Last reviewed · How we verify

NCT03266588

Open Label Safety Study in Acute Treatment of Migraine

Completed Phase 2, PHASE3 Results posted Last updated 16 February 2023
What this trial tests

Phase 2, PHASE3 trial testing Rimegepant in Migraine, With or Without Aura in 3,019 participants. Completed in 15 July 2019.

Timeline
30 August 2017
Primary endpoint
15 July 2019
15 July 2019

Quick facts

Lead sponsorPfizer
PhasePhase 2, PHASE3
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment3,019
Start date30 August 2017
Primary completion15 July 2019
Estimated completion15 July 2019
Sites98 locations across United States

Drugs / interventions tested

Conditions studied

Sponsor

Pfizer — full company profile →

Who can join

18 and older, any sex, with Migraine, With or Without Aura. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Number of Participants With SAEs and AEs Leading to Discontinuation During the Treatment Period Primary · PRN (2-8) and PRN (9-14) groups: Up to 52 weeks; Scheduled EOD + PRN group: Up to 12 weeks

An AE was defined as any new untoward medical occurrence or worsening of a pre-existing medical condition on-treatment in a patient or clinical investigation participant administered an investigational (medicinal) product and that did not necessarily have a causal relationship with this treatment. An SAE was defined as any event that met any of the following criteria: death; life-threatening; inpatient hospitalization or prolongation of existing hospitalization; persistent or significant disability/incapacity; congenital anomaly/birth defect in the offspring of a participant who received rimeg

Overall number of participants with at least 1 AE
GroupValue95% CI
PRN (2-8) Group664
PRN (9-14) Group315
Scheduled EOD + PRN Group109
AE ≥5%-Upper respiratory tract infection
GroupValue95% CI
PRN (2-8) Group108
PRN (9-14) Group38
Scheduled EOD + PRN Group12
Mild-Upper respiratory tract infection
GroupValue95% CI
PRN (2-8) Group56
PRN (9-14) Group21
Scheduled EOD + PRN Group8
Moderate-Upper respiratory tract infection
GroupValue95% CI
PRN (2-8) Group51
PRN (9-14) Group17
Scheduled EOD + PRN Group4
Severe-Upper respiratory tract infection
GroupValue95% CI
PRN (2-8) Group1
PRN (9-14) Group0
Scheduled EOD + PRN Group0
AE ≥5%-Nasopharyngitis
GroupValue95% CI
PRN (2-8) Group72
PRN (9-14) Group41
Scheduled EOD + PRN Group9
Mild-Nasopharyngitis
GroupValue95% CI
PRN (2-8) Group53
PRN (9-14) Group28
Scheduled EOD + PRN Group7
Moderate-Nasopharyngitis
GroupValue95% CI
PRN (2-8) Group19
PRN (9-14) Group13
Scheduled EOD + PRN Group2
Number of Participants With Clinically Significant Laboratory Abnormalities During the Treatment Period Primary · PRN (2-8) and PRN (9-14) groups: Up to 52 weeks: Scheduled EOD + PRN group: Up to 12 weeks

Clinically significant laboratory abnormalities were defined as Grade 3 to 4 on-treatment laboratory test results according to numeric laboratory test criteria found in Common Technical Criteria for Adverse Events (CTCAE) Version 5.0 (2017) if available; otherwise, according to Division of Acquired Immune Deficiency Syndrome (DAIDS) Table for Grading the Severity of Adult and Pediatric Adverse Events Corrected Version 2.1 (2017) for Glucose, LDL-Cholesterol, Uric Acid, and Urinalysis. Laboratory test groups of clinical interest included hematology, serum chemistry, and urinalysis. Participants

Alanine Aminotransferase (ALT)
GroupValue95% CI
PRN (2-8) Group3
PRN (9-14) Group2
Scheduled EOD + PRN Group0
Aspartate Aminotransferase (AST)
GroupValue95% CI
PRN (2-8) Group4
PRN (9-14) Group2
Scheduled EOD + PRN Group0
Albumin
GroupValue95% CI
PRN (2-8) Group0
PRN (9-14) Group0
Scheduled EOD + PRN Group0
Alkaline Phosphatase
GroupValue95% CI
PRN (2-8) Group0
PRN (9-14) Group0
Scheduled EOD + PRN Group0
Bicarbonate
GroupValue95% CI
PRN (2-8) Group0
PRN (9-14) Group0
Scheduled EOD + PRN Group0
Bilirubin
GroupValue95% CI
PRN (2-8) Group0
PRN (9-14) Group0
Scheduled EOD + PRN Group0
Calcium, Low
GroupValue95% CI
PRN (2-8) Group0
PRN (9-14) Group0
Scheduled EOD + PRN Group0
Calcium, High
GroupValue95% CI
PRN (2-8) Group0
PRN (9-14) Group0
Scheduled EOD + PRN Group0
Percentage of Participants With Elevations of AST or ALT > 3 x Upper Limit of Normal (ULN) Concurrent With Total Bilirubin > 2 x ULN During the Treatment Period Secondary · PRN (2-8) and PRN (9-14) groups: Up to 52 weeks; Scheduled EOD + PRN group: Up to 12 weeks

Elevations of on-treatment AST or ALT \> 3 x ULN concurrent with total bilirubin \> 2 x ULN were defined as elevations on the same collection date.

GroupValue95% CI
PRN (2-8) Group0.10.00 – 0.60
PRN (9-14) Group00.00 – 0.96
Scheduled EOD + PRN Group00.00 – 1.60
Number of Participants With Hepatic-related AEs and Hepatic-related AEs Leading to Discontinuation During the Treatment Period Secondary · PRN (2-8) and PRN (9-14) groups: Up to 52 weeks; Scheduled EOD + PRN group: Up to 12 weeks

An AE was defined as any new untoward medical occurrence or worsening of a pre-existing medical condition on-treatment in a patient or clinical investigation patient administered an investigational (medicinal) product and that does not necessarily have a causal relationship with this treatment. Hepatic AEs were defined as all on-treatment PTs under the "Hepatic Disorders" Standardized Medical Dictionary (Version 21.1) for Regulatory Activities Query (SMQ), except those PTs in the "Congenital, Familial, Neonatal and Genetic Disorders of the Liver" SMQ.

Hepatic-related AE
GroupValue95% CI
PRN (2-8) Group16
PRN (9-14) Group10
Scheduled EOD + PRN Group0
Hepatic-related AE leading to discontinuation
GroupValue95% CI
PRN (2-8) Group3
PRN (9-14) Group3
Scheduled EOD + PRN Group0

Adverse events — posted to ClinicalTrials.gov

Time frame: Adverse events were reported from start of study drug treatment up to 52 weeks. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

PRN (2-8) Group
Serious: 28/1033 (3%)
Deaths: 0/1033
PRN (9-14) Group
Serious: 16/481 (3%)
Deaths: 0/481
Scheduled EOD + PRN Group
Serious: 3/286 (1%)
Deaths: 0/286

Serious adverse events (42 terms)

ReactionSystemPRN (2-8) GroupPRN (9-14) GroupScheduled EOD + PRN Group
AppendicitisInfections and infestations
Accidental overdoseInjury, poisoning and procedural complications
PneumoniaInfections and infestations
OsteoarthritisMusculoskeletal and connective tissue disorders
AnaemiaBlood and lymphatic system disorders
Appendiceal mucocoeleGastrointestinal disorders
Colitis ischaemicGastrointestinal disorders
ConstipationGastrointestinal disorders
Diabetic gastroparesisGastrointestinal disorders
GastritisGastrointestinal disorders
Pancreatitis acuteGastrointestinal disorders
Peritoneal haemorrhageGastrointestinal disorders
Chest painGeneral disorders
PyrexiaGeneral disorders
CholecystitisHepatobiliary disorders
Cholecystitis chronicHepatobiliary disorders
BronchitisInfections and infestations
CellulitisInfections and infestations
Gastroenteritis viralInfections and infestations
InfluenzaInfections and infestations
MastitisInfections and infestations
SepsisInfections and infestations
Viral sepsisInfections and infestations
ArthritisMusculoskeletal and connective tissue disorders
Musculoskeletal chest painMusculoskeletal and connective tissue disorders
Other adverse events (3 terms — click to expand)

ReactionSystemPRN (2-8) GroupPRN (9-14) GroupScheduled EOD + PRN Group
Upper respiratory tract infectionInfections and infestations
NasopharyngitisInfections and infestations
SinusitisInfections and infestations

Most-reported serious reactions: Appendicitis, Accidental overdose, Pneumonia, Osteoarthritis, Anaemia, Appendiceal mucocoele, Colitis ischaemic, Constipation.

Data from ClinicalTrials.gov NCT03266588 adverse events section.

Sponsor's own description

The purpose of this study is to evaluate safety and tolerability of BHV-3000 (rimegepant).

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Calcitonin gene-related peptide (CGRP): role in migraine pathophysiology and therapeutic targeting.
    Wattiez AS, Sowers LP, Russo AF. · · 2020 · cited 140× · PMID 32003253 · DOI 10.1080/14728222.2020.1724285
  2. Safety of Rimegepant, an Oral CGRP Receptor Antagonist, Plus CGRP Monoclonal Antibodies for Migraine.
    Berman G, Croop R, Kudrow D, Halverson P, et al · · 2020 · cited 64× · PMID 32799325 · DOI 10.1111/head.13930
  3. Potential for treatment benefit of small molecule CGRP receptor antagonist plus monoclonal antibody in migraine therapy.
    Mullin K, Kudrow D, Croop R, Lovegren M, et al · · 2020 · cited 50× · PMID 31932515 · DOI 10.1212/wnl.0000000000008944
  4. A multicenter, open-label long-term safety study of rimegepant for the acute treatment of migraine.
    Croop R, Berman G, Kudrow D, Mullin K, et al · · 2024 · cited 33× · PMID 38659334 · DOI 10.1177/03331024241232944
  5. Calcitonin Gene-Related Peptide (CGRP)-Targeted Monoclonal Antibodies and Antagonists in Migraine: Current Evidence and Rationale.
    Cohen F, Yuan H, Silberstein SD. · · 2022 · cited 28× · PMID 35476215 · DOI 10.1007/s40259-022-00530-0
  6. Monthly migraine days, tablet utilization, and quality of life associated with Rimegepant - post hoc results from an open label safety study (BHV3000-201).
    Johnston K, Harris L, Powell L, Popoff E, et al · · 2022 · cited 27× · PMID 35038983 · DOI 10.1186/s10194-021-01378-5
  7. Migraine: Advances in the Pathogenesis and Treatment.
    Pleș H, Florian IA, Timis TL, Covache-Busuioc RA, et al · · 2023 · cited 24× · PMID 37755358 · DOI 10.3390/neurolint15030067
  8. CGRP Receptor Antagonists and 5-HT1F Receptor Agonist in the Treatment of Migraine.
    Capi M, De Angelis V, De Bernardini D, De Luca O, et al · · 2021 · cited 19× · PMID 33916043 · DOI 10.3390/jcm10071429

Verify or expand the search:

Other trials of Rimegepant

Trials testing the same drug.

Other Pfizer trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03266588.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing