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NCT03806556

A Pediatric Trial Using Tranexamic Acid in Thrombocytopenia

Terminated Phase 1, PHASE2 Results posted Last updated 20 September 2021
What this trial tests

Phase 1, PHASE2 trial testing Tranexamic Acid in Pediatric Cancer in 11 participants. Terminated before completion.

Timeline
22 April 2019
Primary endpoint
25 August 2020
25 August 2020

Quick facts

Lead sponsorMeghan McCormick
PhasePhase 1, PHASE2
StatusTerminated
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingquadruple
Primary purposeprevention
Enrollment11
Start date22 April 2019
Primary completion25 August 2020
Estimated completion25 August 2020
Sites1 location across United States

Drugs / interventions tested

Conditions studied

Sponsor

Meghan McCormick

Who can join

Adults 2 to 21, any sex, with Pediatric Cancer or Thrombocytopenia. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Safety and Tolerability of Tranexamic Acid in Participants as the Number of Patients With Any Adverse Events and Serious Adverse Events (SAE) as Assessed by CTCAE v4.03 Primary · From activation of the study drug (maximum 30 days) through 30 days from discontinuation of study drug

Adverse Events and Serious Adverse Events (SAE) will be collected on subjects throughout their participation in the study and up to 30 days following discontinuation of the study drug, regardless of attribution. Adverse events and serious adverse events will be tabulated by type and grade according to the NCI CTCAE v 4.03. The hypothesis is that tranexamic acid can be safely added to standard care regimens in patients with hematologic malignancies or solid tumors during periods of severe thrombocytopenia. Analysis limited to a descriptive assessment of the safety of tranexamic acid in patient

Grade 3 Adverse Events : Anemia
GroupValue95% CI
Tranexamic Acid4
Placebo4
Grade 3 Adverse Events : Anorexia
GroupValue95% CI
Tranexamic Acid0
Placebo2
Grade 3 Adverse Events : Bone Pain
GroupValue95% CI
Tranexamic Acid1
Placebo0
Grade 3 Adverse Events : Catheter Related Infection
GroupValue95% CI
Tranexamic Acid3
Placebo1
Grade 3 Adverse Events : Vomiting
GroupValue95% CI
Tranexamic Acid0
Placebo2
Grade 3 Adverse Events : Febrile Neutropenia
GroupValue95% CI
Tranexamic Acid2
Placebo3
Grade 3 Adverse Events : Fever
GroupValue95% CI
Tranexamic Acid0
Placebo1
Grade 3 Adverse Events : Hypoalbuminemia
GroupValue95% CI
Tranexamic Acid1
Placebo0
Feasibility of Tranexamic Acid as an Adjunct to Standard Therapy: Number of Participants Eligible and Recruited Primary · From time of recruitment of the first patient until the last patient is enrolled, up to 16 months in duration

Number of participants eligible for study enrollment and recruited. The hypothesis is that tranexamic acid can be safely added to standard care regimens in patients with hematologic malignancies or solid tumors during periods of severe thrombocytopenia. A descriptive assessment of feasibility of recruitment by monitoring number of patients screened, number of patients eligible for enrollment and rate of recruitment (both start-up and ongoing) during study period to be completed by collecting data on the number of patients screened, the number of patients eligible for study inclusion, the numb

Assessed for Eligibility
GroupValue95% CI
Overall Study693
Screened for Complete Inclusion/Exclusion Criteria
GroupValue95% CI
Overall Study148
Eligible for Enrollment
GroupValue95% CI
Overall Study31
Consented to Participate
GroupValue95% CI
Overall Study11
World Health Organization (WHO) Bleeding Scale Grade 2 or Higher Bleeding Secondary · 30 days after activation of study drug

Proportion of patients with bleeding of WHO grade 2 or above, after activation of study drug. Bleeding graded on a scale ranging from 1 (minor bleeding) through 4 (bleeding that is fatal or life-threatening).

GroupValue95% CI
Tranexamic Acid0
Placebo3
Number of Platelet and Red Blood Cell Transfusions Secondary · 30 days after activation of study drug

Number of platelet and red blood cell transfusions per patient during the first 30 days post prescription activation of study drug

Number of platelet transfusions per patient
GroupValue95% CI
Tranexamic Acid1.50 – 2
Placebo41 – 9
Number of pRBC transfusions per patient
GroupValue95% CI
Tranexamic Acid0.50 – 3
Placebo10 – 2
Number of Days Alive and Without WHO Grade 2 Bleeding or Greater Secondary · 30 days after activation of study drug

Number of days alive and without WHO grade 2 bleeding or greater during the first 30 days post activation of study drug. Bleeding graded on a scale ranging from 1 (minor bleeding) through 4 (bleeding that is fatal or life-threatening).

GroupValue95% CI
Tranexamic Acid5.52 – 8
Placebo10.41 – 18
The Occurrence of Thromboembolic Adverse Events and Serious Adverse Events Secondary · From activation of the study drug (maximum 30 days) through 30 days from discontinuation of study drug

Any venous or arterial thrombosis on standard diagnostic imaging post-randomization

GroupValue95% CI
Tranexamic Acid0
Placebo0
Bleeding of Any Grade Secondary · From activation of the study drug (maximum 30 days) through 30 days from discontinuation of study drug

Proportion of patients with bleeding of any grade as assessed by WHO bleeding score, after activation of study drug

GroupValue95% CI
Tranexamic Acid4
Placebo5
Highest Observed Grade of Bleeding (as Measured on WHO Bleeding Scale) During the Study Period Secondary · From activation of the study drug (maximum 30 days) through 30 days from discontinuation of study drug

Highest grade of bleeding (as measured on WHO bleeding scale) during study period in each enrolled patient. Bleeding graded on a scale ranging from 1 (minor bleeding) through 4 (bleeding that is fatal or life-threatening).

Grade 1 Bleeding
GroupValue95% CI
Tranexamic Acid4
Placebo2
Grade 2 Bleeding
GroupValue95% CI
Tranexamic Acid0
Placebo3
Grade 3 Bleeding
GroupValue95% CI
Tranexamic Acid0
Placebo0
Grade 4 Bleeding
GroupValue95% CI
Tranexamic Acid0
Placebo0
Grade 5 Bleeding
GroupValue95% CI
Tranexamic Acid0
Placebo0

Adverse events — posted to ClinicalTrials.gov

Time frame: From the time of activation of the study drug up to and including 30 days after the last dose of the study drug, an average of 41 days. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Tranexamic Acid
Serious: 6/6 (100%)
Deaths: 0/6
Placebo
Serious: 5/5 (100%)
Deaths: 0/5

Serious adverse events (4 terms)

ReactionSystemTranexamic AcidPlacebo
White Blood Cell DecreasedBlood and lymphatic system disorders
Platelet Count DecreasedBlood and lymphatic system disorders
Blood Bilirubin IncreasedHepatobiliary disorders
Febrile NeutropeniaBlood and lymphatic system disorders
Other adverse events (16 terms — click to expand)

ReactionSystemTranexamic AcidPlacebo
AnemiaBlood and lymphatic system disorders
Catheter Related InfectionInfections and infestations
Febrile NeutropeniaBlood and lymphatic system disorders
AnorexiaMetabolism and nutrition disorders
VomitingGastrointestinal disorders
Rash Maculo-papularSkin and subcutaneous tissue disorders
Bone PainMusculoskeletal and connective tissue disorders
FeverGeneral disorders
HypoalbuminemiaMetabolism and nutrition disorders
HypotensionVascular disorders
HypoxiaRespiratory, thoracic and mediastinal disorders
HypophosphatemiaMetabolism and nutrition disorders
NauseaGastrointestinal disorders
Mucositis OralGastrointestinal disorders
SinusitisInfections and infestations
Skin InfectionInfections and infestations

Most-reported serious reactions: White Blood Cell Decreased, Platelet Count Decreased, Blood Bilirubin Increased, Febrile Neutropenia.

Data from ClinicalTrials.gov NCT03806556 adverse events section.

Sponsor's own description

This study evaluates the use of tranexamic acid (TXA) in addition to standard therapy in children receiving chemotherapy or blood and/or marrow transplantation to decrease the risk of bleeding. Half of participants will receive tranexamic acid and half of participants will receive placebo.

Publications & conference data

No peer-reviewed publications indexed yet for this trial.

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Other trials of Tranexamic Acid

Trials testing the same drug.

Other recruiting trials for Pediatric Cancer

Currently open trials in the same condition.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03806556.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing