new ones.

Timeline
27 February 2019
Primary endpoint
4 December 2024
11 December 2026

Quick facts

Lead sponsorNovartis Pharmaceuticals
PhasePhase 2
StatusActive, enrolled
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposetreatment
Enrollment248
Start date27 February 2019
Primary completion4 December 2024
Estimated completion11 December 2026
Sites36 locations across Denmark, France, Netherlands, Belgium, Austria, Germany, Hungary, Spain

Drugs / interventions tested

Conditions studied

Sponsor

Novartis Pharmaceuticals — full company profile →

Who can join

Adults 18 to 65, any sex, with Hidradenitis Suppurativa. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Percentage of Participants Achieving Clinical Response Measured by Simplified Hidradenitis Suppurativa (sHiSCR) Primary · Baseline, Week 16

sHiSCR was defined as at least a 50 percent (%) reduction in abscess and inflammatory nodule (AN) counts, and no increase in draining fistula count related to baseline. The primary variable was modeled with the binomial distribution. A neutral non-informative Beta (1/3, 1/3) distribution was used as the prior for the response rate for all treatment groups. Based on the priors and the observed primary outcome, posterior distributions for the response rate for the investigational treatment and pooled placebo groups were computed respectively. At the time of the statistical comparison for cohorts

GroupValue95% CI
Cohort A - CFZ533 600 mg17
Cohort B - LYS006 20 mg8
Cohort C - MAS825 300 mg15
Pooled Placebo (Cohorts A, B and C)14
Cohort D - LOU064 25 mg24
Cohort D - LOU064 100 mg16
Pooled Placebo (Cohorts A, B, C and D)17
Cohort E - VAY736 300 mg16
Pooled Placebo (Cohorts A, B, C, D and E)23

Adverse events — posted to ClinicalTrials.gov

Time frame: Cohorts A, B and C: 28 weeks including 12 weeks follow up period. Cohort D: 20 weeks including 4 weeks follow up period. Cohort E (ongoing): up to 116 weeks including 100 weeks follow up period.. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Cohort A - CFZ533 600 mg
Serious: 4/29 (14%)
Deaths: 0/29
Cohort B - LYS006 20 mg
Serious: 2/27 (7%)
Deaths: 0/27
Cohort C - MAS825 300 mg
Serious: 1/33 (3%)
Deaths: 0/33
Cohort D - LOU064 25 mg
Serious: 1/33 (3%)
Deaths: 0/33
Cohort D - LOU064 100 mg
Serious: 1/33 (3%)
Deaths: 0/33
Cohort E - VAY736 300 mg
Serious: 1/32 (3%)
Deaths: 0/32
Pooled Placebo (Cohorts A, B, C, D and E)
Serious: 1/61 (2%)
Deaths: 0/61
Total
Serious: 11/248 (4%)
Deaths: 0/248

Serious adverse events (11 terms)

ReactionSystemCohort A - CFZ533 600 mgCohort B - LYS006 20 mgCohort C - MAS825 300 mgCohort D - LOU064 25 mgCohort D - LOU064 100 mgCohort E - VAY736 300 mgPooled Placebo (Cohorts A,…Total
ColitisGastrointestinal disorders
Pancreatitis acuteGastrointestinal disorders
Abscess limbInfections and infestations
Genital abscessInfections and infestations
Testicular abscessInfections and infestations
Blood creatine phosphokinase increasedInvestigations
Alcohol withdrawal syndromePsychiatric disorders
DepressionPsychiatric disorders
Ovarian cystReproductive system and breast disorders
Testicular torsionReproductive system and breast disorders
Hypertensive crisisVascular disorders
Other adverse events (41 terms — click to expand)

ReactionSystemCohort A - CFZ533 600 mgCohort B - LYS006 20 mgCohort C - MAS825 300 mgCohort D - LOU064 25 mgCohort D - LOU064 100 mgCohort E - VAY736 300 mgPooled Placebo (Cohorts A,…Total
NasopharyngitisInfections and infestations
HeadacheNervous system disorders
HidradenitisSkin and subcutaneous tissue disorders
COVID-19Infections and infestations
FatigueGeneral disorders
DiarrhoeaGastrointestinal disorders
PyrexiaGeneral disorders
AstheniaGeneral disorders
Urine albumin/creatinine ratio increasedInvestigations
HypertensionVascular disorders
PruritusSkin and subcutaneous tissue disorders
SinusitisInfections and infestations
C-reactive protein increasedInvestigations
Crystal urine presentInvestigations
ArthralgiaMusculoskeletal and connective tissue disorders
DizzinessNervous system disorders
Oropharyngeal painRespiratory, thoracic and mediastinal disorders
Abdominal painGastrointestinal disorders
NauseaGastrointestinal disorders
Upper respiratory tract infectionInfections and infestations
Injection related reactionInjury, poisoning and procedural complications
Blood urine presentInvestigations
Pain in extremityMusculoskeletal and connective tissue disorders
ProteinuriaRenal and urinary disorders
BronchitisInfections and infestations
InfluenzaInfections and infestations
Back painMusculoskeletal and connective tissue disorders
ConstipationGastrointestinal disorders
BacteriuriaInfections and infestations
Ear infectionInfections and infestations
Bacterial test positiveInvestigations
MyalgiaMusculoskeletal and connective tissue disorders
DepressionPsychiatric disorders
ErythemaSkin and subcutaneous tissue disorders
Pain of skinSkin and subcutaneous tissue disorders
Blood creatine phosphokinase increasedInvestigations
Increased tendency to bruiseBlood and lymphatic system disorders
FlatulenceGastrointestinal disorders
TonsillitisInfections and infestations
Blood glucose increasedInvestigations

Most-reported serious reactions: Colitis, Pancreatitis acute, Abscess limb, Genital abscess, Testicular abscess, Blood creatine phosphokinase increased, Alcohol withdrawal syndrome, Depression.

Data from ClinicalTrials.gov NCT03827798 adverse events section.

Sponsor's own description

The main purpose of this study is to assess preliminary efficacy and safety of CFZ533/iscalimab (Cohort A), LYS006 (Cohort B), MAS825 (Cohort C), LOU064/remibrutinib (Cohort D) and VAY736/ianalumab (Cohort E) in patients with moderate to severe hidradenitis suppurativa and to determine if CFZ533, LYS006, MAS825, LOU064 and VAY736 have an adequate clinical profile for further clinical development.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. BTK inhibitors in the treatment of hematological malignancies and inflammatory diseases: mechanisms and clinical studies.
    Alu A, Lei H, Han X, Wei Y, et al · · 2022 · cited 88× · PMID 36183125 · DOI 10.1186/s13045-022-01353-w
  2. Hidradenitis Suppurativa: Where We Are and Where We Are Going.
    Scala E, Cacciapuoti S, Garzorz-Stark N, Megna M, et al · · 2021 · cited 85× · PMID 34440863 · DOI 10.3390/cells10082094
  3. New perspectives on the treatment of hidradenitis suppurativa.
    Amat-Samaranch V, Agut-Busquet E, Vilarrasa E, Puig L. · · 2021 · cited 47× · PMID 34840709 · DOI 10.1177/20406223211055920
  4. New and Emerging Targeted Therapies for Hidradenitis Suppurativa.
    Markota Čagalj A, Marinović B, Bukvić Mokos Z. · · 2022 · cited 46× · PMID 35409118 · DOI 10.3390/ijms23073753
  5. Clinical Implementation of Biologics and Small Molecules in the Treatment of Hidradenitis Suppurativa.
    Aarts P, Dudink K, Vossen ARJV, van Straalen KR, et al · · 2021 · cited 38× · PMID 34283386 · DOI 10.1007/s40265-021-01566-2
  6. Skin immunity and its dysregulation in atopic dermatitis, hidradenitis suppurativa and vitiligo.
    Campione E, Lanna C, Diluvio L, Cannizzaro MV, et al · · 2020 · cited 32× · PMID 31905036 · DOI 10.1080/15384101.2019.1707455
  7. Insights into the Pathogenesis of HS and Therapeutical Approaches.
    Rosi E, Fastame MT, Scandagli I, Di Cesare A, et al · · 2021 · cited 27× · PMID 34572354 · DOI 10.3390/biomedicines9091168
  8. Therapeutic Potential of IL-1 Antagonism in Hidradenitis Suppurativa.
    Calabrese L, Malvaso D, Coscarella G, Antonelli F, et al · · 2024 · cited 13× · PMID 38397412 · DOI 10.3390/biom14020175

Verify or expand the search:

Other trials of CFZ533

Trials testing the same drug.

Other recruiting trials for Hidradenitis Suppurativa

Currently open trials in the same condition.

Other Novartis Pharmaceuticals trials

Trials by the same sponsor.

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Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing