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NCT03233204

Olaparib in Treating Patients With Relapsed or Refractory Advanced Solid Tumors, Non-Hodgkin Lymphoma, or Histiocytic Disorders With Defects in DNA Damage Repair Genes (A Pediatric MATCH Treatment Trial)

Completed Phase 2 Results posted Last updated 11 December 2024
What this trial tests

Phase 2 trial testing Olaparib in Advanced Malignant Solid Neoplasm in 6 participants. Completed in 30 June 2024.

Timeline
14 September 2017
Primary endpoint
31 March 2023
30 June 2024

Quick facts

Lead sponsorNational Cancer Institute (NCI)
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationna
Designsingle group
Maskingnone
Primary purposetreatment
Enrollment6
Start date14 September 2017
Primary completion31 March 2023
Estimated completion30 June 2024
Sites113 locations across Puerto Rico, United States

Drugs / interventions tested

Conditions studied

Sponsor

National Cancer Institute (NCI)

Who can join

Adults 12 Months to 21, any sex, with Advanced Malignant Solid Neoplasm or Ann Arbor Stage III Childhood Non-Hodgkin Lymphoma. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Objective Response Rate (Complete Response/Partial Response) Primary · Up to 2 years from study entry

A responder is defined as a patient who achieves a best response of partial response or complete response on the study. Response rates will be calculated as the percent of evaluable patients who are responders, and confidence intervals will be constructed using the Wilson score interval method. The revised Response Evaluation Criteria in Solid Tumors (RECIST) guideline (version 1.1) was used to determine response and progression in this study, with specific criteria outlined for the different subtypes of tumors (e.g., 2-dimensional measurements for central nervous system (CNS) tumors).

GroupValue95% CI
Treatment (Olaparib)00 – 0
Progression Free Survival (PFS) Secondary · Up to 6 months from study entry

The Kaplan-Meier method will be used to estimate the 6 month PFS. PFS is defined as time from initiation of protocol treatment to disease progression, recurrence, death from any cause, or date of last contact.

GroupValue95% CI
Treatment (Olaparib)33.34.6 – 67.6
Percentage of Patients Experiencing Treatment-related Grade 3 or Higher Adverse Events Secondary · Up to 2 years from study entry

Percentage of patients experiencing treatment-related grade 3 or higher adverse events will be evaluated according to National Cancer Institute Common Terminology Criteria for Adverse Events version 5.0.

GroupValue95% CI
Treatment (Olaparib)16.70.4 – 64.1
Pharmacokinetics (PK) of Olaparib, Area Under the Curve (AUC) Secondary · Up to day 8 of cycle 1

The mean (sd) of the AUC.

GroupValue95% CI
Treatment (Olaparib)48.8± 27.8

Adverse events — posted to ClinicalTrials.gov

Time frame: Adverse Events monitored/assessed from enrollment to 30 days after the end of treatment, up to 2 years. All-Cause Mortality monitored/assessed up to 5 years. Reporting threshold: 0%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Treatment (Olaparib)
Serious: 3/6 (50%)
Deaths: 4/6

Serious adverse events (4 terms)

ReactionSystemTreatment (Olaparib)
Disease progressionGeneral disorders
Allergic reactionImmune system disorders
HypercalcemiaMetabolism and nutrition disorders
SeizureNervous system disorders
Other adverse events (47 terms — click to expand)

ReactionSystemTreatment (Olaparib)
Lymphocyte count decreasedInvestigations
AnemiaBlood and lymphatic system disorders
NauseaGastrointestinal disorders
White blood cell decreasedInvestigations
VomitingGastrointestinal disorders
DizzinessNervous system disorders
HeadacheNervous system disorders
HypertensionVascular disorders
Cardiac disorders - Other, specifyCardiac disorders
Sinus tachycardiaCardiac disorders
Eye painEye disorders
Optic nerve disorderEye disorders
Abdominal painGastrointestinal disorders
ConstipationGastrointestinal disorders
DyspepsiaGastrointestinal disorders
Edema limbsGeneral disorders
FatigueGeneral disorders
Gait disturbanceGeneral disorders
General disorders and administration site conditions - Other, specifyGeneral disorders
MalaiseGeneral disorders
ConjunctivitisInfections and infestations
Alanine aminotransferase increasedInvestigations
Aspartate aminotransferase increasedInvestigations
Creatinine increasedInvestigations
Investigations - Other, specifyInvestigations
Neutrophil count decreasedInvestigations
Platelet count decreasedInvestigations
Weight lossInvestigations
AnorexiaMetabolism and nutrition disorders
HyperglycemiaMetabolism and nutrition disorders
HypernatremiaMetabolism and nutrition disorders
HypoalbuminemiaMetabolism and nutrition disorders
HypokalemiaMetabolism and nutrition disorders
HyponatremiaMetabolism and nutrition disorders
Muscle weakness lower limbMusculoskeletal and connective tissue disorders
DysgeusiaNervous system disorders
AnxietyPsychiatric disorders
InsomniaPsychiatric disorders
HematuriaRenal and urinary disorders
ProteinuriaRenal and urinary disorders

Most-reported serious reactions: Disease progression, Allergic reaction, Hypercalcemia, Seizure.

Data from ClinicalTrials.gov NCT03233204 adverse events section.

Sponsor's own description

This phase II Pediatric MATCH trial studies how well olaparib works in treating patients with solid tumors, non-Hodgkin lymphoma, or histiocytic disorders with defects in deoxyribonucleic acid (DNA) damage repair genes that have spread to other places in the body (advanced) and have come back (relapsed) or do not respond to treatment (refractory). Olaparib is an inhibitor of PARP, an enzyme that helps repair DNA when it becomes damaged. Blocking PARP may help keep cancer cells from repairing their damaged DNA, causing them to die. PARP inhibitors are a type of targeted therapy.

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Targeting Molecular Mechanisms Underlying Treatment Efficacy and Resistance in Osteosarcoma: A Review of Current and Future Strategies.
    Lilienthal I, Herold N. · · 2020 · cited 216× · PMID 32961800 · DOI 10.3390/ijms21186885
  2. Current and Future Treatment Strategies for Rhabdomyosarcoma.
    Chen C, Dorado Garcia H, Scheer M, Henssen AG. · · 2019 · cited 131× · PMID 31921698 · DOI 10.3389/fonc.2019.01458
  3. Advances in the Knowledge of the Molecular Biology of Glioblastoma and Its Impact in Patient Diagnosis, Stratification, and Treatment.
    Delgado-Martín B, Medina MÁ. · · 2020 · cited 129× · PMID 32382477 · DOI 10.1002/advs.201902971
  4. Targeting DNA repair pathway in cancer: Mechanisms and clinical application.
    Wang M, Chen S, Ao D. · · 2021 · cited 84× · PMID 34977872 · DOI 10.1002/mco2.103
  5. Pharmaco-proteogenomic profiling of pediatric diffuse midline glioma to inform future treatment strategies.
    Findlay IJ, De Iuliis GN, Duchatel RJ, Jackson ER, et al · · 2022 · cited 77× · PMID 34759345 · DOI 10.1038/s41388-021-02102-y
  6. Drug Resistance in Osteosarcoma: Emerging Biomarkers, Therapeutic Targets and Treatment Strategies.
    Hattinger CM, Patrizio MP, Fantoni L, Casotti C, et al · · 2021 · cited 75× · PMID 34207685 · DOI 10.3390/cancers13122878
  7. Molecular mechanisms underpinning sarcomas and implications for current and future therapy.
    Damerell V, Pepper MS, Prince S. · · 2021 · cited 75× · PMID 34188019 · DOI 10.1038/s41392-021-00647-8
  8. PARP1 in Carcinomas and PARP1 Inhibitors as Antineoplastic Drugs.
    Wang L, Liang C, Li F, Guan D, et al · · 2017 · cited 67× · PMID 28991194 · DOI 10.3390/ijms18102111

Verify or expand the search:

Other trials of Olaparib

Trials testing the same drug.

Other recruiting trials for Advanced Malignant Solid Neoplasm

Currently open trials in the same condition.

Other National Cancer Institute (NCI) trials

Trials by the same sponsor.

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Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT03233204.

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