Last reviewed · How we verify

NCT03255226

Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics Study of Tolvaptan in Pediatric Congestive Heart Failure (CHF) Patients With Volume Overload

Completed Phase 3 Results posted Last updated 23 August 2024
What this trial tests

Phase 3 trial testing Tolvaptan in Pediatric Congestive Heart Failure (CHF) Patients With Volume Overload in 60 participants. Completed in 15 July 2021.

Timeline
7 March 2018
Primary endpoint
11 July 2021
15 July 2021

Quick facts

Lead sponsorOtsuka Pharmaceutical Co., Ltd.
PhasePhase 3
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment60
Start date7 March 2018
Primary completion11 July 2021
Estimated completion15 July 2021
Sites1 location across Japan

Drugs / interventions tested

Conditions studied

Sponsor

Otsuka Pharmaceutical Co., Ltd. — full company profile →

Who can join

Adults 6 Months to 14, any sex, with Pediatric Congestive Heart Failure (CHF) Patients With Volume Overload. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Percentages of Subjects Whose Was Decreased by 1.7% or More Body Weight From Baseline Primary · Day after Day 3 at evaluation dose

The primary endpoint of this trial was the percentage of subjects whose body weight on the day after the third day of treatment with tolvaptan at the evaluation dose (the third day of administration at the evaluation dose) was decreased by 1.7% or more from the weight measured before breakfast (baseline) on the first day of the treatment period (the initial tolvaptan administration day), under the condition that the mean daily urine volume for the 3 days of treatment with tolvaptan at the evaluation dose was higher than the daily urine volume for the pretreatment observation period. The perce

GroupValue95% CI
Tolvaptan22.812.7 – 35.8
Change Rate From Baseline in Daily Urine Volume Secondary · Baseline, Day1, Day2 and Day3 of administration at evaluation dose

Daily urine volume was measured for the time interval starting at urination (an instruction to urinate) after breakfast and ending at complete urination immediately before administration on the following day. Baseline was 100% and the change rate was calculated like this. Percent change (%) = (\[daily urine volume on the Day1, Day2 and Day3 of the tolvaptan at the evaluation dose\] - \[daily urine volume on baseline\] ) / \[daily urine volume on baseline\] ×100

Day 1
GroupValue95% CI
Tolvaptan53.1± 52.9
Day 2
GroupValue95% CI
Tolvaptan47.8± 43.3
Day 3
GroupValue95% CI
Tolvaptan45.8± 29.3
Percent Changes From Baseline in Body Weight (kg) Secondary · Day after Day 3 at evaluation dose

Percent change from baseline in body weight (kg) on the day after the third day of treatment with tolvaptan at the evaluation dose was evaluated. For body weight measured on the day after the third day of administration at the evaluation dose, their percent changes from baseline (before the start of tolvaptan administration on the first day of the treatment period) mean and standard deviation (SD) were calculated. Baseline was 100% and the change rate was alculated like this. Percent change (%) = (\[body weight on the day after the third day of treatment with tolvaptan at the evaluation dose

GroupValue95% CI
Tolvaptan-0.371± 2.470
Improvement Rates of Lower Limb Edema Secondary · Day after Day 3 at evaluation dose

The improvement rate was defined as the percentage of subjects in whom a symptom was present at baseline and then markedly improved or improved after IMP administration. Improvement category is a 4-point scale below: * Markedly improved * Improved * Unchanged * Deteriorated

GroupValue95% CI
Tolvaptan68.650.7 – 83.1
Improvement Rates of Pulmonary Congestion Secondary · Day after Day 3 at evaluation dose

The improvement rate was defined as the percentage of subjects in whom a symptom was present at baseline and then markedly improved or improved after IMP administration. Improvement category is a 4-point scale below: * Markedly improved * Improved * Unchanged * Deteriorated

GroupValue95% CI
Tolvaptan51.633.1 – 69.8

Adverse events — posted to ClinicalTrials.gov

Time frame: Treatment-emergent adverse events (TEAEs) were collected from the start of IMP administration up to 16 days. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Tolvaptan
Serious: 1/60 (2%)
Deaths: 0/60

Serious adverse events (1 terms)

ReactionSystemTolvaptan
Cardiac failure chronicCardiac disorders
Other adverse events (29 terms — click to expand)

ReactionSystemTolvaptan
ThirstGeneral disorders
AnaemiaBlood and lymphatic system disorders
ConstipationGastrointestinal disorders
Dry mouthGastrointestinal disorders
VomitngGastrointestinal disorders
PyrexiaGeneral disorders
HyperkalaemiaMetabolism and nutrition disorders
NeutropeniaBlood and lymphatic system disorders
Cardiovascular insufficiencyCardiac disorders
Erythema of eyelidEye disorders
Abdominal painGastrointestinal disorders
NauseaGastrointestinal disorders
Gastrointestinal hypomotilityGastrointestinal disorders
Anal erythemaGastrointestinal disorders
NasopharyngitisInfections and infestations
Urinary tract infectionInfections and infestations
Bacterial infectionInfections and infestations
Blood pressure increasedInvestigations
Blood pressure systolic decreasedInvestigations
Hepatic enzyme increasedInvestigations
DehydrationMetabolism and nutrition disorders
HypokalaemiaMetabolism and nutrition disorders
PolydipsiaMetabolism and nutrition disorders
DizzinessNervous system disorders
HeadacheNervous system disorders
Renal impairmentRenal and urinary disorders
PruritusSkin and subcutaneous tissue disorders
RashSkin and subcutaneous tissue disorders
Skin exfoliationSkin and subcutaneous tissue disorders

Most-reported serious reactions: Cardiac failure chronic.

Data from ClinicalTrials.gov NCT03255226 adverse events section.

Sponsor's own description

To determine the efficacy, safety, and dose and regimen of tolvaptan in pediatric CHF patients with volume overload

Publications & conference data

1 peer-reviewed publication reference this trial (live from Europe PMC):

  1. Fluid assessment, fluid balance, and fluid overload in sick children: a report from the Pediatric Acute Disease Quality Initiative (ADQI) conference.
    Selewski DT, Barhight MF, Bjornstad EC, Ricci Z, et al · · 2024 · cited 34× · PMID 37934274 · DOI 10.1007/s00467-023-06156-w

Verify or expand the search:

Other trials of Tolvaptan

Trials testing the same drug.

Other Otsuka Pharmaceutical Co., Ltd. trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03255226.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing