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NCT03783078

Pembrolizumab (MK-3475) as First-line Therapy for Advanced Merkel Cell Carcinoma (MK-3475-913)

Completed Phase 3 Results posted Last updated 28 May 2025
What this trial tests

Phase 3 trial testing Pembrolizumab (MK-3475) in Merkel Cell Carcinoma in 55 participants. Completed in 15 February 2024.

Timeline
25 February 2019
Primary endpoint
15 February 2022
15 February 2024

Quick facts

Lead sponsorMerck Sharp & Dohme LLC
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment55
Start date25 February 2019
Primary completion15 February 2022
Estimated completion15 February 2024
Sites22 locations across France, Italy, New Zealand, Sweden, Canada, Australia, United States, Spain

Drugs / interventions tested

Conditions studied

Sponsor

Merck Sharp & Dohme LLC — full company profile →

Who can join

12 and older, any sex, with Merkel Cell Carcinoma. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Objective Response Rate (ORR) Primary · Up to ~34 months

ORR was defined as the percentage of participants with Complete Response (CR: disappearance of all target lesions) or Partial Response (PR: at least a 30% decrease in the sum of diameters of target lesions) per Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST 1.1). The percentage of participants who experienced CR or PR as assessed by blinded independent central review (BICR) were presented.

GroupValue95% CI
Pembrolizumab 200 mg49.135.4 – 62.9
Duration of Response (DOR) Secondary · Up to ~58 months

For participants who demonstrated a confirmed Complete Response (CR: disappearance of all target lesions) or Partial Response (PR: At least a 30% decrease in the sum of diameters of target lesions) per RECIST 1.1, DOR was defined as the time from first documented evidence of a CR or PR until progressive disease (PD) or death. DOR for participants who had not progressed or died at the time of analysis was censored at the date of their last tumor assessment. Per RECIST 1.1, PD was defined as at least a 20% increase in the sum of diameters of target lesions as well as an absolute increase of at l

GroupValue95% CI
Pembrolizumab 200 mg39.823.8 – NA
Progression-free Survival (PFS) Secondary · Up to ~58 months

Progression-Free Survival was defined as the time from the first dose of study treatment to the first documented evidence of disease progression per RECIST 1.1 by BICR or death due to any cause, whichever occurred first. Per RECIST 1.1, PD was defined as ≥20% increase in the sum of diameters of target lesions. In addition to the relative increase of 20%, the sum must also have demonstrated an absolute increase of ≥5 mm. The appearance of one or more new lesions was also considered PD. PFS as assessed by BICR per RECIST 1.1 was presented.

GroupValue95% CI
Pembrolizumab 200 mg9.33.0 – 25.5
Overall Survival (OS) Secondary · Up to ~58 months

OS was defined as the time from the first dose of study treatment until death from any cause.

GroupValue95% CI
Pembrolizumab 200 mg24.312.4 – NA
Number of Participants With One or More Adverse Events (AEs) Secondary · Up to ~58 months

An AE was any untoward medical occurrence in a clinical study participant, temporally associated with the use of study intervention, whether or not considered related to the study intervention. An AE can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of a study intervention. The number of participants with at least one AE was assessed.

GroupValue95% CI
Pembrolizumab 200 mg52
Number of Participants Who Discontinued From Study Treatment Due to an AE Secondary · Up to ~27 months

An AE was any untoward medical occurrence in a clinical study participant, temporally associated with the use of study intervention, whether or not considered related to the study intervention. An AE can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of a study intervention. The number of participants who discontinued from study treatment due to an AE was assessed.

GroupValue95% CI
Pembrolizumab 200 mg18

Adverse events — posted to ClinicalTrials.gov

Time frame: Up to ~58 months. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Pembrolizumab 200 mg
Serious: 24/55 (44%)
Deaths: 32/55

Serious adverse events (30 terms)

ReactionSystemPembrolizumab 200 mg
Basal cell carcinomaNeoplasms benign, malignant and unspecified (incl cysts and polyps)
Pulmonary embolismRespiratory, thoracic and mediastinal disorders
ColitisGastrointestinal disorders
DysphagiaGastrointestinal disorders
Obstructive pancreatitisGastrointestinal disorders
Small intestinal obstructionGastrointestinal disorders
SubileusGastrointestinal disorders
FatigueGeneral disorders
CellulitisInfections and infestations
CystitisInfections and infestations
EmpyemaInfections and infestations
EncephalitisInfections and infestations
ErysipelasInfections and infestations
PneumoniaInfections and infestations
Respiratory syncytial virus infectionInfections and infestations
Upper respiratory tract infectionInfections and infestations
Wound infectionInfections and infestations
Muscular weaknessMusculoskeletal and connective tissue disorders
Squamous cell carcinomaNeoplasms benign, malignant and unspecified (incl cysts and polyps)
Squamous cell carcinoma of skinNeoplasms benign, malignant and unspecified (incl cysts and polyps)
Transitional cell carcinomaNeoplasms benign, malignant and unspecified (incl cysts and polyps)
Cerebral haemorrhageNervous system disorders
Cerebrovascular accidentNervous system disorders
Chronic inflammatory demyelinating polyradiculoneuropathyNervous system disorders
Guillain-Barre syndromeNervous system disorders
Other adverse events (44 terms — click to expand)

ReactionSystemPembrolizumab 200 mg
FatigueGeneral disorders
PruritusSkin and subcutaneous tissue disorders
Aspartate aminotransferase increasedInvestigations
AstheniaGeneral disorders
Alanine aminotransferase increasedInvestigations
Lipase increasedInvestigations
ArthralgiaMusculoskeletal and connective tissue disorders
AnaemiaBlood and lymphatic system disorders
ConstipationGastrointestinal disorders
Back painMusculoskeletal and connective tissue disorders
NauseaGastrointestinal disorders
DiarrhoeaGastrointestinal disorders
PyrexiaGeneral disorders
Weight decreasedInvestigations
Decreased appetiteMetabolism and nutrition disorders
HeadacheNervous system disorders
DyspnoeaRespiratory, thoracic and mediastinal disorders
Abdominal painGastrointestinal disorders
Dry mouthGastrointestinal disorders
VomitingGastrointestinal disorders
Oedema peripheralGeneral disorders
Amylase increasedInvestigations
Pain in extremityMusculoskeletal and connective tissue disorders
EczemaSkin and subcutaneous tissue disorders
RashSkin and subcutaneous tissue disorders
COVID-19Infections and infestations
Blood alkaline phosphatase increasedInvestigations
Blood creatinine increasedInvestigations
MyalgiaMusculoskeletal and connective tissue disorders
OsteoarthritisMusculoskeletal and connective tissue disorders
DysgeusiaNervous system disorders
HaematuriaRenal and urinary disorders
AlopeciaSkin and subcutaneous tissue disorders
VertigoEar and labyrinth disorders
HyperthyroidismEndocrine disorders
HypothyroidismEndocrine disorders
Urinary tract infectionInfections and infestations
FallInjury, poisoning and procedural complications
Blood creatine phosphokinase increasedInvestigations
HypokalaemiaMetabolism and nutrition disorders

Most-reported serious reactions: Basal cell carcinoma, Pulmonary embolism, Colitis, Dysphagia, Obstructive pancreatitis, Small intestinal obstruction, Subileus, Fatigue.

Data from ClinicalTrials.gov NCT03783078 adverse events section.

Sponsor's own description

This is a single-arm, open-label, multicenter, efficacy, and safety study of pembrolizumab in adult and pediatric participants with previously untreated advanced Merkel Cell Carcinoma (MCC). The primary objective of the trial is to assess the objective response rate, as assessed by blinded independent central review per Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST 1.1) modified to follow a maximum of 10 target lesions and a maximum of 5 target lesions per organ, following administration of pembrolizumab.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Society for Immunotherapy of Cancer (SITC) clinical practice guideline on immunotherapy for the treatment of nonmelanoma skin cancer.
    Silk AW, Barker CA, Bhatia S, Bollin KB, et al · · 2022 · cited 28× · PMID 35902131 · DOI 10.1136/jitc-2021-004434
  2. Immune Checkpoint Inhibition in Non-Melanoma Skin Cancer: A Review of Current Evidence.
    Stonesifer CJ, Djavid AR, Grimes JM, Khaleel AE, et al · · 2021 · cited 25× · PMID 34988009 · DOI 10.3389/fonc.2021.734354
  3. Merkel Cell Carcinoma: An Immunotherapy Fairy-Tale?
    Tanda ET, d'Amato AL, Rossi G, Croce E, et al · · 2021 · cited 20× · PMID 34631574 · DOI 10.3389/fonc.2021.739006
  4. FDA Accelerated Approval of Pembrolizumab for Recurrent Locally Advanced or Metastatic Merkel Cell Carcinoma.
    Bradford D, Demko S, Jin S, Mishra-Kalyani P, et al · · 2020 · cited 20× · PMID 32272501 · DOI 10.1634/theoncologist.2020-0184
  5. Recent Updates on Viral Oncogenesis: Available Preventive and Therapeutic Entities.
    Chowdhary S, Deka R, Panda K, Kumar R, et al · · 2023 · cited 13× · PMID 37486263 · DOI 10.1021/acs.molpharmaceut.2c01080
  6. T-Cell Responses in Merkel Cell Carcinoma: Implications for Improved Immune Checkpoint Blockade and Other Therapeutic Options.
    Gehrcken L, Sauerer T, Schaft N, Dörrie J. · · 2021 · cited 5× · PMID 34445385 · DOI 10.3390/ijms22168679
  7. Pembrolizumab for the First-Line Treatment of Recurrent Locally Advanced or Metastatic Merkel Cell Carcinoma: Results from the Single-Arm, Open-Label, Phase III KEYNOTE-913 Study.
    Mortier L, Villabona L, Lawrence B, Arance A, et al · · 2024 · cited 4× · PMID 39377880 · DOI 10.1007/s40257-024-00885-w
  8. Systemic Therapy for Non-Melanoma Skin Cancers: Latest Advances.
    Lessans S, O'Connell KA, Choe J. · · 2024 · cited 4× · PMID 38954315 · DOI 10.1007/s11912-024-01570-1

Verify or expand the search:

Other trials of Pembrolizumab (MK-3475)

Trials testing the same drug.

Other recruiting trials for Merkel Cell Carcinoma

Currently open trials in the same condition.

Other Merck Sharp & Dohme LLC trials

Trials by the same sponsor.

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