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NCT03467958

An Extension Study of Oral Ozanimod for Moderately to Severely Active Crohn's Disease

Terminated Phase 3 Results posted Last updated 17 September 2025
What this trial tests

Phase 3 trial testing Ozanimod in Crohn Disease in 854 participants. Terminated before completion.

Timeline
24 August 2018
Primary endpoint
31 October 2024
31 October 2024

Quick facts

Lead sponsorCelgene
PhasePhase 3
StatusTerminated
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment854
Start date24 August 2018
Primary completion31 October 2024
Estimated completion31 October 2024
Sites766 locations across Hong Kong, Colombia, Finland, Italy, Taiwan, Ireland, Poland, South Korea

Drugs / interventions tested

Conditions studied

Sponsor

Celgene — full company profile →

Who can join

Adults 18 to 75, any sex, with Crohn Disease. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Percentage of Participants With Clinical Remission Primary · At weeks 48, 96, 144, 192, 240

Clinical remission is defined as a Crohn's Disease Activity Index (CDAI) score of \< 150. The CDAI is a composite score that is used to measure the clinical activity of Crohn's disease (CD). The CDAI uses a questionnaire with 8 disease activity variables: number of soft/liquid stools, severity of abdominal pain, general well-being, presence of complications, need for antidiarrheal drugs, presence of an abdominal mass, hematocrit, and deviation in body weight. The sub scores of number of soft/liquid stool, severity of abdominal pain (0 \\\[none\\\] to 3 \\\[Severe\\\]), general well-being (0 \\

Week 48
GroupValue95% CI
RPC01-3201/3202 Placebo19.6
RPC01-3201/3202 Ozanimod 0.92 mg21.0
RPC01-3203 Placebo-Placebo Completers60.6
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers58.8
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers56.0
RPC01-3203 Placebo-Placebo Relapse34.2
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse27.3
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse20.0
RPC01-2201 Ozanimod 0.92 mg84.6
Week 96
GroupValue95% CI
RPC01-3201/3202 Placebo12.3
RPC01-3201/3202 Ozanimod 0.92 mg12.5
RPC01-3203 Placebo-Placebo Completers37.9
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers41.2
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers38.5
RPC01-3203 Placebo-Placebo Relapse18.4
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse15.2
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse15.0
RPC01-2201 Ozanimod 0.92 mg84.6
Week 144
GroupValue95% CI
RPC01-3201/3202 Placebo6.1
RPC01-3201/3202 Ozanimod 0.92 mg7.0
RPC01-3203 Placebo-Placebo Completers22.7
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers23.5
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers18.7
RPC01-3203 Placebo-Placebo Relapse13.2
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse12.1
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse0
RPC01-2201 Ozanimod 0.92 mg61.5
Week 192
GroupValue95% CI
RPC01-3201/3202 Placebo4.5
RPC01-3201/3202 Ozanimod 0.92 mg4.6
RPC01-3203 Placebo-Placebo Completers6.1
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers11.8
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers9.9
RPC01-3203 Placebo-Placebo Relapse2.6
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse3.0
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse5.0
RPC01-2201 Ozanimod 0.92 mg30.8
Week 240
GroupValue95% CI
RPC01-3201/3202 Placebo2.8
RPC01-3201/3202 Ozanimod 0.92 mg3.6
RPC01-3203 Placebo-Placebo Completers1.5
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers3.5
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers1.1
RPC01-3203 Placebo-Placebo Relapse2.6
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse0
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse5.0
RPC01-2201 Ozanimod 0.92 mg38.5
Number of Participants With Treatment Emergent Adverse Events (TEAEs) Primary · From first dose to 90 days post last dose (up to approximately an average of 19 months and a maximum of 65 months)

A treatment-emergent adverse event (TEAE) is any AE that emerges or worsens between the day of the first dose of Open-label Extension Study and 90 days after the last dose of Open-label Extension Study. An Adverse Event (AE) is defined as any new untoward medical occurrence or worsening of a preexisting medical condition in a clinical investigation participant administered study treatment and that does not necessarily have a causal relationship with this treatment. Serious Adverse Events (SAEs) is any untoward medical occurrence that, at any dose: results in death; is life-threatening; require

TEAE
GroupValue95% CI
RPC01-3201/3202 Placebo140
RPC01-3201/3202 Ozanimod 0.92 mg247
RPC01-3203 Placebo-Placebo Completers42
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers63
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers52
RPC01-3203 Placebo-Placebo Relapse26
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse22
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse14
RPC01-2201 Ozanimod 0.92 mg11
Serious TEAE
GroupValue95% CI
RPC01-3201/3202 Placebo38
RPC01-3201/3202 Ozanimod 0.92 mg59
RPC01-3203 Placebo-Placebo Completers9
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers11
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers11
RPC01-3203 Placebo-Placebo Relapse6
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse4
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse2
RPC01-2201 Ozanimod 0.92 mg2
TEAE leading to discontinuation to study drug
GroupValue95% CI
RPC01-3201/3202 Placebo30
RPC01-3201/3202 Ozanimod 0.92 mg43
RPC01-3203 Placebo-Placebo Completers4
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers5
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers3
RPC01-3203 Placebo-Placebo Relapse4
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse7
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse5
RPC01-2201 Ozanimod 0.92 mg1
Percentage of Participants With Abdominal Pain (AP) and Stool Frequency (SF) Clinical Remission Secondary · At weeks 48, 96, 144, 192, 240

Abdominal pain (AP) and stool frequency (SF) clinical remission was defined as average daily abdominal pain score ≤ 1 point, and average daily stool frequency ≤ 3 points with AP and SF no worse than baseline. Participants entered responses in diaries daily. The 7 days entries prior to visit were considered for calculating average AP score and SF. The AP was graded on severity of 0 (none) to 3 (severe) scale and SF was defined number of liquid or soft stools per day. Higher scores indicated worse outcomes.

Week 48
GroupValue95% CI
RPC01-3201/3202 Placebo16.2
RPC01-3201/3202 Ozanimod 0.92 mg21.3
RPC01-3203 Placebo-Placebo Completers53.0
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers52.9
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers45.1
RPC01-3203 Placebo-Placebo Relapse34.2
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse18.2
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse20.0
RPC01-2201 Ozanimod 0.92 mg0
Week 96
GroupValue95% CI
RPC01-3201/3202 Placebo11.2
RPC01-3201/3202 Ozanimod 0.92 mg11.6
RPC01-3203 Placebo-Placebo Completers37.9
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers36.5
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers36.3
RPC01-3203 Placebo-Placebo Relapse18.4
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse12.1
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse15.0
RPC01-2201 Ozanimod 0.92 mg0
Week 144
GroupValue95% CI
RPC01-3201/3202 Placebo5.6
RPC01-3201/3202 Ozanimod 0.92 mg7.3
RPC01-3203 Placebo-Placebo Completers21.2
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers24.7
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers14.3
RPC01-3203 Placebo-Placebo Relapse13.2
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse12.1
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse0
RPC01-2201 Ozanimod 0.92 mg0
Week 192
GroupValue95% CI
RPC01-3201/3202 Placebo2.8
RPC01-3201/3202 Ozanimod 0.92 mg4.9
RPC01-3203 Placebo-Placebo Completers6.1
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers10.6
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers7.7
RPC01-3203 Placebo-Placebo Relapse2.6
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse3.0
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse5.0
RPC01-2201 Ozanimod 0.92 mg0
Week 240
GroupValue95% CI
RPC01-3201/3202 Placebo3.4
RPC01-3201/3202 Ozanimod 0.92 mg3.0
RPC01-3203 Placebo-Placebo Completers1.5
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers1.2
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers1.1
RPC01-3203 Placebo-Placebo Relapse0
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse0
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse5.0
RPC01-2201 Ozanimod 0.92 mg0
Percentage of Participants With Clinical Response Secondary · At weeks 48, 96, 144, 192, 240

Clinical response is defined as a Crohn's Disease Activity Index (CDAI) reduction from baseline of ≥ 100 points or CDAI score of \< 150. The CDAI is a composite score that is used to measure the clinical activity of Crohn's disease (CD). The CDAI uses a questionnaire with 8 disease activity variables: number of soft/liquid stools, severity of abdominal pain, general well-being, presence of complications, need for antidiarrheal drugs, presence of an abdominal mass, hematocrit, and deviation in body weight. The sub scores of number of soft/liquid stool, severity of abdominal pain (0 \\\[none\\\]

Week 48
GroupValue95% CI
RPC01-3201/3202 Placebo26.8
RPC01-3201/3202 Ozanimod 0.92 mg29.2
RPC01-3203 Placebo-Placebo Completers62.1
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers64.7
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers61.5
RPC01-3203 Placebo-Placebo Relapse36.8
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse30.3
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse20.0
RPC01-2201 Ozanimod 0.92 mg84.6
Week 96
GroupValue95% CI
RPC01-3201/3202 Placebo15.1
RPC01-3201/3202 Ozanimod 0.92 mg17.3
RPC01-3203 Placebo-Placebo Completers43.9
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers44.7
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers45.1
RPC01-3203 Placebo-Placebo Relapse18.4
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse15.2
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse15.0
RPC01-2201 Ozanimod 0.92 mg84.6
Week 144
GroupValue95% CI
RPC01-3201/3202 Placebo8.9
RPC01-3201/3202 Ozanimod 0.92 mg9.4
RPC01-3203 Placebo-Placebo Completers22.7
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers28.2
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers19.8
RPC01-3203 Placebo-Placebo Relapse13.2
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse12.1
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse0
RPC01-2201 Ozanimod 0.92 mg61.5
Week 192
GroupValue95% CI
RPC01-3201/3202 Placebo5.0
RPC01-3201/3202 Ozanimod 0.92 mg6.4
RPC01-3203 Placebo-Placebo Completers6.1
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers12.9
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers11.0
RPC01-3203 Placebo-Placebo Relapse2.6
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse3.0
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse5.0
RPC01-2201 Ozanimod 0.92 mg30.8
Week 240
GroupValue95% CI
RPC01-3201/3202 Placebo3.9
RPC01-3201/3202 Ozanimod 0.92 mg4.6
RPC01-3203 Placebo-Placebo Completers1.5
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers3.5
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers2.2
RPC01-3203 Placebo-Placebo Relapse2.6
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse0
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse5.0
RPC01-2201 Ozanimod 0.92 mg38.5

Adverse events — posted to ClinicalTrials.gov

Time frame: Participants were assessed for all-cause mortality from their first dose to their study completion (up to approximately 74 months). SAEs and Other AEs were assessed from first dose to 90 days post the last dose (up to approximately an average of 19 months and a maximum of 65 months).. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

RPC01-3201/3202 Placebo
Serious: 38/179 (21%)
Deaths: 0/179
RPC01-3201/3202 Ozanimod 0.92 mg
Serious: 59/329 (18%)
Deaths: 0/329
RPC01-3203 Placebo-Placebo Completers
Serious: 9/66 (14%)
Deaths: 0/66
RPC01-3203 Ozanimod 0.92 Mg-Placebo Completers
Serious: 11/85 (13%)
Deaths: 0/85
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Completers
Serious: 11/91 (12%)
Deaths: 1/91
RPC01-3203 Placebo-Placebo Relapse
Serious: 6/38 (16%)
Deaths: 0/38
RPC01-3203 Ozanimod 0.92 Mg-Placebo Relapse
Serious: 4/33 (12%)
Deaths: 0/33
RPC01-3203 Ozanimod 0.92 Mg-Ozanimod 0.92 mg Relapse
Serious: 2/20 (10%)
Deaths: 0/20
RPC01-2201 Ozanimod 0.92 mg
Serious: 2/13 (15%)
Deaths: 0/13

Serious adverse events (97 terms)

ReactionSystemRPC01-3201/3202 PlaceboRPC01-3201/3202 Ozanimod 0…RPC01-3203 Placebo-Placebo…RPC01-3203 Ozanimod 0.92 M…RPC01-3203 Ozanimod 0.92 M…RPC01-3203 Placebo-Placebo…RPC01-3203 Ozanimod 0.92 M…RPC01-3203 Ozanimod 0.92 M…RPC01-2201 Ozanimod 0.92 mg
Crohn's diseaseGastrointestinal disorders
Abdominal painGastrointestinal disorders
Anal fistulaGastrointestinal disorders
Intestinal fistulaGastrointestinal disorders
Small intestinal obstructionGastrointestinal disorders
HypersensitivityImmune system disorders
EpilepsyNervous system disorders
AnaemiaBlood and lymphatic system disorders
Iron deficiency anaemiaBlood and lymphatic system disorders
ThrombocytopeniaBlood and lymphatic system disorders
BradycardiaCardiac disorders
Cardiac arrestCardiac disorders
Urachal abnormalityCongenital, familial and genetic disorders
Macular oedemaEye disorders
Retinal degenerationEye disorders
Retinal detachmentEye disorders
Abdominal herniaGastrointestinal disorders
Abdominal pain lowerGastrointestinal disorders
Anal cystGastrointestinal disorders
ColitisGastrointestinal disorders
Diarrhoea haemorrhagicGastrointestinal disorders
Diverticulum intestinal haemorrhagicGastrointestinal disorders
Enterocolonic fistulaGastrointestinal disorders
Gastrointestinal haemorrhageGastrointestinal disorders
Gastrointestinal motility disorderGastrointestinal disorders
Other adverse events (81 terms — click to expand)

ReactionSystemRPC01-3201/3202 PlaceboRPC01-3201/3202 Ozanimod 0…RPC01-3203 Placebo-Placebo…RPC01-3203 Ozanimod 0.92 M…RPC01-3203 Ozanimod 0.92 M…RPC01-3203 Placebo-Placebo…RPC01-3203 Ozanimod 0.92 M…RPC01-3203 Ozanimod 0.92 M…RPC01-2201 Ozanimod 0.92 mg
LymphopeniaBlood and lymphatic system disorders
Crohn's diseaseGastrointestinal disorders
COVID-19Infections and infestations
ArthralgiaMusculoskeletal and connective tissue disorders
Abdominal painGastrointestinal disorders
Upper respiratory tract infectionInfections and infestations
AnaemiaBlood and lymphatic system disorders
NasopharyngitisInfections and infestations
HeadacheNervous system disorders
DiarrhoeaGastrointestinal disorders
VomitingGastrointestinal disorders
PyrexiaGeneral disorders
HypertensionVascular disorders
NauseaGastrointestinal disorders
SinusitisInfections and infestations
Urinary tract infectionInfections and infestations
LeukopeniaBlood and lymphatic system disorders
Abdominal pain upperGastrointestinal disorders
FatigueGeneral disorders
BronchitisInfections and infestations
Back painMusculoskeletal and connective tissue disorders
CoughRespiratory, thoracic and mediastinal disorders
Oropharyngeal painRespiratory, thoracic and mediastinal disorders
Visual impairmentEye disorders
ConstipationGastrointestinal disorders
RashSkin and subcutaneous tissue disorders
DyspepsiaGastrointestinal disorders
Rectal haemorrhageGastrointestinal disorders
ToothacheGastrointestinal disorders
Herpes zosterInfections and infestations
AlopeciaSkin and subcutaneous tissue disorders
PruritusSkin and subcutaneous tissue disorders
VertigoEar and labyrinth disorders
Abdominal tendernessGastrointestinal disorders
StomatitisGastrointestinal disorders
Oedema peripheralGeneral disorders
Peripheral swellingGeneral disorders
CholelithiasisHepatobiliary disorders
CholestasisHepatobiliary disorders
Clostridium difficile colitisInfections and infestations

Most-reported serious reactions: Crohn's disease, Abdominal pain, Anal fistula, Intestinal fistula, Small intestinal obstruction, Hypersensitivity, Epilepsy, Anaemia.

Data from ClinicalTrials.gov NCT03467958 adverse events section.

Sponsor's own description

This is an extension study to evaluate safety and efficacy of ozanimod in participants with moderately to severely active Crohn's Disease.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Targeting Sphingosine-1-Phosphate Signaling in Immune-Mediated Diseases: Beyond Multiple Sclerosis.
    Pérez-Jeldres T, Alvarez-Lobos M, Rivera-Nieves J. · · 2021 · cited 150× · PMID 33983615 · DOI 10.1007/s40265-021-01528-8
  2. Novel and Emerging Therapies for Inflammatory Bowel Disease.
    Al-Bawardy B, Shivashankar R, Proctor DD. · · 2021 · cited 117× · PMID 33935763 · DOI 10.3389/fphar.2021.651415
  3. Perspectives on Current and Novel Treatments for Inflammatory Bowel Disease.
    Na SY, Moon W. · · 2019 · cited 99× · PMID 31195433 · DOI 10.5009/gnl19019
  4. The S1P-S1PR Axis in Neurological Disorders-Insights into Current and Future Therapeutic Perspectives.
    Lucaciu A, Brunkhorst R, Pfeilschifter JM, Pfeilschifter W, et al · · 2020 · cited 53× · PMID 32580348 · DOI 10.3390/cells9061515
  5. Inflammatory Bowel Disease: Emerging Therapies and Future Treatment Strategies.
    Bretto E, Ribaldone DG, Caviglia GP, Saracco GM, et al · · 2023 · cited 38× · PMID 37626745 · DOI 10.3390/biomedicines11082249
  6. Sphingosine 1-Phosphate Modulation in Inflammatory Bowel Diseases: Keeping Lymphocytes Out of the Intestine.
    Dal Buono A, Gabbiadini R, Alfarone L, Solitano V, et al · · 2022 · cited 32× · PMID 35885040 · DOI 10.3390/biomedicines10071735
  7. Review article: the sphingosine 1 phosphate/sphingosine 1 phosphate receptor axis - a unique therapeutic target in inflammatory bowel disease.
    Wang J, Goren I, Yang B, Lin S, et al · · 2022 · cited 31× · PMID 34932238 · DOI 10.1111/apt.16741
  8. Sphingosine-1 Phosphate Receptor Modulators: The Next Wave of Oral Therapies in Inflammatory Bowel Disease.
    Choden T, Cohen NA, Rubin DT. · · 2022 · cited 27× · PMID 36397756

Verify or expand the search:

Other trials of Ozanimod

Trials testing the same drug.

Other recruiting trials for Crohn Disease

Currently open trials in the same condition.

Other Celgene trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03467958.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing