Last reviewed · How we verify

NCT02983617

Safety and Efficacy of the Combination of Tirabrutinib and Entospletinib With and Without Obinutuzumab in Adults With Chronic Lymphocytic Leukemia (CLL)

Completed Phase 2 Results posted Last updated 21 December 2021
What this trial tests

Phase 2 trial testing Tirabrutinib in Chronic Lymphocytic Leukemia in 36 participants. Completed in 1 October 2020.

Timeline
6 April 2017
Primary endpoint
20 February 2019
1 October 2020

Quick facts

Lead sponsorGilead Sciences
PhasePhase 2
StatusCompleted
Study typeINTERVENTIONAL
Allocationnon randomized
Designparallel
Maskingnone
Primary purposetreatment
Enrollment36
Start date6 April 2017
Primary completion20 February 2019
Estimated completion1 October 2020
Sites15 locations across Germany

Drugs / interventions tested

Conditions studied

Sponsor

Gilead Sciences — full company profile →

Who can join

18 and older, any sex, with Chronic Lymphocytic Leukemia. Patients with the condition only — healthy volunteers not accepted.

Results — posted to ClinicalTrials.gov

Per-arm endpoint measurements with 95% confidence intervals where reported. Source: trial results section.

Rate of Complete Remission/Complete Remission With Incomplete Recovery of the Bone Marrow (CR/CRi), as Assessed by Investigator Using Modified International Workshop on Chronic Lymphocytic Leukemia (IWCLL) 2008 Criteria at Week 25 Primary · Week 25

Rate of CR per modified IWCLL 2008 criteria at Week 25 was defined as the percentage of participants who achieved CR/complete remission with incomplete recovery of the bone marrow (CRi) at Week 25. CR: meeting following criteria and no disease related symptoms: no lymphadenopathy \> 1.5 cm/hepatomegaly/splenomegaly; lymphocytes \< 4000/μL; bone marrow sample must be normocellular with 30% lymphocytes and no B-lymphoid nodules; platelets \> 100,000/µL; hemoglobin \> 11 g/dL; and neutrophils \> 1500/µL. CRi: CR criteria (no lymphadenopathy \> 1.5 cm/hepatomegaly/splenomegaly; lymphocytes \< 4000

GroupValue95% CI
Tirabrutinib + Entospletinib00 – 39.3
Tirabrutinib + Entospletinib + Obinutuzumab6.71.2 – 19.5
Rate of CR With Bone Marrow Minimal Residual Disease (CR/BM MRD) Negativity, as Assessed by the Investigator Using the Modified IWCLL 2008 Criteria at Week 25 Secondary · Week 25

Rate of CR/BM MRD at Week 25 was defined as percentage of participants who achieved CR/CRi per modified IWCLL 2008 criteria and also achieved BM MRD negativity at Week 25. CR: meeting following criteria and no disease related symptoms: no lymphadenopathy \> 1.5 cm/hepatomegaly/splenomegaly; lymphocytes \< 4000/μL; bone marrow sample must be normocellular with 30% lymphocytes and no B-lymphoid nodules; platelets \> 100,000/µL; hemoglobin \> 11 g/dL; and neutrophils \> 1500/µL. CRi: CR criteria (no lymphadenopathy \> 1.5 cm/hepatomegaly/splenomegaly; lymphocytes \< 4000/μL; bone marrow \[hypocel

GroupValue95% CI
Tirabrutinib + Entospletinib00 – 39.3
Tirabrutinib + Entospletinib + Obinutuzumab3.30.2 – 14.9
Rate of CR With Peripheral Minimal Residual Disease (CR/PB MRD) Negativity, as Assessed by the Investigator Using the Modified IWCLL 2008 Criteria at Week 25 Secondary · Week 25

Rate of CR/PB MRD at Week 25 was defined as the percentage of participants who achieved CR/CRi per modified IWCLL 2008 criteria and also achieved PB MRD negativity at Week 25. CR: meeting following criteria and no disease related symptoms: no lymphadenopathy \> 1.5 cm/hepatomegaly/splenomegaly; lymphocytes \< 4000/μL; bone marrow sample must be normocellular with 30% lymphocytes and no B-lymphoid nodules; platelets \> 100,000/µL; hemoglobin \> 11 g/dL; and neutrophils \> 1500/µL. CRi: CR criteria (no lymphadenopathy \> 1.5 cm/hepatomegaly/splenomegaly; lymphocytes \< 4000/μL; bone marrow \[hyp

GroupValue95% CI
Tirabrutinib + Entospletinib00 – 39.3
Tirabrutinib + Entospletinib + Obinutuzumab3.30.2 – 14.9
Overall Response Rate (ORR), as Assessed by the Investigator Using the Modified IWCLL 2008 Criteria at Week 25 Secondary · Week 25

ORR was assessed based on modified IWCLL 2008 criteria and was defined as percentage of participants achieving a CR, CRi, partial remission (PR; including nodular partial response \[nPR\]), and PR with lymphocytosis (PR-L). CR and CRi: meeting all the criteria that have been defined in Outcome measures 1, 2 and 3. PR: ≥ 2 of these: ≥ 50% decrease in lymphocytes, lymphadenopathy, size of liver, size of spleen, and 50% decrease in bone marrow infiltrates; and ≥ 1 of these: neutrophils \> 1500/μL or ≥ 50% increase from Baseline, platelets ≥ 100,000/µL or ≥ 50% increase from Baseline, hemoglobin \

GroupValue95% CI
Tirabrutinib + Entospletinib100.060.7 – 100.0
Tirabrutinib + Entospletinib + Obinutuzumab90.076.1 – 97.2
Percentage of Participants Experiencing Any Treatment-Emergent Adverse Events (AEs) and Treatment-Emergent Serious Adverse Events (SAEs) Secondary · First dose date up to the last dose date (maximum: 105.9 weeks) plus 30 days

A treatment emergent AE is defined as an AE that occurs or worsens in severity on or after the date of the first dose of study drug but no later than 30 days after the permanent discontinuation of study drug or an AE leading to discontinuation of study drug. A SAE is defined as an event that, at any dose, resulted in any of the following: death, life-threatening, in-patient hospitalization or prolongation of existing hospitalization, persistent or significant disability/incapacity, a congenital anomaly/birth defect, or a medically important event or reaction.

Any Treatment-Emergent AEs
GroupValue95% CI
Tirabrutinib + Entospletinib100.0
Tirabrutinib + Entospletinib + Obinutuzumab100.0
Treatment-Emergent SAEs
GroupValue95% CI
Tirabrutinib + Entospletinib16.7
Tirabrutinib + Entospletinib + Obinutuzumab50.0

Adverse events — posted to ClinicalTrials.gov

Time frame: Adverse Events: First dose date up to last dose date (maximum: 105.9 weeks) plus 30 days; All-Cause Mortality: Enrollment up to 42 months. Reporting threshold: 5%. Adverse-event reports describe events observed during the trial — not all are caused by the drug.

Tirabrutinib + Entospletinib
Serious: 1/6 (17%)
Deaths: 0/6
Tirabrutinib + Entospletinib + Obinutuzumab
Serious: 15/30 (50%)
Deaths: 4/30

Serious adverse events (24 terms)

ReactionSystemTirabrutinib + EntospletinibTirabrutinib + Entospletin…
PneumoniaInfections and infestations
Infusion related reactionInjury, poisoning and procedural complications
SyncopeNervous system disorders
AnaemiaBlood and lymphatic system disorders
HydroceleCongenital, familial and genetic disorders
Disease progressionGeneral disorders
PyrexiaGeneral disorders
Bronchopulmonary aspergillosisInfections and infestations
Covid-19 pneumoniaInfections and infestations
NasopharyngitisInfections and infestations
PeritonsillitisInfections and infestations
Soft tissue infectionInfections and infestations
TracheobronchitisInfections and infestations
Urinary tract infectionInfections and infestations
Procedural haemorrhageInjury, poisoning and procedural complications
Subdural haematomaInjury, poisoning and procedural complications
Renal impairmentRenal and urinary disorders
Urethral caruncleRenal and urinary disorders
Benign prostatic hyperplasiaReproductive system and breast disorders
Pleural effusionRespiratory, thoracic and mediastinal disorders
PneumonitisRespiratory, thoracic and mediastinal disorders
PemphigoidSkin and subcutaneous tissue disorders
HaematomaVascular disorders
Peripheral arterial occlusive diseaseVascular disorders
Other adverse events (91 terms — click to expand)

ReactionSystemTirabrutinib + EntospletinibTirabrutinib + Entospletin…
NeutropeniaBlood and lymphatic system disorders
FatigueGeneral disorders
PyrexiaGeneral disorders
NasopharyngitisInfections and infestations
NauseaGastrointestinal disorders
CoughRespiratory, thoracic and mediastinal disorders
ConstipationGastrointestinal disorders
DiarrhoeaGastrointestinal disorders
ChillsGeneral disorders
Oedema peripheralGeneral disorders
BronchitisInfections and infestations
Urinary tract infectionInfections and infestations
HeadacheNervous system disorders
HaematomaVascular disorders
VomitingGastrointestinal disorders
Oral herpesInfections and infestations
PruritusSkin and subcutaneous tissue disorders
RashSkin and subcutaneous tissue disorders
Infusion related reactionInjury, poisoning and procedural complications
Blood bilirubin increasedInvestigations
ArthralgiaMusculoskeletal and connective tissue disorders
Back painMusculoskeletal and connective tissue disorders
Pain in extremityMusculoskeletal and connective tissue disorders
AnaemiaBlood and lymphatic system disorders
Abdominal painGastrointestinal disorders
FlatulenceGastrointestinal disorders
GastritisGastrointestinal disorders
Herpes zosterInfections and infestations
PneumoniaInfections and infestations
SinusitisInfections and infestations
Upper respiratory tract infectionInfections and infestations
Arthropod biteInjury, poisoning and procedural complications
Muscle spasmsMusculoskeletal and connective tissue disorders
Neck painMusculoskeletal and connective tissue disorders
DizzinessNervous system disorders
Night sweatsSkin and subcutaneous tissue disorders
PetechiaeSkin and subcutaneous tissue disorders
UrticariaSkin and subcutaneous tissue disorders
LeukopeniaBlood and lymphatic system disorders
ThrombocytopeniaBlood and lymphatic system disorders

Most-reported serious reactions: Pneumonia, Infusion related reaction, Syncope, Anaemia, Hydrocele, Disease progression, Pyrexia, Bronchopulmonary aspergillosis.

Data from ClinicalTrials.gov NCT02983617 adverse events section.

Sponsor's own description

The primary objective of this study is to determine the preliminary efficacy of the combination of tirabrutinib (formerly GS-4059) and entospletinib with obinutuzumab in adults with relapsed or refractory chronic lymphocytic leukemia (CLL).

Publications & conference data

8 peer-reviewed publications reference this trial (live from Europe PMC):

  1. Bruton Tyrosine Kinase Inhibitors: Present and Future.
    Burger JA. · · 2019 · cited 143× · PMID 31764119 · DOI 10.1097/ppo.0000000000000412
  2. From Biology to Therapy: The CLL Success Story.
    Yosifov DY, Wolf C, Stilgenbauer S, Mertens D. · · 2019 · cited 48× · PMID 31723816 · DOI 10.1097/hs9.0000000000000175
  3. Bruton's tyrosine kinase inhibitors: first and second generation agents for patients with Chronic Lymphocytic Leukemia (CLL).
    Thompson PA, Burger JA. · · 2018 · cited 44× · PMID 29125406 · DOI 10.1080/13543784.2018.1404027
  4. Novel Agents in Chronic Lymphocytic Leukemia: New Combination Therapies and Strategies to Overcome Resistance.
    Fürstenau M, Eichhorst B. · · 2021 · cited 31× · PMID 33809580 · DOI 10.3390/cancers13061336
  5. B cell receptor signaling and associated pathways in the pathogenesis of chronic lymphocytic leukemia.
    Schmid VK, Hobeika E. · · 2024 · cited 16× · PMID 38469232 · DOI 10.3389/fonc.2024.1339620
  6. Clinical application of obinutuzumab for treating chronic lymphocytic leukemia.
    Luan C, Chen B. · · 2019 · cited 13× · PMID 31692500 · DOI 10.2147/dddt.s212500
  7. Efficacy and Safety of the Combination of Tirabrutinib and Entospletinib With or Without Obinutuzumab in Relapsed Chronic Lymphocytic Leukemia.
    Kutsch N, Pallasch C, Tausch E, Böhme V, et al · · 2022 · cited 12× · PMID 35284802 · DOI 10.1097/hs9.0000000000000692
  8. Therapeutic approaches and drug-resistance in chronic lymphocytic leukaemia.
    Fatima N, Crassini KR, Thurgood L, Shen Y, et al · · 2020 · cited 3× · PMID 35582439 · DOI 10.20517/cdr.2019.111

Verify or expand the search:

Other trials of Tirabrutinib

Trials testing the same drug.

Other recruiting trials for Chronic Lymphocytic Leukemia

Currently open trials in the same condition.

Other Gilead Sciences trials

Trials by the same sponsor.

Verify against primary sources

Data sources for this page

Drug Landscape aggregates and links these public records for informational use only. Always verify against the primary source before clinical or regulatory decisions. Canonical URL: https://druglandscape.com/trial/NCT02983617.

Primary sources · FDA · ClinicalTrials.gov · EMA · SEC EDGAR · ChEMBL · Wikidata · full sourcing