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NCT03495921: VITA

A Trial For Participants With Ewing's Sarcoma Treated With Vigil in Combination With Irinotecan and Temozolomide

Terminated Phase 3 Results posted Last updated 26 April 2023
What this trial tests

Phase 3 trial testing Vigil in Ewing Sarcoma in 32 participants. Terminated before completion.

Timeline
21 August 2018
Primary endpoint
20 January 2022
20 January 2022

Quick facts

Lead sponsorGradalis, Inc.
PhasePhase 3
StatusTerminated
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingnone
Primary purposetreatment
Enrollment32
Start date21 August 2018
Primary completion20 January 2022
Estimated completion20 January 2022
Sites15 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

Gradalis, Inc. — full company profile →

Who can join

2 and older, any sex, with Ewing Sarcoma or Ewing Family of Tumors. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Progression Free Survival (PFS) Primary · From date of randomization until the date of first documented progression (assessed up to 3 years).

Progression Free Survival (PFS) is defined as the time from randomization to the event of disease recurrence/progression according to Response Evaluation Criteria In Solid Tumors (RECIST) criteria (version 1.1) for target lesions and assessed CT/MRI by local investigator.

GroupValue95% CI
Group A: Vigil in Combination With Irinotecan and Temozolomide2.82.7 – NA
Group B: Irinotecan and Temozolomide9.12.8 – NA
Overall Survival (OS) Secondary · From date of randomization until date of death from any cause, whichever came first (assessed up to 3 years).

OS is defined as time from randomization to death or to the date of last follow-up. The date of last follow-up confirming survival will be used as the censoring date for subjects who are alive and/or do not have a known date of death.

GroupValue95% CI
Group A: Vigil in Combination With Irinotecan and Temozolomide16.114.6 – NA
Group B: Irinotecan and Temozolomide3.33.3 – NA
Overall Response Rate (ORR) Secondary · 6 months after treatment with Vigil.

ORR is defined as the proportion of participants who have prolonged stable disease or a partial or complete response or complete response to therapy according to RECIST 1.1.

GroupValue95% CI
Group A: Vigil in Combination With Irinotecan and Temozolomide0
Group B: Irinotecan and Temozolomide0
Vigil Manufacture Success Rate: Number of Participants Eligible for Treatment on the Main Study. Secondary · From manufacturing start date until 4 weeks post manufacturing for each tissue procurement (assessed up to 17 months).

Participants were considered eligible for treatment, if the tissue submitted to Gradalis met all criteria, including manufacturing product release criteria.

GroupValue95% CI
Total Number of Tissue Procurements4

Adverse events — posted to ClinicalTrials.gov

Time frame: SAEs and Other Adverse Events: following procurement of the subject's tissue for tissue manufacture and for up to 30 days following the last study treatment, a duration of approximately 12 months. All-cause Mortality: from randomization date and until death or protocol termination, up to 3 years.. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Group A: Vigil in Combination With Irinotecan and Temozolomide
Serious: 0/3 (0%)
Deaths: 2/3
Group B: Irinotecan and Temozolomide
Serious: 1/2 (50%)
Deaths: 1/2
Cross-over to Vigil Alone
Serious: 0/1 (0%)
Deaths: 0/1

Serious adverse events (5 terms)

ReactionSystemGroup A: Vigil in Combinat…Group B: Irinotecan and Te…Cross-over to Vigil Alone
DyspneaRespiratory, thoracic and mediastinal disorders
Pleural effusionRespiratory, thoracic and mediastinal disorders
HypoxiaRespiratory, thoracic and mediastinal disorders
AtelectasisRespiratory, thoracic and mediastinal disorders
Pulmonary EdemaRespiratory, thoracic and mediastinal disorders
Other adverse events (49 terms — click to expand)

ReactionSystemGroup A: Vigil in Combinat…Group B: Irinotecan and Te…Cross-over to Vigil Alone
NauseaGastrointestinal disorders
ConstipationGastrointestinal disorders
DiarrheaGastrointestinal disorders
VomitingGastrointestinal disorders
FatigueGeneral disorders
HypernatremiaMetabolism and nutrition disorders
CoughRespiratory, thoracic and mediastinal disorders
AnemiaBlood and lymphatic system disorders
PhotophobiaEye disorders
Abdominal painGastrointestinal disorders
Oral painGastrointestinal disorders
Reflux esophagitisGastrointestinal disorders
FeverGeneral disorders
Injection site reactionGeneral disorders
Non-cardiac chest painGeneral disorders
PainGeneral disorders
PneumoniaInfections and infestations
TonsillitisInfections and infestations
Infusion related reactionInjury, poisoning and procedural complications
Alkaline phosphatase increasedInvestigations
ALT increasedInvestigations
AST increasedInvestigations
Bilirubin increasedInvestigations
Chloride increasedInvestigations
Creatinine increasedInvestigations
Hemoglobin increasedInvestigations
Lymphocyte count decreasedInvestigations
Lymphocyte count increasedInvestigations
Neutrophil count decreasedInvestigations
Platelets decreasedInvestigations
WBC decreasedInvestigations
Weight lossInvestigations
HyperglycemiaMetabolism and nutrition disorders
HypoalbuminemiaMetabolism and nutrition disorders
HypoglycemiaMetabolism and nutrition disorders
HypokalemiaMetabolism and nutrition disorders
HyponatremiaMetabolism and nutrition disorders
ArthralgiaMusculoskeletal and connective tissue disorders
Back painMusculoskeletal and connective tissue disorders
DizzinessNervous system disorders

Most-reported serious reactions: Dyspnea, Pleural effusion, Hypoxia, Atelectasis, Pulmonary Edema.

Data from ClinicalTrials.gov NCT03495921 adverse events section.

Sponsor's own description

The goal of this clinical trial was to compare participants with first relapse or refractory Ewing's sarcoma when treated with investigational product (Vigil) in addition to the standard treatment of irinotecan and temozolomide compared to the standard treatment of irinotecan and temozolomide alone. The main question it aimed to answer is "Will participants who receive Vigil in addition to irinotecan and temozolomide have a prolonged time to progression and improved quality of life compared to the participants who receive irinotecan and temozolomide alone?".

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Targeting Tumor Microenvironment for Cancer Therapy.
    Roma-Rodrigues C, Mendes R, Baptista PV, Fernandes AR. · · 2019 · cited 865× · PMID 30781344 · DOI 10.3390/ijms20040840
  2. Vaccine Therapies for Cancer: Then and Now.
    Morse MA, Gwin WR, Mitchell DA. · · 2021 · cited 156× · PMID 33512679 · DOI 10.1007/s11523-020-00788-w
  3. TGF-beta signal transduction: biology, function and therapy for diseases.
    Tie Y, Tang F, Peng D, Zhang Y, et al · · 2022 · cited 97× · PMID 36534225 · DOI 10.1186/s43556-022-00109-9
  4. Management of recurrent Ewing sarcoma: challenges and approaches.
    Van Mater D, Wagner L. · · 2019 · cited 71× · PMID 30988632 · DOI 10.2147/ott.s170585
  5. Role of immunotherapy in Ewing sarcoma.
    Morales E, Olson M, Iglesias F, Dahiya S, et al · · 2020 · cited 70× · PMID 33293354 · DOI 10.1136/jitc-2020-000653
  6. Emerging novel agents for patients with advanced Ewing sarcoma: a report from the Children's Oncology Group (COG) New Agents for Ewing Sarcoma Task Force.
    Bailey K, Cost C, Davis I, Glade-Bender J, et al · · 2019 · cited 58× · PMID 31031965 · DOI 10.12688/f1000research.18139.1
  7. Why All the Fury over Furin?
    Osman EEA, Rehemtulla A, Neamati N. · · 2022 · cited 38× · PMID 34340303 · DOI 10.1021/acs.jmedchem.1c00518
  8. Immunotherapies for pediatric cancer: current landscape and future perspectives.
    Hutzen B, Paudel SN, Naeimi Kararoudi M, Cassady KA, et al · · 2019 · cited 25× · PMID 31828566 · DOI 10.1007/s10555-019-09819-z

Verify or expand the search:

Other trials of Vigil

Trials testing the same drug.

Other recruiting trials for Ewing Sarcoma

Currently open trials in the same condition.

Other Gradalis, Inc. trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03495921.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing