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NCT03366337: PHOENIX

A Phase 2 Trial of the Safety and Efficacy of Bardoxolone Methyl in Patients With Rare Chronic Kidney Diseases - PHOENIX

Completed Phase 2 Results posted Last updated 3 June 2025
What this trial tests

Phase 2 trial testing Bardoxolone methyl capsules in IgA Nephropathy in 103 participants. Completed in 29 January 2019.

Timeline
26 December 2017
Primary endpoint
2 January 2019
29 January 2019

Quick facts

Lead sponsorBiogen
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationnon randomized
Designparallel
Maskingnone
Primary purposetreatment
Enrollment103
Start date26 December 2017
Primary completion2 January 2019
Estimated completion29 January 2019
Sites30 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

Biogen — full company profile →

Who can join

Adults 18 to 65, any sex, with IgA Nephropathy or CKD Associated With Type 1 Diabetes. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Change From Baseline in Estimated Glomerular Filtration Rate (eGFR) at Week 12 Primary · 12 weeks after participant receives the first dose

To assess the change in eGFR from baseline to week 12. eGFR is a measure of kidney function assessed through blood/serum. Higher eGFRs represent better/improved kidney function. Lower eGFRs represent poorer/decreased kidney function.

GroupValue95% CI
Bardoxolone Methyl - ADPKD9.31± 1.3743
Bardoxolone Methyl - IgAN8.00± 1.5700
Bardoxolone Methyl - T1D5.46± 2.2792
Bardoxolone Methyl - FSGS7.83± 2.216

Adverse events — posted to ClinicalTrials.gov

Time frame: 16 weeks. Reporting threshold: 2%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Bardoxolone Methyl - ADPKD
Serious: 2/31 (6%)
Deaths: 0/31
Bardoxolone Methyl - IgAN
Serious: 0/26 (0%)
Deaths: 0/26
Bardoxolone Methyl - T1D
Serious: 0/28 (0%)
Deaths: 0/28
Bardoxolone Methyl - FSGS
Serious: 1/18 (6%)
Deaths: 0/18

Serious adverse events (5 terms)

ReactionSystemBardoxolone Methyl - ADPKDBardoxolone Methyl - IgANBardoxolone Methyl - T1DBardoxolone Methyl - FSGS
CholecystitisHepatobiliary disorders
Histoplasmosis disseminatedInfections and infestations
SepsisInfections and infestations
Renal failure acuteRenal and urinary disorders
Hypertensive crisisVascular disorders
Other adverse events (164 terms — click to expand)

ReactionSystemBardoxolone Methyl - ADPKDBardoxolone Methyl - IgANBardoxolone Methyl - T1DBardoxolone Methyl - FSGS
Muscle spasmsMusculoskeletal and connective tissue disorders
HeadacheNervous system disorders
NauseaGastrointestinal disorders
FatigueGeneral disorders
Upper respiratory tract infectionInfections and infestations
Transaminases increasedInvestigations
HypertensionVascular disorders
PalpitationsCardiac disorders
ConstipationGastrointestinal disorders
Oedema peripheralGeneral disorders
NasopharyngitisInfections and infestations
Hepatic enzyme increasedInvestigations
HypoglycaemiaMetabolism and nutrition disorders
ArthralgiaMusculoskeletal and connective tissue disorders
MyalgiaMusculoskeletal and connective tissue disorders
ThrombocytopeniaBlood and lymphatic system disorders
Abdominal distensionGastrointestinal disorders
Abdominal painGastrointestinal disorders
DiarrhoeaGastrointestinal disorders
Dry mouthGastrointestinal disorders
VomitingGastrointestinal disorders
Chest painGeneral disorders
BronchitisInfections and infestations
SinusitisInfections and infestations
Urinary tract infectionInfections and infestations
Blood creatinine increasedInvestigations
Brain natriuretic peptide increasedInvestigations
N-terminal prohormone brain natriuretic peptide increasedInvestigations
Decreased appetiteMetabolism and nutrition disorders
GoutMetabolism and nutrition disorders
HyperglycaemiaMetabolism and nutrition disorders
HyperkalaemiaMetabolism and nutrition disorders
Back painMusculoskeletal and connective tissue disorders
Muscular weaknessMusculoskeletal and connective tissue disorders
Musculoskeletal painMusculoskeletal and connective tissue disorders
DizzinessNervous system disorders
DysgeusiaNervous system disorders
RashSkin and subcutaneous tissue disorders
Rash maculo-papularSkin and subcutaneous tissue disorders
HypotensionVascular disorders

Most-reported serious reactions: Cholecystitis, Histoplasmosis disseminated, Sepsis, Renal failure acute, Hypertensive crisis.

Data from ClinicalTrials.gov NCT03366337 adverse events section.

Sponsor's own description

This multi-center, open-label Phase 2 trial will study the safety, tolerability, and efficacy of bardoxolone methyl in qualified patients with the following rare chronic kidney diseases (CKD): CKD associated with type 1 diabetes (T1D), IgA nephropathy (IgAN), focal segmental glomerulosclerosis (FSGS), and autosomal dominant polycystic kidney disease (ADPKD). Patients will be enrolled in disease specific cohorts within the trial, and effectiveness of bardoxolone methyl in treating CKD will be assessed separately by cohort for each rare CKD. All patients in the study will follow the same visit and assessment schedule. Following randomization on Day 1, patients will be scheduled to be assessed during treatment at Weeks 1, 2, 4, 6, 8, and 12, and by telephone contact on Days 3, 10, 21, 31, 38, and 45. Patients will also be scheduled to be assessed at an in-person follow-up visit at Week 16, four weeks after the end of treatment.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Kidney fibrosis: from mechanisms to therapeutic medicines.
    Huang R, Fu P, Ma L. · · 2023 · cited 453× · PMID 36932062 · DOI 10.1038/s41392-023-01379-7
  2. Activators and Inhibitors of NRF2: A Review of Their Potential for Clinical Development.
    Robledinos-Antón N, Fernández-Ginés R, Manda G, Cuadrado A. · · 2019 · cited 443× · PMID 31396308 · DOI 10.1155/2019/9372182
  3. Podocytopathies.
    Kopp JB, Anders HJ, Susztak K, Podestà MA, et al · · 2020 · cited 427× · PMID 32792490 · DOI 10.1038/s41572-020-0196-7
  4. Pathogenic Pathways and Therapeutic Approaches Targeting Inflammation in Diabetic Nephropathy.
    Rayego-Mateos S, Morgado-Pascual JL, Opazo-Ríos L, Guerrero-Hue M, et al · · 2020 · cited 237× · PMID 32471207 · DOI 10.3390/ijms21113798
  5. Can Activation of NRF2 Be a Strategy against COVID-19?
    Cuadrado A, Pajares M, Benito C, Jiménez-Villegas J, et al · · 2020 · cited 168× · PMID 32711925 · DOI 10.1016/j.tips.2020.07.003
  6. Glomerulonephritis: immunopathogenesis and immunotherapy.
    Anders HJ, Kitching AR, Leung N, Romagnani P. · · 2023 · cited 105× · PMID 36635359 · DOI 10.1038/s41577-022-00816-y
  7. Therapeutic trials in adult FSGS: lessons learned and the road forward.
    De Vriese AS, Wetzels JF, Glassock RJ, Sethi S, et al · · 2021 · cited 82× · PMID 34017116 · DOI 10.1038/s41581-021-00427-1
  8. Nrf2: The Master and Captain of Beta Cell Fate.
    Baumel-Alterzon S, Katz LS, Brill G, Garcia-Ocaña A, et al · · 2021 · cited 81× · PMID 33243626 · DOI 10.1016/j.tem.2020.11.002

Verify or expand the search:

Other trials of Bardoxolone methyl capsules

Trials testing the same drug.

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Other Biogen trials

Trials by the same sponsor.

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Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03366337.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing