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NCT03252535: ADORE-DH

Dose-response Evaluation of the Cellavita HD Product in Patients With Huntington's Disease

Completed Phase 2 Results posted Last updated 19 September 2025
What this trial tests

Phase 2 trial testing Cellavita HD lower dose in Huntington Disease in 49 participants. Completed in 30 April 2021.

Timeline
15 January 2018
Primary endpoint
23 March 2021
30 April 2021

Quick facts

Lead sponsorAzidus Brasil
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationrandomized
Designparallel
Maskingtriple
Primary purposetreatment
Enrollment49
Start date15 January 2018
Primary completion23 March 2021
Estimated completion30 April 2021
Sites1 location across Brazil

Drugs / interventions tested

Conditions studied

Sponsor

Azidus Brasil — full company profile →

Who can join

Adults 21 to 65, any sex, with Huntington Disease. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Efficacy by UHDRS-TMS Primary · monthly for eleven months

The primary endpoint was the rate of change (slope) in Unified Huntington's Disease Rating Scale - Total Motor Score from V0 to V11 (minimum 0, the best; and maximum 124, the worst). For each participant, a regression line was fitted (Y = a + bx), where b represents the individual slope, reflecting the annualised rate of motor progression. A negative slope suggests improvement or slower decline; a positive slope indicates worsening. To compare treatment efficacy, the slopes were analysed using a Mixed Model for Repeated Measures (MMRM), which accounts for intra-subject variability and missing

GroupValue95% CI
Nestacell (Former Cellavita HD) Lower Dose-1.23± 0.84
Nestacell (Former Cellavita HD) Higher Dose0.84± 0.90
Placebo Group8.91± 1.11
Efficacy by UHDRS-TFC Secondary · monthly for eleven months

Assessed by the rate of change (slope) from V0 to V11 in the UHDRS-TFC. The response of each participant or means of all participants was evaluated by the slopes of each regression line of UHDRS-TFC determined as follows: The equation describes the regression line: Y = a + bx, where: * "Y" is the dependent variable. * "a" is the constant that represents the intersection of the line with the vertical axis. * "b" is the angular coefficient, that is, the slope. * "x" is the independent variable. Therefore, the 'b' value represents the slope of the straight line that best fits the values collec

GroupValue95% CI
Nestacell (Former Cellavita HD) Lower Dose-0.29± 0.18
Nestacell (Former Cellavita HD) Higher Dose0.73± 0.18
Placebo Group-0.89± 0.26
Exposure to NestaCell (Former Cellavita HD) Product Secondary · eleven months

Number of administrations of NestaCell (Former Cellavita HD) and Placebo

GroupValue95% CI
Nestacell (Former Cellavita HD) Lower Dose9.0± 0.0
Nestacell (Former Cellavita HD) Higher Dose8.4± 1.5
Placebo Group9.0± 0.0

Adverse events — posted to ClinicalTrials.gov

Time frame: 11 months. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Nestacell (Former Cellavita HD) Lower Dose
Serious: 1/14 (7%)
Deaths: 0/14
Nestacell (Former Cellavita HD) Higher Dose
Serious: 0/14 (0%)
Deaths: 0/14
Placebo Group
Serious: 0/7 (0%)
Deaths: 0/7

Serious adverse events (1 terms)

ReactionSystemNestacell (Former Cellavit…Nestacell (Former Cellavit…Placebo Group
hospitalized for sinusitisInfections and infestations
Other adverse events (68 terms — click to expand)

ReactionSystemNestacell (Former Cellavit…Nestacell (Former Cellavit…Placebo Group
AlopeciaSkin and subcutaneous tissue disorders
FallInjury, poisoning and procedural complications
DyslipidemiaMetabolism and nutrition disorders
InfluenzaRespiratory, thoracic and mediastinal disorders
Abnormal hair growthSkin and subcutaneous tissue disorders
WoundSkin and subcutaneous tissue disorders
OverweightMetabolism and nutrition disorders
Back painMusculoskeletal and connective tissue disorders
Pain in extremitiesMusculoskeletal and connective tissue disorders
DiarrheaGastrointestinal disorders
NauseaGastrointestinal disorders
VomitGastrointestinal disorders
AnxietyPsychiatric disorders
DepressionPsychiatric disorders
Altered moodPsychiatric disorders
Depressed moodPsychiatric disorders
InsomniaPsychiatric disorders
Urinary tract infectionRenal and urinary disorders
Dermal cystSkin and subcutaneous tissue disorders
Subcutaneous hemorrhageSkin and subcutaneous tissue disorders
Change in hair colorSkin and subcutaneous tissue disorders
PruritusSkin and subcutaneous tissue disorders
Atopic dermatitisImmune system disorders
HypertriglyceridemiaMetabolism and nutrition disorders
AkathisiaNervous system disorders
HeadacheNervous system disorders
Cervicogenic gourd painNervous system disorders
InsomniaNervous system disorders
SomnolenceNervous system disorders
DizzinessNervous system disorders
Essential tremorNervous system disorders
VertigoNervous system disorders
Normochromic and normocytic anemiaBlood and lymphatic system disorders
ThrombocytopeniaBlood and lymphatic system disorders
MyalgiaMusculoskeletal and connective tissue disorders
DyspepsiaGastrointestinal disorders
Gastroesophageal reflux diseaseGastrointestinal disorders
OdynophagiaGastrointestinal disorders
Aphthous ulcerGastrointestinal disorders
Chest painGeneral disorders

Most-reported serious reactions: hospitalized for sinusitis.

Data from ClinicalTrials.gov NCT03252535 adverse events section.

Sponsor's own description

Cellavita HD is a stem-cell therapy for Huntington's Disease. This is a prospective, phase II, single-center, randomized (2:2:1), triple-blind, placebo controlled study, with two test doses of Cellavita HD product.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. New Avenues for the Treatment of Huntington's Disease.
    Kim A, Lalonde K, Truesdell A, Gomes Welter P, et al · · 2021 · cited 130× · PMID 34445070 · DOI 10.3390/ijms22168363
  2. Cell therapies in the clinic.
    Wang LL, Janes ME, Kumbhojkar N, Kapate N, et al · · 2021 · cited 99× · PMID 34027097 · DOI 10.1002/btm2.10214
  3. Differentiation of Human Mesenchymal Stem Cells towards Neuronal Lineage: Clinical Trials in Nervous System Disorders.
    Hernández R, Jiménez-Luna C, Perales-Adán J, Perazzoli G, et al · · 2020 · cited 95× · PMID 31649208 · DOI 10.4062/biomolther.2019.065
  4. From Pathogenesis to Therapeutics: A Review of 150 Years of Huntington's Disease Research.
    Jiang A, Handley RR, Lehnert K, Snell RG. · · 2023 · cited 88× · PMID 37629202 · DOI 10.3390/ijms241613021
  5. Current and Possible Future Therapeutic Options for Huntington's Disease.
    Ferguson MW, Kennedy CJ, Palpagama TH, Waldvogel HJ, et al · · 2022 · cited 66× · PMID 35615642 · DOI 10.1177/11795735221092517
  6. Huntington’s Disease Clinical Trials Corner: February 2018
    Rodrigues FB, Wild EJ. · · 2018 · cited 45× · PMID 29480210 · DOI 10.3233/jhd-189001
  7. Huntington's Disease Clinical Trials Corner: March 2024.
    Estevez-Fraga C, Tabrizi SJ, Wild EJ. · · 2024 · cited 31× · PMID 38489195 · DOI 10.3233/jhd-240017
  8. The Clinical Trials of Mesenchymal Stromal Cells Therapy.
    Kouchakian MR, Baghban N, Moniri SF, Baghban M, et al · · 2021 · cited 30× · PMID 34745268 · DOI 10.1155/2021/1634782

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Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03252535.

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